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Michele Carrer

ionis pharmaceuticals, inc., carlsbad, california, usa

9H-index
27Paper Count
778Citation Count
Published Papers 17
Publication Date
Antisense oligonucleotides targeting valosin-containing protein ameliorate muscle pathology and molecular defects in cell and mouse models of multisystem proteinopathy
err2025-12-08
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errOAAI
errPallabi Pal; Michele Carrer; Lan Weiss; Olga G. Jaime; Cheng Cheng; Alyaa Shmara; Victoria Boock; Danae Bosch; Marwan Youssef; Yasamin Fazeli; Megan Afetian; Tamar R. Grossman; Michael R. Hicks; Paymaan Jafar-nejad; Virginia Kimonis
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Hepatocyte KCTD17-mediated SERPINA3 inhibition determines liver fibrosis in metabolic dysfunction-associated steatohepatitis
err2025-08-01
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errOAAI
errYelin Jeong; Ah-Reum Oh; Young Hoon Jung; Kyung Hee Jung; Seongju Lee; Michele Carrer; Sang Bae Lee; Luca Valenti; Utpal B. Pajvani; KyeongJin Kim
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Skeletal muscle effects of antisense oligonucleotides targeting glycogen synthase 1 in a mouse model of Pompe disease
err2025-04-23
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errOAAI
errWeiss, Lan; Carrer, Michele; Shmara, Alyaa; Martin, Angela; Yin, Hong; Pal, Pallabi; Cheng, Cheng; Ta, Lac; Boock, Victoria; Fazeli, Yasamin; Chang, Mindy; Paguio, Marvin; Lee, Jonathan; Yu, Howard; Weiss, John; Grossman, Tamar R.; Raben, Nina; Jafar-Nejad, Paymaan; Kimonis, Virginia
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Conjugation to a transferrin receptor 1-binding Bicycle peptide enhances ASO and siRNA potency in skeletal and cardiac muscles
err2025-04-10
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PREAI
errOstergaard, Michael E.; Carrer, Michele; Anderson, Brooke A.; Afetian, Megan; Bakooshli, Mohsen A.; Santos, Jinro A.; Klein, Stephanie K.; Capitanio, Juliana; Freestone, Graeme C.; Tanowitz, Michael; Galindo-Murillo, Rodrigo; Gaus, Hans J.; Dwyer, Chrissa A.; Jackson, Michaela; Jafar-nejad, Paymaan; Rigo, Frank; Seth, Punit P.; Gaynor, Katherine U.; Stanway, Steven J.; Urbonas, Liudvikas; St. Denis, Megan A.; Pellegrino, Simone; Bezerra, Gustavo A.; Rigby, Michael; Gowans, Ellen; Van Rietschoten, Katerine; Beswick, Paul; Skynner, Michael J.; Swayze, Eric E.
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Targeting mechanistic target of rapamycin complex 2 attenuates immunopathology in systemic lupus erythematosus
err2024-12-04
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errAi, Minji; Zhou, Xian; Carrer, Michele; Jafar-nejad, Paymaan; Li, Yanfeng; Gades, Naomi; Alexander, Mariam; Bautista-Vargas, Mario
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KCTD17-mediated Ras stabilization promotes hepatocellular carcinoma progression
err2024-10-01
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errJung, Young Hoon; Lee, Yun Ji; Dao, Tam; Jung, Kyung Hee; Yu, Junjie; Oh, Ah-Reum; Jeong, Yelin; Gi, Hyunjoon; Kim, Young Un; Ryu, Dongryeol; Carrer, Michele; Pajvani, Utpal B.; Lee, Sang Bae; Hong, Soon-Sun; Kim, Kyeongjin
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Adjunct treatment with glycogen synthase (GYS1) antisense oligonucleotides with enzyme replacement therapy (ERT) reduces glycogen more effectively in the Pompe disease mouse model
err2024-04-01
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PREAI
errMartin, Angela; Weiss, Lan; Carrer, Michele; Shmara, Alyaa; Boock, Victoria; Ibrahim, Matthew; Hettrick, Lisa; Watt, Andy; Jafar-nejad, Paymaan; Kimonis, Virginia
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Antisense oligonucleotides targeting a NOTCH3 mutation in male mice ameliorate the cortical osteopenia of lateral meningocele syndrome
errBONE
IF3.6
err2023-12-01
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errOAAI
errCanalis, Ernesto; Mocarska, Magda; Schilling, Lauren; Jafar-nejad, Paymaan; Carrer, Michele
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Hepatocyte TLR4 triggers inter-hepatocyte Jagged1/Notch signaling to determine NASH-induced fibrosis
err2021-06-23
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errOAAI
errYu, Junjie; Zhu, Changyu; Wang, Xiaobo; Kim, KyeongJin; Bartolome, Alberto; Dongiovanni, Paola; Yates, Katherine P.; Valenti, Luca; Carrer, Michele; Sadowski, Thorsten; Qiang, Li; Tabas, Ira; Lavine, Joel E.; Pajvani, Utpal B.
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Antisense Oligonucleotides Targeting Jagged 1 Reduce House Dust Mite-induced Goblet Cell Metaplasia in the Adult Murine Lung
err2020-07-01
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PREAI
errCarrer, Michele; Crosby, Jeff R.; Sun, Guizhen; Zhao, Chenguang; Damle, Sagar S.; Kuntz, Steven G.; Monia, Brett P.; Hart, Christopher E.; Grossman, Tamar R.
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Antisense oligonucleotides targeting Notch2 ameliorate the osteopenic phenotype in a mouse model of Hajdu-Cheney syndrome
err2020-03-01
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errOAAI
errCanalis, Ernesto; Grossman, Tamar R.; Carrer, Michele; Schilling, Lauren; Yu, Jungeun
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Antisense oligonucleotide targeting glycogen synthase (GYS1) in a Pompe disease mouse model
err2020-02-01
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errOAAI
errKimonis, Virginia E.; Weiss, Lan; Carrer, Michele; Ta, Lac; Chang, Mindy; Cheng, Cheng; Hettrick, Lisa; Watt, Andy; Raben, Nina; Grossman, Tamar
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Antisense oligonucleotide treatment targeting glycogen synthase (GYS1) in a mouse model of Pompe disease
err2019-02-01
err1
PREAI
errKimonis, Virginia; Weiss, Lan; Carrer, Michele; Yu, Howard; Raben, Nina; Grossman, Tamar
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Antisense therapy targeting complement factor B
err2018-10-01
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PREAI
errGrossman, Tamar; Carrer, Michele; Johnson, Robert; Shen, Lijiang; Hettrick, Lisa; Henry, Scott; Monia, Brett; McCaleb, Michael
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Control of mitochondrial metabolism and systemic energy homeostasis by microRNAs 378 and 378☆
err2012-09-04
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errCarrer, Michele; Liu, Ning; Grueter, Chad E.; Williams, Andrew H.; Frisard, Madlyn I.; Hulver, Matthew W.; Bassel-Duby, Rhonda; Olson, Eric N.
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Histone deacetylases 1 and 2 regulate autophagy flux and skeletal muscle homeostasis in mice
err2012-01-17
err120
errOAAI
errMoresi, Viviana; Carrer, Michele; Grueter, Chad E.; Rifki, Oktay F.; Shelton, John M.; Richardson, James A.; Bassel-Duby, Rhonda; Olson, Eric N.
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Redundant Control of Adipogenesis by Histone Deacetylases 1 and 2
err2010-05-01
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errHaberland, Michael; Carrer, Michele; Mokalled, Mayssa H.; Montgomery, Rusty L.; Olson, Eric N.
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