Not logged in Adults With Acid Sphingomyelinase Deficiency Have Sustained Improvements in Clinical Outcomes With up to 5 Years of Olipudase Alfa Enzyme Replacement Therapy: ASCEND Trial Final Results Wasserstein, Melissa P.; Hollak, Carla E.; Barbato, Antonio; Gallagher, Renata C.; Giugliani, Roberto; Guelbert, Norberto Bernardo; Hennermann, Julia B.; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Thurberg, Beth L.; Villarrubia, Jesus; Armstrong, Nicole M.; Bhushan, Shashi; Kim, Yong; Kumar, Monica Share Save
Cognitive Behavioral Therapy for Youth With Childhood-Onset Lupus: A Randomized Clinical Trial Cunningham, Natoshia R.; Senger-carpenter, Thea; Zuckerman, Jocelyn; Adler, Michelle; Reid, Mallet R.; Danguecan, Ashley; Pereira, Luana Flores; Mossad, Sarah I.; Ely, Samantha L.; Abulaban, Khalid; Kessler, Elizabeth A.; Rosenwasser, Natalie; Rubinstein, Tamar B.; Ogbu, Ekemini A.; Smitherman, Emily A.; Miller, Alaina; Abounader, Taylor; Ross, Elizabeth; Timmerman, Livie; Sharma, Dhriti; Stinson, Jennifer N.; Allen, Stacy; Nanda, Kabita; El Tal, Tala; Levy, Deborah M.; Hiraki, Linda T.; Brunner, Hermine I.; Reeves, Mathew; Pierce, Steven J.; Knight, Andrea Share Save
A Case of EBV-Driven Histiocytic Sarcoma as PTLD in a Pediatric Heart Transplant Patient Chelemedos, Kasey; Shah, Nishma; Quijano, Kaitlyn; Hari, Nikhila; Bendari, Ahmed; Stratford, Rylen; Banerjee, Surita; Weiss, Danielle; Baker, Amanda; Kobets, Andrew; Tal, Adit Share Save
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Employing effective recruitment and retention strategies to engage a diverse pediatric population in genomics research Ramos, Michelle A.; Bonini, Katherine E.; Scarimbolo, Laura; Kelly, Nicole R.; Insel, Beverly; Suckiel, Sabrina A.; Brown, Kaitlyn; Di Biase, Miranda; Gallagher, Katie M.; Lopez, Jessenia; Aguiniga, Karla Lopez; Marathe, Priya N.; Maria, Estefany; Odgis, Jacqueline A.; Rodriguez, Jessica E.; Rodriguez, Michelle A.; Ruiz, Nairovylex; Sebastin, Monisha; Yelton, Nicole M.; Cunningham-Rundles, Charlotte; Gertner, Melvin; Laguerre, Irma; McDonald, Thomas, V; McGoldrick, Patricia E.; Robinson, Mimsie; Rubinstein, Arye; Shulman, Lisa H.; Williams, Trinisha; Wolf, Steven M.; Yozawitz, Elissa G.; Zinberg, Randi E.; Abul-Husn, Noura S.; Bauman, Laurie J.; Diaz, George A.; Ferket, Bart S.; Greally, John M.; Jobanputra, Vaidehi; Gelb, Bruce D.; Kenny, Eimear E.; Wasserstein, Melissa P.; Horowitz, Carol R. Share Save
Concordance of MASLD and NAFLD nomenclature in youth participating in the TARGET-NASH real-world cohort Sanchez-Torres, Cristian; Tovar, Ana Ramirez; Chatman, Kelsey; Morris, Heather L.; Yu, Feng; Mospan, Andrea R.; Diehl, Anna Mae; Leung, Daniel H.; Viswanathan, Preeti; Squires, James E.; Palle, Sirish; Vos, Miriam B. Share Save
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Designing Prefaculty Competencies for Diverse Learners Through a Modified Delphi Process Lee, Rosa; Lucas, Raymond; Dickerman, Joel; Day, Lukejohn W.; Guzman, Daniel; Kothari, Pooja; Love, LaTanya; McDade, William; Rodgers, Ashley; Verduzco-Gutierrez, Monica; Zhang, Lindy; Sanchez, John Paul Share Save
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Multicenter Analysis of Valganciclovir Prophylaxis in Pediatric Solid Organ Transplant Recipients Foca, Marc; Demirhan, Salih; Munoz, Flor M.; Deray, Kristen G. Valencia; Bocchini, Claire E.; Sharma, Tanvi S.; Sherman, Gilad; Muller, William J.; Heald-Sargent, Taylor; Danziger-Isakov, Lara; Blum, Samantha; Boguniewicz, Juri; Bacon, Samantha; Joseph, Tuhina; Smith, Jodi; Ardura, Monica, I; Su, Yin; Maron, Gabriela M.; Ferrolino, Jose; Herold, Betsy C. Share Save
Evaluating parental personal utility of pediatric genetic and genomic testing in a diverse, multilingual population Marathe, Priya N.; Suckiel, Sabrina A.; Bonini, Katherine E.; Kelly, Nicole R.; Scarimbolo, Laura; Insel, Beverly J.; Odgis, Jacqueline A.; Sebastin, Monisha; Ramos, Michelle A.; Di Biase, Miranda; Gallagher, Katie M.; Brown, Kaitlyn; Rodriguez, Jessica E.; Yelton, Nicole; Aguiniga, Karla Lopez; Rodriguez, Michelle A.; Maria, Estefany; Lopez, Jessenia; Zinberg, Randi E.; Diaz, George A.; Greally, John M.; Abul-Husn, Noura S.; Bauman, Laurie J.; Gelb, Bruce D.; Wasserstein, Melissa P.; Kenny, Eimear E.; Horowitz, Carol R. Share Save
Pediatric Department Approaches to Promote Diversity, Equity, and Inclusion Cabana, Michael D.; Alarcon, Pedro A. de; Allen, Erin; Bean, Xylina D.; Brophy, Patrick D.; Ortega, Loretta Cordova de; Degnon, Laura; First, Lewis R.; Dennery, Phyllis A.; Salazar, Juan C.; Schleien, Charles; Geme, Joseph W. St.; Parra-Roide, Lilia; Walker-Harding, Leslie R. Share Save
ACR Appropriateness Criteria® Soft Tissue Vascular Anomalies: Vascular Malformations and Infantile Vascular Tumors (Non-CNS)-Child Bardo, Dianna M. E.; Gill, Anne E.; Iyer, Ramesh S.; Chan, Sherwin S.; Cooper, Matthew L.; Dasgupta, Roshni A.; Guimaraes, Carolina V.; Hammer, Matthew R.; Krowchuk, Daniel P.; Levin, Terry L.; Liang, Marilyn G.; Meyers, Mariana L.; Samet, Jonathan D.; Sammer, Marla B. K.; Schooler, Gary R.; Squires, Judy H.; Sura, Amit S.; Trout, Andrew T.; Pruthi, Sumit Share Save
Testicular Dysfunction in Male Childhood Cancer Survivors Treated With Radiation Therapy: A PENTEC Comprehensive Review Baliga, Sujith; Patel, Samir; El Naqa, Issam; Li, X. Allen; Cohen, Laurie E.; Howell, Rebecca M.; Hoppe, Bradford S.; Constine, Louis S.; Palmer, Joshua D.; Hamstra, Daniel; Olch, Arthur J. Share Save