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Heteroduplex oligonucleotide technology boosts oligonucleotide splice switching activity of morpholino oligomers in a Duchenne muscular dystrophy mouse model Hasegawa, Juri; Nagata, Tetsuya; Ihara, Kensuke; Tanihata, Jun; Ebihara, Satoe; Yoshida-Tanaka, Kie; Yanagidaira, Mitsugu; Ohara, Masahiro; Sasaki, Asuka; Nakayama, Miyu; Yamamoto, Syunsuke; Ishii, Takashi; Iwata-Hara, Rintaro; Naito, Mitsuru; Miyata, Kanjiro; Sakaue, Fumika; Yokota, Takanori Share Save
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Size-Dependent Glioblastoma Targeting by Polymeric Nanoruler with Prolonged Blood Circulation Ishibashi, Yukine; Naito, Mitsuru; Watanuki, Yusuke; Hori, Mao; Ogura, Satomi; Taniwaki, Kaori; Cho, Masaru; Komiya, Ryosuke; Mochida, Yuki; Miyata, Kanjiro Share Save
Hydrophobicity Tuning of Cationic Polyaspartamide Derivatives for Enhanced Antisense Oligonucleotide Delivery Yum, Jongmin; Aulia, Fadlina; Kamiya, Keisuke; Hori, Mao; Qiao, Nan; Kim, Beob Soo; Naito, Mitsuru; Ogura, Satomi; Nagata, Tetsuya; Yokota, Takanori; Uchida, Satoshi; Obika, Satoshi; Kim, Hyun Jin; Miyata, Kanjiro Share Save
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In situ-formable, dynamic crosslinked poly(ethylene glycol) carrier for localized adeno-associated virus infection and reduced off-target effects Kato, Motoi; Ishikawa, Shohei; Shen, Qi; Du, Zening; Katashima, Takuya; Naito, Mitsuru; Numahata, Takao; Okazaki, Mutsumi; Sakai, Takamasa; Kurita, Masakazu Share Save
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