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Utility of patient subgrouping in ALS clinical trials: a World Federation of Neurology white paper Rosenfeld, Jeffrey; Abrahams, Sharon; Mchutchinson, Caroline; Ajroud-Driss, Senda; Weber, Markus; Paganoni, Sabrina; Mitsumoto, Hiroshi; Genge, Angela; Grosskreutz, Julian; Van Den Berg, Leonard; Andrews, Jinsy; Kiernan, Matthew C. Share Save
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Reldesemtiv in Amyotrophic Lateral Sclerosis: Results From the COURAGE-ALS Randomized Clinical Trial Shefner, Jeremy M.; Cudkowicz, Merit E.; Genge, Angela; Hardiman, Orla; Al-Chalabi, Ammar; Andrews, Jinsy A.; Chio, Adriano; Corcia, Philippe; Couratier, Philippe; de Carvalho, Mamede; Heiman-Patterson, Terry; Henderson, Robert D.; Ingre, Caroline; Johnston, Wendy; Ludolph, Albert; Maragakis, Nicholas J.; Miller, Timothy M.; Mora, Jesus S.; Petri, Susanne; Simmons, Zachary; van den Berg, Leonard H.; Zinman, Lorne; Kupfer, Stuart; Malik, Fady I.; Meng, Lisa; Simkins, Tyrell J.; Wei, Jenny; Wolff, Andrew A.; Rudnicki, Stacy A.; COURAGE ALS Study Grp Share Save
Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis, A Randomized Clinical Trial Paganoni, Sabrina; Fournier, Christina N.; Macklin, Eric A.; Chibnik, Lori B.; Quintana, Melanie; Saville, Benjamin R.; Detry, Michelle A.; Vestrucci, Matteo; Marion, Joe; Mcglothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A.; Yu, Hong; Sherman, Alexander V.; Shefner, Jeremy M.; Hall, Meghan; Kittle, Gale; Berry, James D.; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H.; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J.; Simmons, Zachary; Miller, Timothy M.; Olney, Nicholas; Weiss, Michael D.; Goutman, Stephen A.; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A.; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S.; Arcila-Londono, Ximena; Jackson, Carlayne E.; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B.; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Kasarskis, Edward J.; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; Mcilduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A.; Cohen, Jeffrey A.; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R.; Wymer, James P.; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L.; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W.; Cudkowicz, Merit E. Share Save
Design and Statistical Innovations in a Platform Trial for Amyotrophic Lateral Sclerosis Quintana, Melanie R.; Saville, Benjamin; Vestrucci, Matteo A.; Detry, Michelle; Chibnik, Lori; Shefner, Jeremy D.; Berry, James; Chase, Marianne; Andrews, Jinsy V.; Sherman, Alexander; Yu, Hong; Drake, Kristin; Cudkowicz, Merit; Paganoni, Sabrina A.; Macklin, Eric; HEALEY ALS Platform Trial Study Grp Share Save
Evidence for Survival Benefit in ALS with CNM-Au8 Treatment Across Three Study Populations Berry, James; Maragakis, Nicholas; Paganoni, Sabrina; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Detry, Michelle; Menon, Parvathi; Huynh, William; Mahoney, Colin; Stommel, Elijah; Hall, Meghan; Connolly, Mariah; Kittle, Gale; Chase, Marianne; Sherman, Alexander; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; Glanzman, Robert; Hotchkin, Michael; Vucic, Steve; Kiernan, Matthew; Cudkowicz, Merit Share Save
Results from the first four regimens of the HEALEY ALS Platform Trial Paganoni, Sabrina; Berry, James; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Fournier, Christina; Babu, Suma; Maragakis, Nicholas; Oskarsson, Bjorn; Detry, Michelle; Chase, Marianne; Sherman, Alex; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; McGlothlin, Anna; Marion, Joseph; Duda, Petra; Harvey, Brittany; Qureshi, Irfan; Donohue, Mary; Granit, Volkan; Grossman, Katheryn; Glanzman, Robert; Hotchkin, Michael; Goldberg, Y. Paul; Leitner, Melanie; Hayden, Michael; Cudkowicz, Merit Share Save
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Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS Miller, Timothy M.; Cudkowicz, Merit E.; Genge, Angela; Shaw, Pamela J.; Sobue, Gen; Bucelli, Robert C.; Chio, Adriano; Van Damme, Philip; Ludolph, Albert C.; Glass, Jonathan D.; Andrews, Jinsy A.; Babu, Suma; Benatar, Michael; McDermott, Christopher J.; Cochrane, Thos; Chary, Sowmya; Chew, Sheena; Zhu, Han; Wu, Fan; Nestorov, Ivan; Graham, Danielle; Sun, Peng; McNeill, Manjit; Fanning, Laura; Ferguson, Toby A.; Fradette, Stephanie Share Save
Design of a Randomized, Placebo-Controlled, Phase 3 Trial of Tofersen Initiated in Clinically Presymptomatic SOD1 Variant Carriers: the ATLAS Study (May, 10.1007/s13311-022-01237-4, 2022) Benatar, Michael; Wuu, Joanne; Andersen, Peter M.; Bucelli, Robert C.; Andrews, Jinsy A.; Otto, Markus; Farahany, Nita A.; Harrington, Elizabeth A.; Chen, Weiping; Mitchell, Adele A.; Ferguson, Toby; Chew, Sheena; Gedney, Liz; Oakley, Sue; Heo, Jeong; Chary, Sowmya; Fanning, Laura; Graham, Danielle; Sun, Peng; Liu, Yingying; Wong, Janice; Fradette, Stephanie Share Save
Design of a Randomized, Placebo-Controlled, Phase 3 Trial of Tofersen Initiated in Clinically Presymptomatic SOD1 Variant Carriers: the ATLAS Study Benatar, Michael; Wuu, Joanne; Andersen, Peter M.; Bucelli, Robert C.; Andrews, Jinsy A.; Otto, Markus; Farahany, Nita A.; Harrington, Elizabeth A.; Chen, Weiping; Mitchell, Adele A.; Ferguson, Toby; Chew, Sheena; Gedney, Liz; Oakley, Sue; Heo, Jeong; Chary, Sowmya; Fanning, Laura; Graham, Danielle; Sun, Peng; Liu, Yingying; Wong, Janice; Fradette, Stephanie Share Save
The importance of offering early genetic testing in everyone with amyotrophic lateral sclerosis Salmon, Kristiana; Kiernan, Matthew C.; Kim, Seung H.; Andersen, Peter M.; Chio, Adriano; van den Berg, Leonard H.; Van Damme, Philip; Al-Chalabi, Ammar; Lillo, Patricia; Andrews, Jinsy A.; Genge, Angela Share Save
Adaptive Platform Trials to Transform Amyotrophic Lateral Sclerosis Therapy Development Paganoni, Sabrina; Berry, James D.; Quintana, Melanie; Macklin, Eric; Saville, Benjamin R.; Detry, Michelle A.; Chase, Marianne; Sherman, Alexander, V; Yu, Hong; Drake, Kristin; Andrews, Jinsy; Shefner, Jeremy; Chibnik, Lori B.; Vestrucci, Matteo; Cudkowicz, Merit E. Share Save
Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study (vol 18, pg 1127, 2021) Rudnicki, Stacy A.; Andrews, Jinsy A.; Duong, Tina; Cockroft, Bettina M.; Malik, Fady I.; Meng, Lisa; Wei, Jenny; Wolff, Andrew A.; Genge, Angela; Johnson, Nicholas E.; Tesi-Rocha, Carolina; Connolly, Anne M.; Darras, Basil T.; Felice, Kevin; Finkel, Richard S.; Shieh, Perry B.; Mah, Jean K.; Statland, Jeffrey; Campbell, Craig; Habib, Ali A.; Kuntz, Nancy L.; Oskoui, Maryam; Day, John W. Share Save
Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study Rudnicki, Stacy A.; Andrews, Jinsy A.; Duong, Tina; Cockroft, Bettina M.; Malik, Fady I.; Meng, Lisa; Wei, Jenny; Wolff, Andrew A.; Genge, Angela; Johnson, Nicholas E.; Tesi-Rocha, Carolina; Connolly, Anne M.; Darras, Basil T.; Felice, Kevin; Shieh, Perry B.; Mah, Jean K.; Statland, Jeffrey; Campbell, Craig; Habib, Ali A.; Kuntz, Nancy L.; Oskoui, Maryam; Day, John W. Share Save
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