Not logged in Final Results of the ILLUMINATE-A Phase 3 Clinical Trial of Lumasiran for Primary Hyperoxaluria 1 Frishberg, Yaacov; Saland, Jeffrey M.; Lieske, John C.; Du, Weiming; Coenen, Martin; Hogan, Julien; Sellier-Leclerc, Anne-Laure; Groothoff, Jaap W.; Kaspar, Cristin; Gansner, John M.; Hulton, Sally-Anne Share Save
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Long-term lumasiran therapy final results from a Phase 2 open-label extension study in primary hyperoxaluria Frishberg, Yaacov; Groothoff, Jaap W.; Hulton, Sally-Anne; Harambat, Jerome; Hogan, Julien; Sellier-Leclerc, Anne-Laure; Hayes, Wesley; Coenen, Martin J.; Willey, Richard; Gansner, John M.; Magen, Daniella Share Save
Long-term efficacy and safety in the 60-month, Phase 3 ILLUMINATE-B trial of lumasiran in infants and young children with primary hyperoxaluria type 1 Frishberg, Yaacov; Hayes, Wesley; Ben-Shalom, Efrat; Shasha-Lavsky, Hadas; Sas, David; Michael, Mini; Sellier-Leclerc, Anne-Laure; Hogan, Julien; Willey, Richard; Gansner, John; Kaspar, Cristin; Magen, Daniella Share Save
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Real-world use of complement inhibitors for haemolytic uraemic syndrome: an analysis of the European Rare Kidney Disease Registry cohort Vujovic, Aleksandra; Sellier-Leclerc, Anne-Laure; Mancuso, Maria Cristina; Boyer, Olivia; Awan, Atif; Gargiulo, Antonio; Loos, Sebastian; Fila, Marc; Jankauskiene, Augustina; Ariceta, Gema; Kanzelmeyer, Nele; Vidal, Enrico; Van Dyck, Maria; Levart, Tanja Kersnik; Simankova, Nadezda; Decramer, Stephane; Hofstetter, Jonas; Vivarelli, Marina; Sciascia, Savino; van de Kar, Nicole C. A. J.; Schaefer, Franz Share Save
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Assessment of respiratory function in children after kidney transplantation Toubal, Marine; Allain-Launay, Emma; Bruel, Alexandra; Sellier-Leclerc, Anne-Laure; Dehoux, Laurene; Novo, Robert; Baudouin, Veronique; Bihouee-Roussey, Tiphaine; Roussey, Gwenaelle; Porcheret, Florence; Bernard, Josselin Share Save
Real-Life Data of 2-Year Lumasiran Use in the DAILY-LUMA Cohort Sellier-Leclerc, Anne-Laure; Cloarec, Melissa; Knebelmann, Bertrand; Allard, Lise; Boyer, Olivia; Cloarec, Sylvie; Dossier, Claire; Le Quintrec, Moglie; Stehle, Thomas; Vrillon, Isabelle; Burtey, Stephane; Cornec-Le Gall, Emilie; Courbebaisse, Marie; Frouget, Thierry; Garnier, Arnaud; Krummel, Thierry; Lemoine, Sandrine; Monet-Didailler, Catherine; Rousset-Rouviere, Caroline; Ryckewaert, Amelie; Schendel, Adeline; Flammier, Sacha; Acquaviva-Bourdain, Cecile; Bacchetta, Justine Share Save
Favorable Outcome After Single-kidney Transplantation From Small Donors in Children: A Match-controlled CERTAIN Registry Study Schild, Raphael; Abreu, Karla Carvajal; Buescher, Anja; Kanzelmeyer, Nele; Lezius, Susanne; Krupka, Kai; Weitz, Marcus; Prytula, Agnieszka; Printza, Nikoleta; Berta, Laszlo; Saygili, Seha Kamil; Sellier-Leclerc, Anne-Laure; Sparta, Giuseppina; Marks, Stephen D.; Kemper, Markus J.; Koenig, Sabine; Topaloglu, Rezan; Mueller, Dominik; Klaus, Guenter; Weber, Stefanie; Oh, Jun; Herden, Uta; Carraro, Andrea; Dello Strologo, Luca; Ariceta, Gema; Hoyer, Peter; Toenshoff, Burkhard; Pape, Lars Share Save
Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1 : Results from a Phase III Clinical Trial Saland, Jeffrey M.; Lieske, John C.; Groothoff, Jaap W.; Frishberg, Yaacov; Shasha-Lavsky, Hadas; Magen, Daniella; Moochhala, Shabbir H.; Simkova, Eva; Coenen, Martin; Hayes, Wesley; Hogan, Julien; Sellier-Leclerc, Anne-Laure; Willey, Richard; Gansner, John M.; Hulton, Sally -Anne Share Save
Metabolic Acidosis Is Associated With an Accelerated Decline of Allograft Function in Pediatric Kidney Transplantation Prytula, Agnieszka; Shroff, Rukshana; van Gremberghe, Ineke; Krupka, Kai; Bacchetta, Justine; Benetti, Elisa; Grenda, Ryszard; Guzzo, Isabella; Kanzelmeyer, Nele; Buyukkaragoez, Bahar; Kranz, Birgitta; Nalcacoglu, Hulya; Oh, Jun; Pape, Lars; Shenoy, Mohan; Sellier-Leclerc, Anne -Laure; Tonshoff, Burkhard Share Save
Nedosiran Safety and Efficacy in PH1 Interim Analysis of PHYOX3 Groothoff, Jaap; Sellier-Leclerc, Anne -Laure; Deesker, Lisa; Bacchetta, Justine; Schalk, Gesa; Toenshoff, Burkhard; Lipkin, Graham; Lemoine, Sandrine; Bowman, Thomas; Zhou, Jing; Hoppe, Bernd Share Save
Lumasiran for Advanced Primary Hyperoxaluria Type 1: Phase 3 ILLUMINATE-C Trial Michael, Mini; Groothoff, Jaap W.; Shasha-Lavsky, Hadas; Lieske, John C.; Frishberg, Yaacov; Simkova, Eva; Sellier-Leclerc, Anne-Laure; Devresse, Arnaud; Guebre-Egziabher, Fitsum; Bakkaloglu, Sevcan A.; Mourani, Chebl; Saqan, Rola; Singer, Richard; Willey, Richard; Habtemariam, Bahru; Gansner, John M.; Bhan, Ishir; McGregor, Tracy; Magen, Daniella Share Save
Idiopathic nephrotic syndrome relapse following COVID-19 vaccination: a series of 25 cases Hummel, Aurelie; Oniszczuk, Julie; Kervella, Delphine; Charbit, Marina; Guerrot, Dominique; Testa, Angelo; Philipponnet, Carole; Chauvet, Cecile; Guincestre, Thomas; Brochard, Karine; Benezech, Ariane; Figueres, Lucile; Belenfant, Xavier; Guarnieri, Andrea; Demoulin, Nathalie; Benetti, Elisa; Miglinas, Marius; Dessaix, Kathleen; Morelle, Johann; Angeletti, Andrea; Sellier-Leclerc, Anne-Laure; Ranchin, Bruno; Goussard, Guillaume; Hudier, Laurent; Bacchetta, Justine; Servais, Aude; Audard, Vincent Share Save
Phase 3 trial of lumasiran for primary hyperoxaluria type 1: A new RNAi therapeutic in infants and young children Sas, David J.; Magen, Daniella; Hayes, Wesley; Shasha-Lavsky, Hadas; Michael, Mini; Schulte, Indra; Sellier-Leclerc, Anne-Laure; Lu, Jiandong; Seddighzadeh, Ali; Habtemariam, Bahru; McGregor, Tracy L.; Fujita, Kenji P.; Frishberg, Yaacov Share Save
Randomized Clinical Trial on the Long-Term Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1 Hulton, Sally A.; Groothoff, Jaap W.; Frishberg, Yaacov; Koren, Michael J.; Overcash, J. Scott; Sellier-Leclerc, Anne-Laure; Shasha-Lavsky, Hadas; Saland, Jeffrey M.; Hayes, Wesley; Magen, Daniella; Moochhala, Shabbir H.; Coenen, Martin; Simkova, Eva; Garrelfs, Sander F.; Sas, David J.; Meliambro, Kristin A.; Ngo, Taylor; Sweetser, Marianne T.; Habtemariam, Bahru A.; Gansner, John M.; McGregor, Tracy L.; Lieske, John C. Share Save
Preemptive Kidney Transplantation Is Associated With Transplantation Outcomes in Children: Results From the French Kidney Replacement Therapy Registry Prezelin-Reydit, Mathilde; Madden, Iona; Macher, Marie-Alice; Salomon, Remi; Sellier-Leclerc, Anne-Laure; Roussey, Gwenaelle; Lahoche, Annie; Garaix, Florentine; Decramer, Stephane; Ulinski, Tim; Fila, Marc; Dunand, Olivier; Merieau, Elodie; Pongas, Marios; Zaloszyc, Ariane; Baudouin, Veronique; Berard, Etienne; Couchoud, Cecile; Leffondre, Karen; Harambat, Jerome Share Save
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