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SavePilot study of newborn screening for six lysosomal diseases in Brazil
Kubaski, Francyne; Sousa, Ines; Amorim, Tatiana; Pereira, Danilo; Silva, Camilo; Chaves, Vitor; Brusius-Facchin, Ana Carolina; Netto, Alice B. O.; Soares, Juliano; Vairo, Filippo; Poletto, Edina; Trometer, Joe; Souza, Alexandre; Ranieri, Enzo; Polo, Giulia; Hong, Xinying; Herbst, Zackary M.; Burlina, Alberto; Gelb, Michael H.; Giugliani, Roberto
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SaveAt-Risk Genomic Findings for Pediatric-Onset Disorders From Genome Sequencing vs Medically Actionable Gene Panel in Proactive Screening of Newborns and Children
Balciuniene, Jorune; Liu, Ruby; Bean, Lora; Guo, Fen; Nallamilli, Babi Ramesh Reddy; Guruju, Naga; Chen-Deutsch, Xiangwen; Yousaf, Rizwan; Fura, Kristina; Chin, Ephrem; Mathur, Abhinav; Ma, Zeqiang; Carmichael, Jonathan; da Silva, Cristina; Collins, Christin; Hegde, Madhuri
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SaveA lipoglycopeptide antibiotic for Gram-positive biofilm-related infections
Blaskovich, Mark A. T.; Hansford, Karl A.; Butler, Mark S.; Ramu, Soumya; Kavanagh, Angela M.; Jarrad, Angie M.; Prasetyoputri, Anggia; Pitt, Miranda E.; Huang, Johnny X.; Lindahl, Fredrik; Ziora, Zyta M.; Bradford, Tanya; Muldoon, Craig; Rajaratnam, Premraj; Pelingon, Ruby; Edwards, David J.; Zhang, Bing; Amado, Maite; Elliott, Alysha G.; Zuegg, Johannes; Coin, Lachlan; Woischnig, Anne-Kathrin; Khanna, Nina; Breidenstein, Elena; Stincone, Anna; Mason, Clive; Khan, Nawaz; Cho, Hye-Kyung; Karau, Melissa J.; Greenwood-Quaintance, Kerryl E.; Patel, Robin; Wootton, Mandy; James, Meagan L.; Hutton, Melanie L.; Lyras, Dena; Ogunniyi, Abiodun D.; Mahdi, Layla K.; Trott, Darren J.; Wu, Xiaoqian; Niles, Samantha; Lewis, Kim; Smith, Jordan R.; Barber, Katie E.; Yim, Juwon; Rice, Seth Alan; Rybak, Michael J.; Ishmael, Chad R.; Hori, Kellyn R.; Bernthal, Nicholas M.; Francis, Kevin P.; Roberts, Jason A.; Paterson, David L.; Cooper, Matthew A.
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SaveA united front on tackling a pandemic - the true value of industry and government partnerships
Jarvis, Ian; Chin, Ephrem; Rosendorff, Adam; Bean, Lora; Dallaire, Stephanie; Best, John; Wilbraham, Stephanie; Romigh, Sean; Borandi, P. J.; Ma, Zeqiang; Dennewitz, LeeAnn; Habibi, Max; Burrows, Miles; Hegde, Madhuri
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SavePilot study update: Newborn screening for lysosomal disorders in Brazil
Kubaski, Francyne; Sousa, Ines; Amorim, Tatiana; Badaro, Juliana; Pereira, Danilo; Silva, Camilo; Brusius-Facchin, Ana C.; Netto, Alice B. O.; Trometer, Joe; Souza, Alexandre; Ranieri, Enzo; Polo, Giulia; Hong, Xinying; Burlina, Alberto; Gelb, Michael; Giugliani, Roberto
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