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James Hamilton

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21H-index
140Paper Count
3.1KCitation Count
Published Papers 20
Publication Date
Zodasiran, an RNAi therapeutic targeting ANGPTL3, for treating patients with homozygous familial hypercholesterolaemia (GATEWAY): an open-label, randomised, phase 2 trial
err2025-12-18
err0
PREAI
errFrederick J Raal; Jean Bergeron; Daniel Gaudet; Robert S Rosenson; David R Sullivan; Traci Turner; Robert A Hegele; Christie M Ballantyne; Joshua W Knowles; Nicholas J Leeper; Ira J Goldberg; Rong Zhou; Ma'an Muhsin; Jennifer Hellawell; James Hamilton; Gerald F Watts
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A Clinical-Stage Inhaled RNAi Therapeutic For Pulmonary Inflammation Mediates Durable RAGE Silencing In Nonhuman Primates (NHP)
err2023-10-27
err1
PREAI
errKasahara, David; Klossowski, Szymon; Turner, Ben; Hamilton, Holly; Reed, Taylor; Pei, Tao; Hamilton, James; Bush, Erik
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Late Breaking Abstract - A first-in-human study of ARO-RAGE, an RNAi therapy designed to silence pulmonary RAGE expression
err2023-10-27
err2
PREAI
errO'Carroll, Mark; Huetsch, John; Hamilton, James; Moser, Lindsey; Alagarsamy, Sudar; Salathe, Matthias
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Silencing TSLP expression with a lungtargeted RNAi molecule suppresses pulmonary allergic inflammation
err2023-10-27
err0
PREAI
errYuan, Tingting; Klossowski, Szymon; Afrazi, Maria; Hamilton, Holly; Hegge, Julia; Hamilton, James; Pei, Tao; Bush, Erik
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A Lung-Targeted RNAi Therapeutics Delivery Platform Compatible With Subcutaneous (s.c.) Administration Mediates Pulmonary RAGE Silencing In Rodents And Nonhuman Primates
err2023-10-27
err1
PREAI
errKasahara, David; Turner, Ben; Hamilton, Holly; Reed, Taylor; Klossowski, Szymon; Williams, Clay; Cousineau, Christopher; Chen, Jing; Hegge, Julia; Branca-Afrazi, Maria; Hamilton, James; Pei, Tao; Bush, Erik
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A clinical-stage RNAi therapeutic candidate for IPF mediates durable MMP7 silencing in nonhuman primates and human lung tissue
err2023-10-27
err2
PREAI
errYuan, Tingting; Klossowski, Szymon; Afrazi, Maria; Hamilton, Holly; Hegge, Julia; Hamilton, James; Pei, Tao; Bush, Erik
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A phase I/II study of ARO-HSD, an RNA interference therapeutic, for the treatment of non-alcoholic steatohepatitis
err2023-04-01
err26
PREAI
errMak, Lung-Yi; Gane, Ed; Schwabe, Christian; Yoon, Ki Tae; Heo, Jeong; Scott, Russell; Lee, Jeong-Hoon; Lee, Jung Il; Kweon, Young Oh; Weltman, Martin; Harrison, Stephen A.; Neuschwander-Tetri, Brent A.; Cusi, Kenneth; Loomba, Rohit; Given, Bruce D.; Christianson, Dawn R.; Garcia-Medel, Eric; Yi, Min; Hamilton, James; Yuen, Man-Fung
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Combination treatments including the small-interfering RNA JNJ-3989 induce rapid and sometimes prolonged viral responses in patients with CHB
err2022-11-01
err52
errOAAI
errYuen, Man-Fung; Locarnini, Stephen; Lim, Tien Huey; Strasser, Simone, I; Sievert, William; Cheng, Wendy; Thompson, Alex J.; Given, Bruce D.; Schluep, Thomas; Hamilton, James; Biermer, Michael; Kalmeijer, Ronald; Beumont, Maria; Lenz, Oliver; De Ridder, Filip; Cloherty, Gavin; Wong, Danny Ka-Ho; Schwabe, Christian; Jackson, Kathy; Lai, Ching Lung; Gish, Robert G.; Gane, Edward
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Fazirsiran for Liver Disease Associated with Alpha1-Antitrypsin Deficiency
err2022-08-11
err53
errOAAI
errStrnad, Pavel; Mandorfer, Mattias; Choudhury, Gourab; Griffiths, William; Trautwein, Christian; Loomba, Rohit; Schluep, Thomas; Chang, Ting; Yi, Min; Given, Bruce D.; Hamilton, James C.; Martin, Javier San; Teckman, Jeffery H.
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Development of an RNAi therapeutic for alpha-1-antitrypsin liver disease
err2020-06-18
err41
errOAAI
errWooddell, Christine I.; Blomenkamp, Keith; Peterson, Ryan M.; Subbotin, Vladimir M.; Schwabe, Christian; Hamilton, James; Chu, Qili; Christianson, Dawn R.; Hegge, Julia O.; Kolbe, John; Hamilton, Holly L.; Branca-Afrazi, Maria F.; Given, Bruce D.; Lewis, David L.; Gane, Edward; Kanner, Steven B.; Teckman, Jeffrey H.
