arrow
Back
B

Brigitte C. Widemann

national cancer institute

71H-index
679Paper Count
1.6WCitation Count
Published Papers 118
Publication Date
New Approaches to Clinical Trials for Rare Diseases: Decentralized Trial Design for Neurofibromatosis Type 1 and Schwannomatosis
errCancers
IF4.4
err2026-08-01
err0
errOAAI
errVanessa L. Merker; Shivani Ahlawat; Robert A. Avery; Diana Bradford; Andrea M. Gross; Jennifer Janusz; Andrés J. Lessing; Linda Manth; Miranda L. McManus; Beverly Oberlander; Dominique C. Pichard; William Riter; Kavita Y. Sarin; Steven Sheard; Russell Taylor Sundby; Karin S. Walsh; Pamela L. Wolters; Brigitte C. Widemann; Scott R. Plotkin
errShare
errSave
Malignant peripheral nerve sheath tumor development during MEK inhibitor treatment: A pre-clinical study and a clinical case series
err2026-07-11
err0
errOAAI
errAndrea M Gross; Steven D Rhodes; Anne Dufek; Eva Dombi; Andrea Baldwin; John F Shern; Russell Taylor Sundby; Xiyuan Zhang; Melike Pekmezci; D Wade Clapp; Joseph G Pressey; Brian D Weiss; Miriam Bornhorst; AeRang Kim; Michael J Fisher; Brigitte C Widemann; null
errShare
errSave
Trabectedin and low-dose irinotecan to target EWS::FLI1 in Ewing sarcoma: a phase 1/2 trial
err2026-04-16
err0
PREAI
errPatrick J. Grohar; Rachel Heise; Mary Frances Wedekind; Karla Ballman; Leo Mascarenhas; Steven G. DuBois; Robert G. Maki; Elissa A. Boguslawski; Jenna M. Gedminas; Elizabeth R. Wilson; Elaine Thomas; Blair Segers; Lea F. Surrey; Cora Ricker; Kelly Klega; Fariba Navid; Gretchen Y. Lam; Stephanie The; Rebecca Kaufman; Ryan D. Roberts; Masanori Hayashi; Esther Mena; Lindsey Overman; Cody Peer; Keith Schmidt; Mark S. Diamond; William D. Figg; Rochelle Bagatell; M. Liza Lindenberg; Peter L. Choyke; Brian D. Crompton; Brigitte C. Widemann; John W. Glod; Theodore W. Laetsch; Denise K. Reinke; Rashmi Chugh
errShare
errSave
The prostate is a common site of disease in patients with MEN2B and medullary thyroid carcinoma
err2026-01-01
err0
PREAI
errKraft, Ira L.; Akshintala, Srivandana; Gross, Andrea; Dombi, Eva; Turkbey, Baris; Bednarova, Sandra; Ward, John F.; Yedururi, Sireesha; Merino, Maria; Pinto, Peter A.; Widemann, Brigitte C.; Shern, Jack F.; Waguespack, Steven G.; Glod, John
errShare
errSave
The impact of focused federal initiatives on pediatric cancer research
errCANCER
IF5.1
err2025-11-15
err0
errOAAI
errJagu, Subhashini; Smith, Malcolm A.; Seibel, Nita L.; Tonorezos, Emily S.; Widemann, Brigitte C.; Gibbons, Holly A.; Holohan, Mary K.; Ababiya, Ziky A.; Guidry Auvil, Jaime M.; Lowy, Douglas R.; Doroshow, James H.; Lubenow, Anne E.; Reaman, Gregory H.
