Prenatal Spectrum of COL2A1-Related Spondyloepiphyseal Dysplasia Congenita: A Review and Two Case Reports

Interim Results From a Multicenter Observational Safety Study of Patients Treated With Voretigene Neparvovec-rzyl in the United States

2026-07-22

0

PRE

AI

A

Aaron Nagiel *

S

Stephen R. Russell

B

Byron L. Lam

J

Jason Comander

T

Tomás S. Alemán

C

Cagri G. Besirli

R

Robert A. Sisk

P

Paul Yang

C

Christina Y. Weng

D

Daniel C. Chung

A

Aishwarya Thakre

J

Juha‐Matti Savola

D

D. Rousso *

DOI：10.1016/j.ophtha.2026.07.007

Original request for help

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En 中文

To assess long-term safety and exploratory ophthalmic outcomes in patients treated with voretigene neparvovec-rzyl (VN) in US clinical practice.