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SaveRationale and design of the multi organ inflammation with serial testing study: a comprehensive assessment of functional and structural abnormalities in patients with recovered COVID-19
Paterson, D. Ian; White, James A.; Beaulieu, Christian; Sherrington, Rachel; Prado, Carla M.; Tandon, Puneeta; Halloran, Kieran; Smith, Stephanie; McCombe, Jennifer A.; Ritchie, Bruce; Pituskin, Edith; Haykowsky, Mark J.; Coulden, Richard; Emery, Derek; Tsui, Albert K.; Wu, Kai Y.; Oudit, Gavin Y.; Ezekowitz, Justin A.; Thompson, Richard B.
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SaveGaradacimab for hereditary angioedema attack prevention: long-term efficacy, quality of life, and safety data from a phase 2, randomised, open-label extension study
Craig, Timothy J.; Levy, Donald S.; Reshef, Avner; Lumry, William R.; Martinez-Saguer, Inmaculada; Jacobs, Joshua S.; Yang, William H.; Ritchie, Bruce; Aygoeren-Puersuen, Emel; Keith, Paul K.; Busse, Paula; Feuersenger, Henrike; Bica, Mihai Alexandru; Jacobs, Iris; Pragst, Ingo; Magerl, Markus
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SaveEfficacy and safety of garadacimab, a factor XIIa inhibitor for hereditary angioedema prevention (VANGUARD): a global, multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Craig, Timothy J.; Reshef, Avner; Li, H. Henry; Jacobs, Joshua S.; Bernstein, Jonathan A.; Farkas, Henriette; Yang, William H.; Stroes, Erik S. G.; Ohsawa, Isao; Tachdjian, Raffi; Manning, Michael E.; Lumry, William R.; Saguer, Inmaculada Martinez; Aygoeren-Puersuen, Emel; Ritchie, Bruce; Sussman, Gordon L.; Anderson, John; Kawahata, Kimito; Suzuki, Yusuke; Staubach, Petra; Treudler, Regina; Feuersenger, Henrike; Glassman, Fiona; Jacobs, Iris; Magerl, Markus
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SaveClinical efficacy, safety and tolerability of a new subcutaneous immunoglobulin 16.5% (Octanorm [Cutaquig®]) in the treatment of patients with primary immunodeficiencies (vol 10, 40, 2019)
Kobayashi, Roger H.; Gupta, Sudhir; Melamed, Isaac; Mandujano, J. Fernando; Kobayashi, Ai Lan; Ritchie, Bruce; Geng, Bob; Atkinson, Thomas Prescott; Rehman, Syed; Turpel-Kantor, Eva; Litzman, Jiri
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Saveα2,6-Sialylation Is Upregulated in Severe COVID-19, Implicating the Complement Cascade
Qin, Rui; Kurz, Emma; Chen, Shuhui; Zeck, Briana; Chiribogas, Luis; Jackson, Dana; Herchen, Alex; Attia, Tyson; Carlock, Michael; Rapkiewicz, Amy; Bar-Sagi, Dafna; Ritchie, Bruce; Ross, Ted M.; Mahal, Lara K.
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SaveLong-term efficacy, safety, and tolerability of a subcutaneous immunoglobulin 16.5% (cutaquig®) in the treatment of patients with primary immunodeficiencies
Kobayashi, Roger H.; Litzman, Jiri; Melamed, Isaac; Mandujano, J. Fernando; Kobayashi, Ai Lan; Ritchie, Bruce; Geng, Bob; Atkinson, T. Prescott; Rehman, Syed; Hoeller, Sonja; Turpel-Kantor, Eva; Kreuwel, Huub; Speer, J. C.; Gupta, Sudhir
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SaveProphylactic use of an anti-activated factor XII monoclonal antibody, garadacimab, for patients with C1-esterase inhibitor-deficient hereditary angioedema: a randomised, double-blind, placebo-controlled, phase 2 trial
Craig, Timothy; Magerl, Markus; Levy, Donald S.; Reshef, Avner; Lumry, William R.; Martinez-Saguer, Inmaculada; Jacobs, Joshua S.; Yang, William H.; Ritchie, Bruce; Aygoeren-Puersuen, Emel; Keith, Paul K.; Busse, Paula; Feuersenger, Henrike; Pawaskar, Dipti; Jacobs, Iris; Pragst, Ingo; Doyle, Mittie K.
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SaveThe international WAO/EAACI guideline for the management of hereditary angioedema - The 2021 revision and update
Maurer, Marcus; Magerl, Markus; Betschel, Stephen; Aberer, Werner; Ansotegui, Ignacio J.; Aygoeren-Puersuen, Emel; Banerji, Aleena; Bara, Noemi-Anna; Boccon-Gibod, Isabelle; Bork, Konrad; Bouillet, Laurence; Boysenl, Henrik Balle; Brodszki, Nicholas; Busse, Paula J.; Bygum, Anette; Caballero, Teresa; Cancian, Mauro; Castaldol, Anthony J.; Cohn, Danny M.; Csuka, Dorottya; Farkas, Henriette; Gompels, Mark; Gower, Richard; Grumach, Anete S.; Guidos-Fogelbach, Guillermo; Hide, Michihiro; Kang, Hye-Ryun; Kaplan, Allen P.; Katelaris, Constance H.; Kiani-Alikhan, Sorena; Lei, Wei-Te; Lockey, Richard F.; Longhurst, Hilary; Lumry, William; MacGinnitie, Andrew; Malbran, Alejandro; Martinez Saguer, Inmaculada; Matta Campos, Juan Jose; Nast, Alexander; Dinh Nguyen; Nieto-Martinez, Sandra A.; Pawankar, Ruby; Peter, Jonathan; Porebski, Grzegorz; Prior, Nieves; Reshef, Avner; Riedl, Marc; Ritchie, Bruce; Sheikh, Farrukh Rafique; Smith, William B.; Spaeth, Peter J.; Stobiecki, Marcin; Toubi, Elias; Varga, Lilian Agnes; Weller, Karsten; Zanichelli, Andrea; Zhi, Yuxiang; Zuraw, Bruce; Craig, Timothy
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SaveThe international WAO/EAACI guideline for the management of hereditary angioedema-The 2021 revision and update
Maurer, Marcus; Magerl, Markus; Betschel, Stephen; Aberer, Werner; Ansotegui, Ignacio J.; Aygoeren-Puersuen, Emel; Banerji, Aleena; Bara, Noemi-Anna; Boccon-Gibod, Isabelle; Bork, Konrad; Bouillet, Laurence; Boysen, Henrik Balle; Brodszki, Nicholas; Busse, Paula J.; Bygum, Anette; Caballero, Teresa; Cancian, Mauro; Castaldo, Anthony; Cohn, Danny M.; Csuka, Dorrottya; Farkas, Henriette; Gompels, Mark; Gower, Richard; Grumach, Anete S.; Guidos-Fogelbach, Guillermo; Hide, Michihiro; Kang, Hye-Ryun; Kaplan, Allen Phillip; Katelaris, Constance; Kiani-Alikhan, Sorena; Lei, Wei-Te; Lockey, Richard; Longhurst, Hilary; Lumry, William R.; MacGinnitie, Andrew; Malbran, Alejandro; Saguer, Inmaculada Martinez; Matta, Juan Jose; Nast, Alexander; Nguyen, Dinh; Nieto-Martinez, Sandra A.; Pawankar, Ruby; Peter, Jonathan; Porebski, Grzegorz; Prior, Nieves; Reshef, Avner; Riedl, Marc; Ritchie, Bruce; Sheikh, Farrukh Rafique; Smith, William R.; Spaeth, Peter J.; Stobiecki, Marcin; Toubi, Elias; Varga, Lilian Agnes; Weller, Karsten; Zanichelli, Andrea; Zhi, Yuxiang; Zuraw, Bruce; Craig, Timothy
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SaveEfficacy and safety of givosiran for acute hepatic porphyria: 24-month interim analysis of the randomized phase 3 ENVISION study
Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera-Peiro, Paula; Bissell, D. Montgomery; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh, Eliane
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SaveDefinition, aims, and implementation of GA2LEN/HAEi Angioedema Centers of Reference and Excellence
Maurer, Marcus; Werner, Aberer; Agondi, Rosana; Al-Ahmad, Mona; Al-Nesf, Maryam Ali; Ansotegui, Ignacio; Arnaout, Rand; Arruda, Luisa Karla; Asero, Riccardo; Aygoeren-Puersue, Emel; Banerji, Aleena; Bauer, Andrea; Ben-Shoshan, Moshe; Berardi, Alejandro; Bernstein, Jonathan A.; Betschel, Stephen; Bindslev-Jensen, Carsten; Bizjak, Mojca; Boccon-Gibod, Isabelle; Bork, Konrad; Bouillet, Laurence; Boysen, Henrik Balle; Brodszki, Nicholas; Broesby-Olsen, Sigurd; Busse, Paula; Buttgereit, Thomas; Bygum, Anette; Caballero, Teresa; Campos, Regis A.; Cancian, Mauro; Cherrez-Ojeda, Ivan; Cohn, Danny M.; Costa, Celia; Craig, Timothy; Criado, Paulo Ricardo; Criado, Roberta F.; Csuka, Dorottya; Dissemond, Joachim; Du-Thanh, Aurelie; Ensina, Luis Felipe; Ertas, Ragip; Fabiani, Jose E.; Fantini, Claudio; Farkas, Henriette; Ferrucci, Silvia Mariel; Figueras-Nart, Ignasi; Fili, Natalia L.; Fomina, Daria; Fukunaga, Atsushi; Gelincik, Asli; Gimenez-Arnau, Ana; Godse, Kiran; Gompels, Mark; Goncalo, Margarida; Gotua, Maia; Gower, Richard; Grumach, Anete S.; Guidos-Fogelbach, Guillermo; Hide, Michihiro; Ilina, Natalia; Inomata, Naoko; Jakob, Thilo; Josviack, Dario O.; Kang, Hye-Ryun; Kaplan, Allen; Kasperska-Zajac, Alicja; Katelaris, Constance; Kessel, Aharon; Kleinheinz, Andreas; Kocaturk, Emek; Kosnik, Mitja; Krasowska, Dorota; Kulthanan, Kanokvalai; Kumaran, M. Sendhil; Larco Sousa, Jose Ignacio; Longhurst, Hilary J.; Lumry, William; MacGinnitie, Andrew; Magerl, Markus; Makris, Michael P.; Malbran, Alejandro; Marsland, Alexander; Martinez-Saguer, Inmaculada; Medina, Iris V.; Meshkova, Raisa; Metz, Martin; Nasr, Iman; Nicolay, Jan; Nishigori, Chikako; Ohsawa, Isao; Ozyurt, Kemal; Papadopoulos, Nikolaos G.; Parisi, Claudio A. S.; Peter, Jonathan Grant; Pfuetzner, Wolfgang; Popov, Todor; Prior, Nieves; Ramon, German D.; Reich, Adam; Reshef, Avner; Riedl, Marc A.; Ritchie, Bruce; Rockmann-Helmbach, Heike; Rudenko, Michael; Salman, Andac; Sanchez-Borges, Mario; Schmid-Grendelmeier, Peter; Serpa, Faradiba S.; Serra-Baldrich, Esther; Sheikh, Farrukh R.; Smith, William; Soria, Angele; Staubach, Petra; Steiner, Urs C.; Stobiecki, Marcin; Sussman, Gordon; Tagka, Anna; Thomsen, Simon Francis; Treudler, Regina; Valle, Solange; van Doorn, Martijn; Varga, Lilian; Vazquez, Daniel O.; Wagner, Nicola; Wang, Liangchun; Weber-Chrysochoou, Christina; Ye, Young-Min; Zalewska-Janowska, Anna; Zanichelli, Andrea; Zhao, Zuotao; Zhi, Yuxiang; Zuberbier, Torsten; Zwiener, Ricardo D.; Castaldo, Anthony
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SaveOverall Health, Daily Functioning, and Quality of Life in Acute Hepatic Porphyria Patients: ENVISION, a Phase 3 Global, Multicenter, Randomized, Double-Blind, Placebo-Controlled Trial
Sardh, E.; Gouya, L.; Rees, D. C.; Stein, P.; Stoelzel, U.; Aguilera Peiro, P.; Bissell, D. M.; Bonkovsky, H. L.; Keel, S.; Parker, C.; Phillips, J. D.; Silver, S.; Windyga, J.; D'Avola, D.; Ross, G.; Stewart, P.; Ritchie, B.; Oh, J.; Harper, P.; Wang, J. D.; Langendonk, J. G.; Ivanova, A.; Horie, Y.; Anderson, K. E.; Ventura, P.; Kauppinen, R.; Vassiliou, D.; Wang, B.; Hother-Nielsen, O.; Nakahara, T.; Lee, M. J.; Sasapu, A.; Scalera, S.; Lin, T.; Penz, C.; Simon, A.; Ko, J.; Balwani, M.
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