errShare
errSave
Investigating fatigue in adults with neuroendocrine neoplasms using a biopsychosocial model
err2025-10-17
err0
PREAI
errSarah W. Peters; Pamela L. Wolters; Jaydira Del Rivero; Mary Frances Wedekind; Karlyne M. Reilly; Crystal Flowers; Brigitte Widemann; Robin Lockridge
errShare
errSave
The spectrum of pathogenic NF1 variants in participants enrolling on clinical trials of MEK inhibitors for plexiform neurofibroma
err2025-10-15
err0
PREAI
errChelsea Kotch; Alicia Gomes; Krista S. Schatz; Eva Dombi; Symone Brown; Andrea M. Gross; Mélanie Alves; Sébastien Perreault; Sabine Mueller; Alyssa T. Reddy; Carlos Romo; Miriam Bornhorst; James Tonsgard; Brian D. Weiss; Brigitte Widemann; Michael J. Fisher
errShare
errSave
Long-term Ocular Safety in Children Treated with MAPK Pathway Inhibitor Therapy
err2025-10-10
err0
PREAI
errRobert A. Avery; Andrea M. Gross; Chantal Cousineau-Krieger; Tiarnán D.L. Keenan; Taylor McManus; Connor J. Dallas; Christopher Hampton; Andrea Baldwin; Fangming Jin; Kara Heisey; Kristen Zeller; Grant T. Liu; Chinwe Okeagu; Rachel Bishop; Michael J. Fisher; Brigitte C. Widemann; M.Teresa Magone
errShare
errSave
How to foster new treatment development in ultra-rare tumours? Joint EMA-EORTC multi-stakeholder workshops on ultra-rare sarcomas as a model for rare cancers
err2025-08-06
err0
PREAI
errSilvia Stacchiotti; Pan Pantziarka; Hugh Leonard; Caroline Voltz; Laura Abatedaga; Gauthier Bouche; Christelle Bouygues; Judith V.M.G. Bovee; Winette T.A. Van der Graaf; Teresa De Rojas; Lorenzo D’Ambrosio; Martha Donoghue; Harald Enzmann; Gerry Feeney; Paolo Foggi; Anna Maria Frezza; Ralf Herold; Robin L. Jones; Bernd Kasper; Kit Roes; Sandrine Marreaud; Rosalba Miceli; Denise Robinson; Josh Sommer; William D. Tap; Caitlin Tydings; Annalisa Trama; Winan Van Houdt; Gerard van Oortmerssen; Andrew J. Wagner; Brigitte Widemann; Hans Gelderblom; Alessandro Gronchi; Andrea Napolitano; Armelle Dufresne; Elena R. Fumagalli; Giacomo Baldi; Gloria Marquina; Hanna Koseła-Paterczyk; Javier Broto Martin Javier; Niels Junker; Piotr Rutkowski; Wim J.G. Oyen; Denis Lacombe; Francesco Pignatti; Pierre Demolis
errShare
errSave
Treatment of Cutaneous Neurofibromas in Neurofibromatosis Type 1 With MEK Inhibitor Selumetinib A Nonrandomized Clinical Trial
err2025-02-26
err0
PREAI
errGross, Andrea M.; Reid, Olivia H.; Baldwin, Lauren A.; Cannon, Ashley; Choo-Wosoba, Hyoyoung; Steinberg, Seth M.; Lobbous, Mina; Wolters, Pamela L.; Pichard, Dominique C.; Tibery, Cecilia M.; Dombi, Eva; Derdak, Joanne; Widemann, Brigitte C.; Korf, Bruce R.
errShare
errSave
errShare
errSave
Malignant peripheral nerve sheath tumors in neurofibromatosis type 1 arise from distinct nodular lesions: A retrospective imaging analysis
err2025-01-01
err0
errOAAI
errSalamon, Johannes; Widemann, Brigitte C.; Gross, Andrea M.; Baldwin, Andrea; Farschtschi, Said C.; Mautner, Victor F.; Dombi, Eva
errShare
errSave
Anthropometric measurements of children with neurofibromatosis type I: impact of plexiform neurofibroma volume and treatment
err2024-08-28
err1
PREAI
errLemberg, Kathryn M.; Gross, Andrea M.; Sproule, Lauren M.; Liewehr, David J.; Dombi, Eva; Baldwin, Andrea; Steinberg, Seth M.; Bornhorst, Miriam; Lodish, Maya; Blakeley, Jaishri O.; Widemann, Brigitte C.
errShare
errSave
snRNA-seq of human cutaneous neurofibromas before and after selumetinib treatment implicates role of altered Schwann cell states, inter-cellular signaling, and extracellular matrix in treatment response
err2024-06-21
err1
errOAAI
errChurch, Cameron; Fay, Christian X.; Kriukov, Emil; Liu, Hui; Cannon, Ashley; Baldwin, Lauren Ashley; Crossman, David K.; Korf, Bruce; Wallace, Margaret R.; Gross, Andrea M.; Widemann, Brigitte C.; Kesterson, Robert A.; Baranov, Petr; Wallis, Deeann
errShare
errSave
MANAGEMENT TRENDS OF MEK INHIBITOR DERMATOLOGIC ADVERSE EVENTS FOR NEUROFIBROMATOSIS PATIENTS
err2024-06-18
err0
errOAAI
errParisi, Rose; Dhulipalla, Sanjana; Widemann, Brigitte; Pichard, Dominique C.; Gross, Andrea; Weintraub, Lauren
errShare
errSave
LOWER BODY SURFACE AREA IS ASSOCIATED WITH INCREASED LIKELIHOOD OF PLEXIFORM NEUROFIBROMA RESPONSE TO MEK INHIBITION
err2024-06-18
err0
errOAAI
errKotch, Chelsea; Dombi, Eva; Gross, Andrea; Weiss, Brian; Mueller, Sabine; Reddy, Alyssa T.; Perreault, Sebastien; Alves, Melanie; Brown, Symone; Li, Yimei; Widemann, Brigitte C.; Fisher, Michael J.
errShare
errSave
Virtual multi-institutional tumor board: a strategy for personalized diagnoses and management of rare CNS tumors
err2024-03-01
err1
errOAAI
errRogers, James L.; Wall, Thomas; Acquaye-Mallory, Alvina A.; Boris, Lisa; Kim, Yeonju; Aldape, Kenneth; Quezado, Martha M.; Butman, John A.; Smirniotopoulos, James G.; Chaudhry, Huma; Tsien, Christina I.; Chittiboina, Prashant; Zaghloul, Kareem; Aboud, Orwa; Avgeropoulos, Nicholas G.; Burton, Eric C.; Cachia, David M.; Dixit, Karan S.; Drappatz, Jan; Dunbar, Erin M.; Forsyth, Peter; Komlodi-Pasztor, Edina; Mandel, Jacob; Ozer, Byram H.; Lee, Eudocia Q.; Ranjan, Surabhi; Lukas, Rimas V.; Raygada, Margarita; Salacz, Michael E.; Smith-Cohn, Matthew A.; Snyder, James; Soldatos, Ariane; Theeler, Brett J.; Widemann, Brigitte C.; Camphausen, Kevin A.; Heiss, John D.; Armstrong, Terri S.; Gilbert, Mark R.; Penas-Prado, Marta
errShare
errSave
Selumetinib for children with neurofibromatosis type 1 and plexiform neurofibromas: A plain language summary of SPRINT
err2024-02-22
err0
errOAAI
errGross, Andrea M.; Achee, Colette; Hart, Sarah E.; Brewer, Lindsay; Baldwin, Andrea; Wolters, Pamela L.; Widemann, Brigitte C.
errShare
errSave
Imaging as an early biomarker to predict sensitivity to everolimus for progressive NF2-related vestibular schwannoma
err2024-02-19
err2
errOAAI
errNghiemphu, Phioanh Leia; Vitte, Jeremie; Dombi, Eva; Nguyen, Thien; Wagle, Naveed; Ishiyama, Akira; Sepahdari, Ali R.; Cachia, David; Widemann, Brigitte C.; Brackmann, Derald E.; Doherty, Joni K.; Kalamarides, Michel; Giovannini, Marco
errShare
errSave
Understanding rare cancers in Hispanic/Latinx populations: Insights from the MyPART natural history study of rare solid tumors
err2023-12-01
err0
PREAI
errPineda, Juan C. Fierro; Ahmed, Shadin; Reilly, Karlyne; Lockridge, Robin; Raygada, Margarita; Thomas, Barbara; Glod, John; Sandier, Abby; Widemann, Brigitte; Malone, Mary Frances Wedekind
errShare
errSave