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Craig M. McDonald

university of california davis health

75H-index
488Paper Count
2.2WCitation Count
Published Papers 80
Publication Date
Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial
err2026-07-29
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errCraig M McDonald; Chet Villa; Jonathan H Soslow; Kati Maharry; Nathaniel Hogan; Michael Binks; Kevin C Berth; Kristi A Elliott; Michael Taylor; Kan N Hor; James Signorovich; Erik K Henricson; Han C Phan; Susan Apkon; Partha S Ghosh; Cuixia Tian; Aravindhan Veerapandiyan; Leigh Ramos-Platt; Katheryn Gambetta; Saunder M Bernes
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Cardiac Safety Outcomes in Delandistrogene Moxeparvovec Clinical Trials for Duchenne Muscular Dystrophy with Up to 5 Years of Follow-up
err2026-07-01
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errAravindhan Veerapandiyan; John Bourke; Jonathan H. Soslow; John W. Day; Craig M. McDonald; Jerry R. Mendell; Craig M. Zaidman; Stefanie Mason; Jianfeng Meng; Mark Vivien; Alexander P. Murphy; Christoph Wandel; James Richardson
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Five-Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: A Phase 1/2a Study
err2026-06-03
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errJerry R. Mendell; Zarife Sahenk; Linda P. Lowes; Megan A. Iammarino; Lindsay N. Alfano; Craig M. McDonald; James E. Signorovitch; Jim Jin; Jing Li; Stefanie Mason; Louise R. Rodino-Klapac
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Heart Transplantation and Ventricular Assist Device in Duchenne Muscular Dystrophy: A New Era
err2025-12-21
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PREAI
errRosenthal, David N.; Amodeo, Antonio; Butterfield, Russell J.; Butts, Ryan; Chrzanowski, Stephen; Cripe, Linda; Day, John; Davies, Ryan; Duong, Tina; Evers, Patrick; Gambetta, Katheryn; Harris, Rachel; Hayes, Emily; Kaufman, Beth; Lorts, Angela; Mack, Gordon; Mackenzie, Samuel J.; Mammen, Pradeep; Markham, Larry; Mcalister, Jennifer; Mcdonald, Craig; Nakano, Stephanie J.; Nandi, Deipanjan; Navaratnam, Manchula; Nelson, Stanley; Parent, John J.; Piccoli, Cara; Richmond, Marc; Rocha, Carolina; Sawnani, Hemant; Schrader, Rachel; Shell, Richard; Shih, Renata; Shugh, Svetlana; Smart, Theodore; Soslow, John; Spinner, Joseph; Taivassalo, Tanja; Tunugtla, Hari; Vanderpluym, Christina; Veerapandiyan, Aravindhan; Villa, Chet; Wittlieb-weber, Carol; Zafarullah, Marwa; Hollander, Seth
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Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4-to <7-year children
err2025-11-01
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errMummidivarpu, Swati; Dang, Utkarsh J.; Ziemba, Michael; Hathout, Yetrib; Clemens, Paula R.; Damsker, Jesse; Hagerty, Laura; Jusko, William J.; Smith, Edward C.; Mah, Jean K.; Guglieri, Michela; Nevo, Yoram; Kuntz, Nancy; Mcdonald, Craig M.; Ryan, Monique M.; Castro, Diana; Finkel, Richard S.; Conklin, Laurie S.; Mccall, John M.; Nagaraju, Kanneboyina; Van Den Anker, John; Hoffman, Eric P.