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RNA Interference Therapy With ARC-520 Results in Prolonged Hepatitis B Surface Antigen Response in Patients With Chronic Hepatitis B Infection
err2020-04-23
err91
errOAAI
errYuen, Man-Fung; Schiefke, Ingolf; Yoon, Jung-Hwan; Ahn, Sang Hoon; Heo, Jeong; Kim, Ju Hyun; Chan, Henry Lik Yuen; Yoon, Ki Tae; Klinker, Hartwig; Manns, Michael; Petersen, Joerg; Schluep, Thomas; Hamilton, James; Given, Bruce D.; Ferrari, Carlo; Lai, Ching-Lung; Locarnini, Stephen A.; Gish, Robert G.
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Role of angiopoietin-like protein 3 in sugar-induced dyslipidemia in rhesus macaques: suppression by fish oil or RNAi[S]
err2020-03-01
err12
errOAAI
errButler, Andrew A.; Graham, James L.; Stanhope, Kimber L.; Wong, So; King, Sarah; Bremer, Andrew A.; Krauss, Ronald M.; Hamilton, James; Havel, Peter J.
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Fructose-induced hypertriglyceridemia in rhesus macaques is attenuated with fish oil or ApoC3 RNA interference
err2019-04-01
err20
errOAAI
errButler, Andrew A.; Price, Candice A.; Graham, James L.; Stanhope, Kimber L.; King, Sarah; Hung, Yu-Han; Sethupathy, Praveen; Wong, So; Hamilton, James; Krauss, Ronald M.; Bremer, Andrew A.; Havel, Peter J.
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Short term RNA interference therapy in chronic hepatitis B using JNJ-3989 brings majority of patients to HBsAg < 100 IU/ml threshold
err2019-04-01
err24
PREAI
errYuen, Man-Fung; Locarnini, Stephen; Lim, Tien Huey; Strasser, Simone; Sievert, William; Cheng, Wendy; Thompson, Alex; Given, Bruce; Schluep, Thomas; Hamilton, James; Cloherty, Gavin; Wong, Danny; Schwabe, Christian; Jackson, Kathy; Ferrari, Carlo; Lai, Ching Lung; Gish, Robert G.; Gane, Edward
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Hepatic-targeted RNA interference provides robust and persistent knockdown of alpha-1 antitrypsin levels in ZZ patients
err2018-08-01
err54
errOAAI
errTurner, Alice M.; Stolk, Jan; Bals, Robert; Lickliter, Jason D.; Hamilton, James; Christianson, Dawn R.; Given, Bruce D.; Burdon, Jonathan G.; Loomba, Rohit; Stoller, James K.; Teckman, Jeffery H.
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RNAi-based treatment of chronically infected patients and chimpanzees reveals that integrated hepatitis B virus DNA is a source of HBsAg
err2017-09-27
err370
errOAAI
errWooddell, Christine I.; Yuen, Man-Fung; Chan, Henry Lik-Yuen; Gish, Robert G.; Locarnini, Stephen A.; Chavez, Deborah; Ferrari, Carlo; Given, Bruce D.; Hamilton, James; Kanner, Steven B.; Lai, Ching-Lung; Lau, Johnson Y. N.; Schluep, Thomas; Xu, Zhao; Lanford, Robert E.; Lewis, David L.
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Validation of the Hong Kong Liver Cancer Staging System in Determining Prognosis of the North American Patients Following Intra-arterial Therapy
err2017-05-01
err34
errOAAI
errSohn, Jae Ho; Duran, Rafael; Zhao, Yan; Fleckenstein, Florian; Chapiro, Julius; Sahu, Sonia; Schernthaner, Rudiger E.; Qian, Tianchen; Lee, Howard; Zhao, Li; Hamilton, James; Frangakis, Constantine; Lin, MingDe; Salem, Riad; Geschwind, Jean-Francois
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Targeting Factor 12 (F12) with a Novel RNAi Delivery Platform As a Prophylactic Treatment for Hereditary Angioedema (HAE)
err2016-02-01
err4
errOAAI
errMelquist, Stacey; Wakefield, Darren; Hamilton, Holly; Chu, Qili; Almeida, Aaron; Almeida, Lauren; Walters, Megan; Montez, Jessica; Hegge, Julia; Klein, Jason; Hazlett, Christine; Milarch, Tracie; Stephanie-Bertin; Andersen, Aaron; Doss, Edie; Schmidt, Rachael; Goth, Linda; Ferger, Sheryl; Rozema, David; Hamilton, James; Lewis, David; Kanner, Steven
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Neosaxitoxin as a local anesthetic
err2007-02-01
err59
errOAAI
errRodriguez-Navarro, Alberto J.; Lagos, Nestor; Lagos, Marcelo; Braghetto, Italo; Csendes, Attila; Hamilton, James; Figueroa, Cristian; Truan, Dominique; Garcia, Carlos; Rojas, Andres; Iglesias, Veronica; Brunet, Luis; Alvarez, Francisco
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Intrasphincteric neosaxitoxin injection: Evidence of lower esophageal sphincter relaxation in achalasia
err2006-11-01
err12
PREAI
errRodriguez-Navaro, Alberto J.; Lagos, Nestor; Lagos, Marcelo; Braghetto, Italo; Csendes, Attila; Hamilton, James; Berger, Zoltan; Wiedmaier, Gonzalo; Henriquez, Ana
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