Not logged inImproved targeted delivery of antisense oligonucleotide with an antibody mask
Hsia, Hung-En; Zanini, Chiara; Simonneau, Claire; Fraidling, Johannes; Kraft, Thomas e; Mayer, Klaus; Sommer, Annika; Indlekofer, Annette; Wirth, Tamara; Benz, Jorg; Georges, Guy; Langer, Lukas M.; Gassner, Christian; Larraillet, Vincent; Lohmann, Sabine; Koller, Erich; Manso, Mads; Ravn, Jacob; Hofer, Kerstin; Emrich, Thomas; Niewohner, Jens; Schumacher, Felix; Brinkmann, Ulrich
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SaveA novel DPH5-related diphthamide-deficiency syndrome causing embryonic lethality or profound neurodevelopmental disorder (vol 24, pg 1567, 2022)
Shankar, Suma P.; Grimsrud, Kristin; Lanoue, Louise; Egense, Alena; Willis, Brandon; Horberg, Johanna; Al Abdi, Lama; Mayer, Klaus; Utkur, Koray; Monaghan, Kristin G.; Krier, Joel; Stoler, Joan; Alnemer, Maha; Shankar, Prabhu R.; Schaffrath, Raffael; Alkuraya, Fowzan S.; Brinkmann, Ulrich; Eriksson, Leif A.; Lloyd, Kent; Rauen, Katherine A.
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