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Descriptive characterization of ambulatory health states in Duchenne muscular dystrophy: Motor function trajectories and times to loss of ambulation
err2025-09-23
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errFrancesco Muntoni; James Signorovitch; Michaela Johnson; Andres Gomez-Lievano; Nate Posner; Patricia Dorling; Katherine Beaverson; Jose Alvir; Matthias Mahn; Susan J Ward; Nathalie Goemans; Krista Vandenborne; Eugenio Mercuri; Craig M McDonald
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Consensus recommendations and considerations for the delivery and monitoring of gene therapy in patients with Duchenne muscular dystrophy
err2025-08-23
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PREAI
errJodi M. Wolff; Nora Capocci; Evrim Atas; Diana X. Bharucha-Goebel; John F. Brandsema; Russell J. Butterfield; Christina B. Chadwick; Manuela Corti; Thomas O. Crawford; Linda Cripe; John W. Day; Tina Duong; Mai K. ElMallah; Kevin M. Flanigan; Lindsey A. George; Natalie L. Goedeker; Erica Goude; Sharon Hesterlee; Brian Lin; Natalie K. Katz; Susan E. Matesanz; Craig McDonald; Elizabeth M. McNally; Claudia Mercado-Rodriguez; Deipanjan Nandi; Julie A. Parsons; Crystal Proud; Leigh Ramos-Platt; Angela Lek; Stephanie M. Salabarria; Eric Camino; Rachel Schrader; Erin Shea; Richard Shell; Perry B. Shieh; Jonathan H. Soslow; Jane B. Taylor; Aravindhan Veerapandiyan; Chet Villa; Michele L. Yang; Craig M. Zaidman; Carmen Leon-Astudillo; Barry J. Byrne
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Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons
err2025-08-19
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errCraig M. McDonald; Michela Guglieri; Dragana Vučinić; Gyula Acsadi; John F. Brandsema; Claudio Bruno; Erika L. Finanger; Amy Harper; Mercedes Lopez Lobato; Riccardo Masson; Nuria Muelas; Francina Munell; Yoram Nevo; Yann Péréon; Han Phan; Valeria A. Sansone; Mariacristina Scoto; Tracey Willis; Richard S. Finkel; Krista Vandenborne; Sara Cazzaniga; Silvia Montrasio; Federica Alessi; Paolo Bettica; Eugenio Mercuri; the Givinostat Study 51 Investigators; the Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS) Investigators; the ImagingDMD Investigators
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Association between exon-skipping therapy with eteplirsen and cardiac outcomes in Duchenne muscular dystrophy
err2025-08-19
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errJoel Iff; Isabelle Desguerre; Yunjuan Liu; Francois Sarkozy; Edward Tuttle; Francesco Muntoni; Craig M McDonald; Marie-Christine Nougues; Helge Amthor; Yi Zhong; Karim Wahbi
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Caregiver Global Impression Observations from EMBARK: A Phase 3 Study Evaluating Delandistrogene Moxeparvovec in Ambulatory Patients with Duchenne Muscular Dystrophy
err2024-11-26
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errMcdonald, Craig M.; Elkins, Jacob S.; Dharmarajan, Sai; Gooch, Katherine; Ciobanu, Teofil; Lansdall, Claire J.; Murphy, Alexander P.; Mcdougall, Fiona; Mercuri, Eugenio M.; Audhya, Ivana
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AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial
err2024-10-09
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errMendell, Jerry R.; Muntoni, Francesco; McDonald, Craig M.; Mercuri, Eugenio M.; Ciafaloni, Emma; Komaki, Hirofumi; Leon-Astudillo, Carmen; Nascimento, Andres; Proud, Crystal; Schara-Schmidt, Ulrike; Veerapandiyan, Aravindhan; Zaidman, Craig M.; Guridi, Maitea; Murphy, Alexander P.; Reid, Carol; Wandel, Christoph; Asher, Damon R.; Darton, Eddie; Mason, Stefanie; Potter, Rachael A.; Singh, Teji; Zhang, Wenfei; Fontoura, Paulo; Elkins, Jacob S.; Rodino-Klapac, Louise R.
