Not logged in Phase 3 trial of lumasiran for primary hyperoxaluria type 1: A new RNAi therapeutic in infants and young children Sas, David J.; Magen, Daniella; Hayes, Wesley; Shasha-Lavsky, Hadas; Michael, Mini; Schulte, Indra; Sellier-Leclerc, Anne-Laure; Lu, Jiandong; Seddighzadeh, Ali; Habtemariam, Bahru; McGregor, Tracy L.; Fujita, Kenji P.; Frishberg, Yaacov Share Save
Post-intervention Status in Patients With Refractory Myasthenia Gravis Treated With Eculizumab During REGAIN and Its Open-Label Extension Mantegazza, Renato; Wolfe, Gil, I; Muppidi, Srikanth; Wiendl, Heinz; Fujita, Kenji P.; O'Brien, Fanny L.; Booth, Heather D. E.; Howard, James F., Jr. Share Save
Long-term efficacy and safety of eculizumab in Japanese patients with generalized myasthenia gravis: A subgroup analysis of the REGAIN open-label extension study Murai, Hiroyuki; Uzawa, Akiyuki; Suzuki, Yasushi; Imai, Tomihiro; Shiraishi, Hirokazu; Suzuki, Hidekazu; Okumura, Meinoshin; O'Brien, Fanny; Wang, Jing-Jing; Fujita, Kenji P.; Utsugisawa, Kimiaki Share Save
Eculizumab in Aquaporin-4-Positive Neuromyelitis Optica Spectrum Disorder Pittock, S. J.; Berthele, A.; Fujihara, K.; Kim, H. J.; Levy, M.; Palace, J.; Nakashima, I.; Terzi, M.; Totolyan, N.; Viswanathan, S.; Wang, K. -C.; Pace, A.; Fujita, K. P.; Armstrong, R.; Wingerchuk, D. M. Share Save
Natural History of Perinatal and Infantile Hypophosphatasia: A Retrospective Study Whyte, Michael P.; Leung, Edward; Wilcox, William R.; Liese, Johannes; Argente, Jesus; Martos-Moreno, Gabriel A.; Reeves, Amy; Fujita, Kenji P.; Moseley, Scott; Hofmann, Christine; Beck, Michael; DiMeglio, Linda; Hwu, Paul Wuh-Liang; Madson, Katherine L.; Nanda, Upasana; Simm, Peter; Simmons, Jill; Steelman, Joel; Steiner, Robert D.; Superti-Furga, Andrea Share Save
Efficacy and Safety of Asfotase Alfa in Infants and Young Children With Hypophosphatasia: A Phase 2 Open-Label Study Hofmann, Christine E.; Harmatz, Paul; Vockley, Jerry; Hoegler, Wolfgang; Nakayama, Hideki; Bishop, Nick; Martos-Moreno, Gabriel A.; Moseley, Scott; Fujita, Kenji P.; Liese, Johannes; Rockman-Greenberg, Cheryl Share Save
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Asfotase alfa therapy for children with hypophosphatasia Whyte, Michael P.; Madson, Katherine L.; Phillips, Dawn; Reeves, Amy L.; McAlister, William H.; Yakimoski, Amy; Mack, Karen E.; Hamilton, Kim; Kagan, Kori; Fujita, Kenji P.; Thompson, David D.; Moseley, Scott; Odrljin, Tatjana; Rockman-Greenberg, Cheryl Share Save
Haemodynamic effects of rolofylline in the treatment of patients with heart failure and impaired renal function Ponikowski, Piotr; Mitrovic, Veselin; O'Connor, Christopher M.; Dittrich, Howard; Cotter, Gad; Massie, Barry M.; Givertz, Michael M.; Chen, Erluo; Murray, Meredith; Weatherley, Beth D.; Fujita, Kenji P.; Metra, Marco Share Save
Impact of Serial Troponin Release on Outcomes in Patients With Acute Heart Failure Analysis From the PROTECT Pilot Study O'Connor, Christopher M.; Fiuzat, Mona; Lombardi, Carlo; Fujita, Kenji; Jia, Gang; Davison, Beth A.; Cleland, John; Bloomfield, Daniel; Dittrich, Howard C.; DeLucca, Paul; Givertz, Michael M.; Mansoor, George; Ponikowski, Piotr; Teerlink, John R.; Voors, Adriaan A.; Massie, Barry M.; Cotter, Gad; Metra, Marco Share Save