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Skeletal muscle effects of antisense oligonucleotides targeting glycogen synthase 1 in a mouse model of Pompe disease Weiss, Lan; Carrer, Michele; Shmara, Alyaa; Martin, Angela; Yin, Hong; Pal, Pallabi; Cheng, Cheng; Ta, Lac; Boock, Victoria; Fazeli, Yasamin; Chang, Mindy; Paguio, Marvin; Lee, Jonathan; Yu, Howard; Weiss, John; Grossman, Tamar R.; Raben, Nina; Jafar-Nejad, Paymaan; Kimonis, Virginia Share Save
Conjugation to a transferrin receptor 1-binding Bicycle peptide enhances ASO and siRNA potency in skeletal and cardiac muscles Ostergaard, Michael E.; Carrer, Michele; Anderson, Brooke A.; Afetian, Megan; Bakooshli, Mohsen A.; Santos, Jinro A.; Klein, Stephanie K.; Capitanio, Juliana; Freestone, Graeme C.; Tanowitz, Michael; Galindo-Murillo, Rodrigo; Gaus, Hans J.; Dwyer, Chrissa A.; Jackson, Michaela; Jafar-nejad, Paymaan; Rigo, Frank; Seth, Punit P.; Gaynor, Katherine U.; Stanway, Steven J.; Urbonas, Liudvikas; St. Denis, Megan A.; Pellegrino, Simone; Bezerra, Gustavo A.; Rigby, Michael; Gowans, Ellen; Van Rietschoten, Katerine; Beswick, Paul; Skynner, Michael J.; Swayze, Eric E. Share Save
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KCTD17-mediated Ras stabilization promotes hepatocellular carcinoma progression Jung, Young Hoon; Lee, Yun Ji; Dao, Tam; Jung, Kyung Hee; Yu, Junjie; Oh, Ah-Reum; Jeong, Yelin; Gi, Hyunjoon; Kim, Young Un; Ryu, Dongryeol; Carrer, Michele; Pajvani, Utpal B.; Lee, Sang Bae; Hong, Soon-Sun; Kim, Kyeongjin Share Save
Adjunct treatment with glycogen synthase (GYS1) antisense oligonucleotides with enzyme replacement therapy (ERT) reduces glycogen more effectively in the Pompe disease mouse model Martin, Angela; Weiss, Lan; Carrer, Michele; Shmara, Alyaa; Boock, Victoria; Ibrahim, Matthew; Hettrick, Lisa; Watt, Andy; Jafar-nejad, Paymaan; Kimonis, Virginia Share Save
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Hepatocyte TLR4 triggers inter-hepatocyte Jagged1/Notch signaling to determine NASH-induced fibrosis Yu, Junjie; Zhu, Changyu; Wang, Xiaobo; Kim, KyeongJin; Bartolome, Alberto; Dongiovanni, Paola; Yates, Katherine P.; Valenti, Luca; Carrer, Michele; Sadowski, Thorsten; Qiang, Li; Tabas, Ira; Lavine, Joel E.; Pajvani, Utpal B. Share Save
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Antisense oligonucleotide targeting glycogen synthase (GYS1) in a Pompe disease mouse model Kimonis, Virginia E.; Weiss, Lan; Carrer, Michele; Ta, Lac; Chang, Mindy; Cheng, Cheng; Hettrick, Lisa; Watt, Andy; Raben, Nina; Grossman, Tamar Share Save
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