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Long-term lumasiran therapy final results from a Phase 2 open-label extension study in primary hyperoxaluria Frishberg, Yaacov; Groothoff, Jaap W.; Hulton, Sally-Anne; Harambat, Jerome; Hogan, Julien; Sellier-Leclerc, Anne-Laure; Hayes, Wesley; Coenen, Martin J.; Willey, Richard; Gansner, John M.; Magen, Daniella Share Save
Long-term efficacy and safety in the 60-month, Phase 3 ILLUMINATE-B trial of lumasiran in infants and young children with primary hyperoxaluria type 1 Frishberg, Yaacov; Hayes, Wesley; Ben-Shalom, Efrat; Shasha-Lavsky, Hadas; Sas, David; Michael, Mini; Sellier-Leclerc, Anne-Laure; Hogan, Julien; Willey, Richard; Gansner, John; Kaspar, Cristin; Magen, Daniella Share Save
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Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1 : Results from a Phase III Clinical Trial Saland, Jeffrey M.; Lieske, John C.; Groothoff, Jaap W.; Frishberg, Yaacov; Shasha-Lavsky, Hadas; Magen, Daniella; Moochhala, Shabbir H.; Simkova, Eva; Coenen, Martin; Hayes, Wesley; Hogan, Julien; Sellier-Leclerc, Anne-Laure; Willey, Richard; Gansner, John M.; Hulton, Sally -Anne Share Save
Moral clarity at WHO needs to be clearer Beyar, Rafael; Blazer, Shraga; Breuer, Edward; Carmi, Rivka; Ciechanover, Aaron; Clarfield, A. Mark; Glick, Shimon; Magen, Daniella; Manor, Orly; Paltiel, Ora; Skorecki, Karl Share Save
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Diagnostic Utility of Exome Sequencing Among Israeli Children With Kidney Failure Ben-Moshe, Yishay; Shlomovitz, Omer; Atias-Varon, Danit; Haskin, Orly; Ben-Shalom, Efrat; Lavsky, Hadas Shasha; Volovelsky, Oded; Mane, Shrikant; Ben-Ruby, Dror; Chowers, Guy; Skorecki, Karl; Borovitz, Yael; Kagan, Maayan; Mor, Nofar; Khavkin, Yulia; Tzvi-Behr, Shimrit; Pollack, Shirley; Toder, Moran Plonsky; Geylis, Michael; Schnapp, Aviad; Becker-Cohen, Rachel; Weissman, Irith; Schreiber, Ruth; Davidovits, Miriam; Frishberg, Yaacov; Magen, Daniella; Barel, Ortal; Vivante, Asaf Share Save
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Lumasiran for Advanced Primary Hyperoxaluria Type 1: Phase 3 ILLUMINATE-C Trial Michael, Mini; Groothoff, Jaap W.; Shasha-Lavsky, Hadas; Lieske, John C.; Frishberg, Yaacov; Simkova, Eva; Sellier-Leclerc, Anne-Laure; Devresse, Arnaud; Guebre-Egziabher, Fitsum; Bakkaloglu, Sevcan A.; Mourani, Chebl; Saqan, Rola; Singer, Richard; Willey, Richard; Habtemariam, Bahru; Gansner, John M.; Bhan, Ishir; McGregor, Tracy; Magen, Daniella Share Save
Dialysis in Israeli Children between 1990 and 2020: Trends and International Comparisons Regev-Epstein, Lilach C. C.; Frishberg, Yaacov; Davidovits, Miriam; Landau, Daniel; Magen, Daniella; Weismann, Irit; Stern-Zimmer, Michal; Beckerman, Pazit; Keinan-Boker, Lital; Calderon-Margalit, Ronit; Vivante, Asaf Share Save
Phase 3 trial of lumasiran for primary hyperoxaluria type 1: A new RNAi therapeutic in infants and young children Sas, David J.; Magen, Daniella; Hayes, Wesley; Shasha-Lavsky, Hadas; Michael, Mini; Schulte, Indra; Sellier-Leclerc, Anne-Laure; Lu, Jiandong; Seddighzadeh, Ali; Habtemariam, Bahru; McGregor, Tracy L.; Fujita, Kenji P.; Frishberg, Yaacov Share Save
Randomized Clinical Trial on the Long-Term Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1 Hulton, Sally A.; Groothoff, Jaap W.; Frishberg, Yaacov; Koren, Michael J.; Overcash, J. Scott; Sellier-Leclerc, Anne-Laure; Shasha-Lavsky, Hadas; Saland, Jeffrey M.; Hayes, Wesley; Magen, Daniella; Moochhala, Shabbir H.; Coenen, Martin; Simkova, Eva; Garrelfs, Sander F.; Sas, David J.; Meliambro, Kristin A.; Ngo, Taylor; Sweetser, Marianne T.; Habtemariam, Bahru A.; Gansner, John M.; McGregor, Tracy L.; Lieske, John C. Share Save
Phase 1/2 Study of Lumasiran for Treatment of Primary Hyperoxaluria Type 1 A Placebo-Controlled Randomized Clinical Trial Frishberg, Yaacov; Deschenes, Georges; Groothoff, Jaap W.; Hulton, Sally-Anne; Magen, Daniella; Harambat, Jerome; van't Hoff, William G.; Lorch, Ulrike; Milliner, Dawn S.; Lieske, John C.; Haslett, Patrick; Garg, Pushkal P.; Vaishnaw, Akshay K.; Talamudupula, Sandeep; Lu, Jiandong; Habtemariam, Bahru A.; Erbe, David, V; McGregor, Tracy L.; Cochat, Pierre Share Save
A Novel Homozygous In-Frame Deletion in Complement Factor 3 Underlies Early-Onset Autosomal Recessive Atypical Hemolytic Uremic Syndrome-Case Report Pollack, Shirley; Eisenstein, Israel; Mory, Adi; Paperna, Tamar; Ofir, Ayala; Baris-Feldman, Hagit; Weiss, Karin; Veszeli, Nora; Csuka, Dorottya; Shemer, Revital; Glaser, Fabian; Prohaszka, Zoltan; Magen, Daniella Share Save
Lumasiran, an RNAi Therapeutic for Primary Hyperoxaluria Type 1 Garrelfs, Sander F.; Frishberg, Yaacov; Hulton, Sally A.; Koren, Michael J.; O'Riordan, William D.; Cochat, Pierre; Deschenes, Georges; Shasha-Lavsky, Hadas; Saland, Jeffrey M.; van't Hoff, William G.; Fuster, Daniel G.; Magen, Daniella; Moochhala, Shabbir H.; Schalk, Gesa; Simkova, Eva; Groothoff, Jaap W.; Sas, David J.; Meliambro, Kristin A.; Lu, Jiandong; Sweetser, Marianne T.; Garg, Pushkal P.; Vaishnaw, Akshay K.; Gansner, John M.; McGregor, Tracy L.; Lieske, John C. Share Save