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Integrative Multiomics in the Lung Reveals a Protective Role of Asporin in Pulmonary Arterial Hypertension Hong, Jason; Medzikovic, Lejla; Sun, Wasila; Wong, Brenda; Ruffenach, Gregoire; Rhodes, Christopher J.; Brownstein, Adam; Liang, Lloyd L.; Aryan, Laila; Li, Min; Vadgama, Arjun; Kurt, Zeyneb; Schwantes-An, Tae-Hwi; Mickler, Elizabeth A.; Graf, Stefan; Eyries, Melanie; Lutz, Katie A.; Pauciulo, Michael W.; Trembath, Richard C.; Perros, Frederic; Montani, David; Morrell, Nicholas W.; Soubrier, Florent; Wilkins, Martin R.; Nichols, William C.; Aldred, Micheala A.; Desai, Ankit A.; Tregouet, David-Alexandre; Umar, Soban; Saggar, Rajan; Channick, Richard; Tuder, Rubin M.; Geraci, Mark W.; Stearman, Robert S.; Yang, Xia; Eghbali, Mansoureh Share Save
The Clinical Development of Taldefgrobep Alfa: An Anti-Myostatin Adnectin for the Treatment of Duchenne Muscular Dystrophy Muntoni, Francesco; Byrne, Barry J.; Mcmillan, Hugh J.; Ryan, Monique M.; Wong, Brenda L.; Dukart, Juergen; Bansal, Amita; Cosson, Valerie; Dreghici, Roxana; Guridi, Maitea; Rabbia, Michael; Staunton, Hannah; Tirucherai, Giridhar S.; Yen, Karl; Yuan, Xiling; Wagner, Kathryn R. Share Save
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Moving Beyond the 2018 Minimum International Care Considerations for Osteoporosis Management in Duchenne Muscular Dystrophy (DMD): Meeting Report from the 3rd International Muscle-Bone Interactions Meeting 7th and 14th November 2022 Phung, Kim; Crabtree, Nicola; Connolly, Anne M.; Furlong, Pat; Hoffman, Eric P.; Jackowski, Stefan A.; Jayash, Soher Nagi; Johnson, Alex; Koujok, Khaldoun; Munns, Craig F.; Niks, Erik; Rauch, Frank; Schrader, Rachel; Turner, Cathy; Vroom, Elizabeth; Weber, David R.; Wong, Brenda L.; Guglieri, Michela; Ward, Leanne M.; Wong, Sze Choong Share Save
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Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy Lek, Angela; Wong, Brenda; Keeler, Allison; Blackwood, Meghan; Ma, Kaiyue; Huang, Shushu; Sylvia, Katelyn; Batista, A. Rita; Artinian, Rebecca; Kokoski, Danielle; Parajuli, Shestruma; Putra, Juan; Carreon, C. Katte; Lidov, Hart; Woodman, Keryn; Pajusalu, Sander; Spinazzola, Janelle M.; Gallagher, Thomas; Larovere, Joan; Balderson, Diane; Black, Lauren; Sutton, Keith; Horgan, Richard; Lek, Monkol; Flotte, Terence Share Save
DMD Genotypes and Motor Function in Duchenne Muscular Dystrophy Muntoni, Francesco; Signorovitch, James; Sajeev, Gautam; Lane, Henry; Jenkins, Madeline; Dieye, Ibrahima J.; Ward, Susan; McDonald, Craig; Goemans, Nathalie H.; Niks, Erik; Wong, Brenda; Servais, Laurent; Straub, Volker; Guglieri, Michela; de Groot, Imelda J. M.; Chesshyre, Mary; Tian, Cuixia Y.; Manzur, Adnan; Mercuri, Eugenio; Aartsma-Rus, Annemieke Share Save
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Parent Project Muscular Dystrophy Females with Dystrophinopathy Conference, Orlando, Florida June 26-June 27, 2019 Apkon, Susan; Kinnett, Kathi; Cripe, Linda; Duan, Dongsheng; Jackson, Jamie L.; Kornegay, Joe N.; Mah, May Ling; Nelson, Stanley F.; Rao, Vamshi; Scavina, Mena; Wong, Brenda L.; Flanigan, Kevin M. Share Save
Safety and efficacy of teriparatide treatment for severe osteoporosis in patients with Duchenne muscular dystrophy Nasomyont, N.; Keefe, C.; Tian, C.; Hornung, L.; Khoury, J.; Tilden, J. C.; Hochwalt, P.; Jackson, E.; Rybalsky, I; Wong, B. L.; Rutter, Meilan M. Share Save
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MRI vastus lateralis fat fraction predicts loss of ambulation in Duchenne muscular dystrophy Naarding, Karin J.; Reyngoudt, Harmen; van Zwet, Erik W.; Hooijmans, Melissa T.; Tian, Cuixia; Rybalsky, Irina; Shellenbarger, Karen C.; Le Louer, Julien; Wong, Brenda L.; Carlier, Pierre G.; Kan, Hermien E.; Niks, Erik H. Share Save
Electrical impedance myography for reducing sample size in Duchenne muscular dystrophy trials Leitner, Melanie L.; Kapur, Kush; Darras, Basil T.; Yang, Michele; Wong, Brenda; Pazze, Laura Dalle; Florence, Julaine; Buck, Martin; Freedman, Laura; Bohorquez, Jose; Rutkove, Seward; Zaidman, Craig Share Save
Comparison of Pulmonary Function Decline in Steroid-Treated and Steroid-Naive Patients with Duchenne Muscular Dystrophy Sawnani, Hemant; Horn, Paul S.; Wong, Brenda; Darmahkasih, Andrew; Rybalsky, Irina; Shellenbarger, Karen C.; Tian, Cuixia; Rutter, Meilan M.; Simakajornboon, Narong; Amin, Raouf; Gurbani, Neepa; Pascoe, John; Burrows, Carolyn; Khirani, Sonia; Amaddeo, Alessandro; Fauroux, Brigitte Share Save
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Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial McDonald, Craig M.; Campbell, Craig; Erazo Torricelli, Ricardo; Finkel, Richard S.; Flanigan, Kevin M.; Goemans, Nathalie; Heydemann, Peter; Kaminska, Anna; Kirschner, Janbernd; Muntoni, Francesco; Nascimento Osorio, Andres; Schara, Ulrike; Sejersen, Thomas; Shieh, Perry B.; Sweeney, H. Lee; Topaloglu, Haluk; Tulinius, Mar; Vilchez, Juan J.; Voit, Thomas; Wong, Brenda; Elfring, Gary; Kroger, Hans; Luo, Xiaohui; McIntosh, Joseph; Ong, Tuyen; Riebling, Peter; Souza, Marcio; Spiegel, Robert J.; Peltz, Stuart W.; Mercuri, Eugenio Share Save
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