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SavePRPF8 Mutation-Induced Defects in Human iPSC-Derived RPE Are Rescued by Adenine Base Editing
Sun, Xihao; Liang, Yuan; Liang, Yuqin; Li, Wenwei; Chen, Hang; Ding, Chengcheng; Duan, Chunwen; Zhou, Yalan; Zhang, Ruting; Xu, Huizhuo; Chen, Jiansu
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