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Factors Associated With Early Motor Function Trajectories in DMD After Glucocorticoid Initiation Post Hoc Analysis of the FOR-DMD Trial
err2024-05-28
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PREAI
errSchiava, Marianela; McDermott, Michael P.; Broomfield, Jonathan; Abrams, Keith R.; Mayhew, Anna G.; McDonald, Craig M.; Martens, William B.; Gregory, Stephanie J.; Griggs, Robert C.; Guglieri, Michela
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Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy
err2024-04-01
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errMendell, Jerry R.; Proud, Crystal; Zaidman, Craig M.; Mason, Stefanie; Darton, Eddie; Wang, Shufang; Wandel, Christoph; Murphy, Alexander P.; Mercuri, Eugenio; Muntoni, Francesco; Mcdonald, Craig M.
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Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy
err2024-03-12
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errDang, Utkarsh J.; Damsker, Jesse M.; Guglieri, Michela; Clemens, Paula R.; Perlman, Seth J.; Smith, Edward C.; Horrocks, Iain; Finkel, Richard S.; Mah, Jean K.; Deconinck, Nicolas; Goemans, Nathalie M.; Haberlova, Jana; Straub, Volker; Mengle-Gaw, Laurel; Schwartz, Benjamin D.; Harper, Amy; Shieh, Perry B.; De Waele, Liesbeth; Castro, Diana; Yang, Michele L.; Ryan, Monique M.; McDonald, Craig M.; Tulinius, Mar; Webster, Richard I.; Mcmillan, Hugh J.; Kuntz, Nancy; Rao, Vamshi K.; Baranello, Giovanni; Spinty, Stefan; Childs, Anne-Marie; Sbrocchi, Annie M.; Selby, Kathryn A.; Monduy, Migvis; Nevo, Yoram; Vilchez, Juan J.; Nascimento-Osorio, Andres; Niks, Erik H.; De Groot, Imelda J. M.; Katsalouli, Marina; van den Anker, John N.; Ward, Leanne M.; Leinonen, Mika; D'Alessandro, Andrea L.; Hoffman, Eric P.
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Draft Guidance for Industry Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and Related Dystrophinopathies - Developing Potential Treatments for the Entire Spectrum of Disease
err2024-02-13
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errMcDonald, Craig; Camino, Eric; Escandon, Rafael; Finkel, Richard S.; Fischer, Ryan; Flanigan, Kevin; Furlong, Pat; Juhasz, Rose; Martin, Ann S.; Villa, Chet; Sweeney, H. Lee
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Gait Event Detection and Travel Distance Using Waist-Worn Accelerometers across a Range of Speeds: Automated Approach
errSENSORS
IF3.5
err2024-02-09
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errRamli, Albara Ah; Liu, Xin; Berndt, Kelly; Chuah, Chen-Nee; Goude, Erica; Kaethler, Lynea B.; Lopez, Amanda; Nicorici, Alina; Owens, Corey; Rodriguez, David; Wang, Jane; Aranki, Daniel; Mcdonald, Craig M.; Henricson, Erik K.
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Findings from the Longitudinal CINRG Becker Natural History Study
err2023-11-17
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errClemens, Paula R.; Gordish-Dressman, Heather; Niizawa, Gabriela; Gorni, Ksenija; Guglieri, Michela; Connolly, Anne M.; Wicklund, Matthew; Bertorini, Tulio; Mah, Jean; Thangarajh, Mathula; Smith, Edward C.; Kuntz, Nancy L.; McDonald, Craig M.; Henricson, Erik; Upadhyayula, S.; Byrne, Barry; Manousakis, Georgios; Harper, Amy; Iannaccone, Susan; Dang, Utkarsh J.
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Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged=4 to <8?Years) with Duchenne Muscular Dystrophy: 1-Year Interim Results from Study SRP-9001-103 (ENDEAVOR)
err2023-09-07
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errZaidman, Craig M.; Proud, Crystal M.; Mcdonald, Craig M.; Lehman, Kelly J.; Goedeker, Natalie L.; Mason, Stefanie; Murphy, Alexander P.; Guridi, Maitea; Wang, Shufang; