Not logged inClesrovimab for Prevention of RSV Disease in Healthy Infants
Zar, Heather J.; Simoes, Eric A. F.; Madhi, Shabir A.; Ramilo, Octavio; Senders, Shelly D.; Shepard, Julie S.; Laoprasopwattana, Kamolwish; Piedrahita, Jorge; Novoa, Jose M.; Vargas, Sergio L.; Dionne, Marc; Jackowska, Teresa; Liu, Enmei; Ishihara, Yasunori; Ikeda, Kazushige; Zhang, Ying; Railkar, Radha A.; Lutkiewicz, Jeannine; Vora, Kalpit A.; Zang, Xiaowei; Maas, Brian M.; Lee, Andrew W.; Guerra, Andrea; Sinha, Anushua
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SaveStructure-guided AAV capsid evolution strategies for enhanced CNS gene delivery
Gonzalez, Trevor J.; Mitchell-Dick, Aaron; Blondel, Leo O.; Fanous, Marco M.; Hull, Joshua A.; Oh, Daniel K.; Moller-Tank, Sven; Rivera, Ruth M. Castellanos; Piedrahita, Jorge A.; Asokan, Aravind
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SaveA postnatal network of co-hepato/pancreatic stem/progenitors in the biliary trees of pigs and humans (vol 8, 40, 2023)
Zhang, Wencheng; Wang, Xicheng; Lanzoni, Giacomo; Wauthier, Eliane; Simpson, Sean; Ezzell, Jennifer Ashley; Allen, Amanda; Suitt, Carolyn; Krolik, Jonah; Jhirad, Alexander; Dominguez-Bendala, Juan; Cardinale, Vincenzo; Alvaro, Domenico; Overi, Diletta; Gaudio, Eugenio; Sethupathy, Praveen; Carpino, Guido; Adin, Christopher; Piedrahita, Jorge A.; Mathews, Kyle; He, Zhiying; Reid, Lola McAdams
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SaveA postnatal network of co-hepato/pancreatic stem/progenitors in the biliary trees of pigs and humans
Zhang, Wencheng; Wang, Xicheng; Lanzoni, Giacomo; Wauthier, Eliane; Simpson, Sean; Ezzell, Jennifer Ashley; Allen, Amanda; Suitt, Carolyn; Krolik, Jonah; Jhirad, Alexander; Dominguez-Bendala, Juan; Cardinale, Vincenzo; Alvaro, Domenico; Overi, Diletta; Gaudio, Eugenio; Sethupathy, Praveen; Carpino, Guido; Adin, Christopher; Piedrahita, Jorge A.; Mathews, Kyle; He, Zhiying; Reid, Lola McAdams
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SaveA LGR5 reporter pig model closely resembles human intestine for improved study of stem cells in disease
Schaaf, Cecilia R.; Polkoff, Kathryn M.; Carter, Amber; Stewart, Amy S.; Sheahan, Breanna; Freund, John; Ginzel, Joshua; Snyder, Joshua C.; Roper, Jatin; Piedrahita, Jorge A.; Gonzalez, Liara M.
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SaveCross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editing
Gonzalez, Trevor J.; Simon, Katherine E.; Blondel, Leo O.; Fanous, Marco M.; Roger, Angela L.; Maysonet, Maribel Santiago; Devlin, Garth W.; Smith, Timothy J.; Oh, Daniel K.; Havlik, L. Patrick; Castellanos Rivera, Ruth M.; Piedrahita, Jorge A.; ElMallah, Mai K.; Gersbach, Charles A.; Asokan, Aravind
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SavePatch grafting of organoids of stem/progenitors into solid organs can correct genetic-based disease states
Zhang, Wencheng; Wauthier, Eliane; Lanzoni, Giacomo; Hani, Homayoun; Yi, Xianwen; Overi, Diletta; Shi, Lei; Simpson, Sean; Allen, Amanda; Suitt, Carolyn; Ezzell, Jennifer Ashley; Alvaro, Domenico; Cardinale, Vincenzo; Gaudio, Eugenio; Carpino, Guido; Prestwich, Glenn; Dominguez-Bendala, Juan; Gerber, David; Mathews, Kyle; Piedrahita, Jorge; Adin, Christopher; Sethupathy, Praveen; He, Zhiying; Reid, Lola M.
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SaveLGR5 is a conserved marker of hair follicle stem cells in multiple species and is present early and throughout follicle morphogenesis
Polkoff, Kathryn M.; Gupta, Nithin K.; Green, Adrian J.; Murphy, Yanet; Chung, Jaewook; Gleason, Katherine L.; Simpson, Sean G.; Walker, Derek M.; Collins, Bruce; Piedrahita, Jorge A.
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SavePatch grafting, strategies for transplantation of organoids into solid organs such as liver
Zhang, Wencheng; Lanzoni, Giacomo; Hani, Homayoun; Overi, Diletta; Cardinale, Vincenzo; Simpson, Sean; Pitman, Wendy; Allen, Amanda; Yi, Xianwen; Wang, Xicheng; Gerber, David; Prestwich, Glenn; Lozoya, Oswaldo; Gaudio, Eugenio; Alvaro, Domenico; Tokaz, Debra; Dominguez-Bendala, Juan; Adin, Christopher; Piedrahita, Jorge; Mathews, Kyle; Sethupathy, Praveen; Carpino, Guido; He, Zhiying; Wauthier, Eliane; Reid, Lola M.
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SaveHigh mobility group A2 (HMGA2) deficiency in pigs leads to dwarfism, abnormal fetal resource allocation, and cryptorchidism
Chung, Jaewook; Zhang, Xia; Collins, Bruce; Sper, Renan B.; Gleason, Katherine; Simpson, Sean; Koh, Sehwon; Sommer, Jeffrey; Flowers, William L.; Petters, Robert M.; Piedrahita, Jorge A.
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