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SavePhenotypic characterization of dominantly inherited distal nebulin myopathy
Henning, Franclo; Naidu, Kireshnee; Thomas, Pearl; Schoeman, Mardelle; Zaharie, Dan; Patel, Krutik; Dominik, Natalia; Efthymiou, Stephanie; Wilson, Lindsay A.; Hanna, Michael G.; Straub, Volker; Sagath, Lydia; Lehtokari, Vilma-Lotta
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SaveAdults With Acid Sphingomyelinase Deficiency Have Sustained Improvements in Clinical Outcomes With up to 5 Years of Olipudase Alfa Enzyme Replacement Therapy: ASCEND Trial Final Results
Wasserstein, Melissa P.; Hollak, Carla E.; Barbato, Antonio; Gallagher, Renata C.; Giugliani, Roberto; Guelbert, Norberto Bernardo; Hennermann, Julia B.; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Thurberg, Beth L.; Villarrubia, Jesus; Armstrong, Nicole M.; Bhushan, Shashi; Kim, Yong; Kumar, Monica
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SaveFixed-wing air transport of patients with spinal pathologies: a scoping review of current evidence and future research priorities
Thamilmaran, Ashviniy; Hodgson, Zak; Peramatzis, Konstantinos; Karampouga, Maria; Jarratt, Mark; Tsianaka, Eleni; Janssen, Insa K.; Tasiou, Anastasia; Keser, Nese; Murphy, Mary
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SaveEffectiveness of galcanezumab versus topiramate, amitriptyline, and other select traditional oral migraine preventives with evidence of efficacy: 3-Month results from the TRIUMPH study
Joshi, Shivang; Tassorelli, Cristina; Matharu, Manjit; Alsaadi, Taoufik; Vallarino, Carlos; Viktrup, Lars; Vincent, Maurice; Robinson, Rebecca L.
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SaveProspective Evaluation of the Neurology Same Day Emergency Care (NeuroSDEC) Model in Secondary Care: data from 931 patients over the first 12 months
Alim-Marvasti, Ali; Balaratnam, Michelle; Sacks, Benjamin; Bierrum, William; Rocha, Maria Francisca; See, Isaiah; Macarimban, Roberto; Lane, Charlie; Koohi, Nehzat; Schlattl, Anne; Gregson, Christine; Killingley, Ben; Henry, Alun Marc; Baruah, Timothy; Turner, Chris; Kaski, Diego; Chandratheva, Arvind; Simister, Robert; Haider, Salman
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SaveAnti-inflammatory effects and safety of omega-3 fatty acids in haemodialysis: A systematic review and meta-analysis
Blair, Carolyn; Slee, Adrian; McKeaveney, Clare; Maxwell, Alexander P.; Awan, Faizan; Brown, Malcolm; Davenport, Andrew; Fogarty, Damian; Fouque, Denis; Johnston, William; Kalantar-Zadeh, Kamyar; Mullan, Robert; Noble, Helen; Porter, Sam; Seres, David S.; Shields, Joanne; Swaine, Ian; Witham, Miles; Reid, Joanne
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SaveREMOTE-Neuro: co-produced recommendations to optimise remote neurology
Fuller, Patricia; Fearn, Sarah; Dace, Sally; Wollam, Amanda; Zarkali, Angeliki; Cowan, Adam; Mountney, Sam; Carr, Georgina; Eriksson, Sofia H.; Kipps, Christopher
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SaveVutrisiran Improved Outcomes Versus Placebo in Patients with Transthyretin Amyloidosis with Cardiomyopathy and Severe Chronic Kidney Disease: Post Hoc Analysis of HELIOS-B
Sheikh, Farooq H.; Dang, Julien; Fontana, Marianna; Audard, Vincent; Garcia-Pavia, Pablo; Khouri, Michel; Jobbe-Duval, Antoine; Brailovsky, Yevgeniy; Zheng, Hua; Early, Satish; Moffitt, Colleen; Yilmaz, Ali; Akyol, Nuriye
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SaveThe Endoscopic ExtraForaminal TransChoroid (EFTC) Approach in the Management of Pineal Tumors: Gross Total Resection through a Single Burr Hole
Vitulli, Francesca; Lorenzetti, Marco; Vasilica, Anca-Mihaela; Reisz, Zita; Dias, Ana; Leitch, Jane; Siddiqui, Ata; Im, Jean-Marie U. -King; Pace, Erika; Mandeville, Henry; Angelini, Paola; Carceller, Fernando; Zebian, Bassel
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SavePragmatic, open-label, multicentre, randomised controlled trial to guide initial therapy for immune checkpoint inhibitor-induced inflammatory arthritis comparing standard of care (prednisolone) to adalimumab without glucocorticoids: REACT trial protocol
Fisher, Benjamin A.; Rowe, Anna; Hodson, Chris; Wilkhu, Manpreet; Williams, Emily; Turner, Elliot; Allard, Andrew; Blake, Tim; Bombardieri, Michele; Cope, Andrew P.; Dubey, Shirish; Mankia, Kulveer; Malley, Tamir; Moore, Owen; Payne, Miranda; Plummer, Ruth; Tilby, Michael; Tillett, Tania; Wong, Ernest; Wu, Yin; Filer, Andrew; Pratt, Arthur; Pallan, Lalit; Homer, Victoria
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SaveComparing artificial intelligence and healthcare professional performance in surgical and interventional video analysis: a systematic review and meta-analysis
Rafati Fard, Amir; Williams, Simon C.; Smith, Kieran J.; Dhaliwal, Jasneet K.; Ferreira, Tomas; Das, Adrito; Starup-Hansen, Joachim; Hanrahan, John G.; Koh, Chan Hee; Khan, Danyal Z.; Stoyanov, Danail; Marcus, Hani J.
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SavePaediatric and adult neurological point-of-care ultrasound: Review of the evidence, and the UK accreditation pathway
Waraich, Manprit; Zoica, Bogdana; Alexander, Emma; Stephens, Jennie; Conway, Hannah; Griksaitis, Michael; Kirk-Bayley, Justin; Miller, Ashley; Parulekar, Prashant; Peck, Marcus; Rubino, Antonio; Wilkinson, Jonathan Nicholas
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SaveClinical guideline for ventilation-perfusion scintigraphy in pulmonary hypertension
Parthipun, Arum; Gopalan, Deepa; Gibbs, Simon; Sajjan, Rakesh; Redman, Stewart; Ellis, Beverley; Han, Sai; Hossen, Lucy; Elms, Matthew; O'brien, Joseph; Notghi, Alp; Wechalekar, Kshama
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SaveThe Cerebral Palsy Link Worker (CP LINK) study: Protocol for a feasibility study with integrated process evaluation
Smith, Kimberley J.; Ranzato, Erica; Creeger, Miriam; Stevenson, Valerie L.; Lowton, Karen; Kilbride, Cherry; Norris, Meriel; Victor, Christina; Budzynski, Thelonious McCarthy; Emma, Livingstone
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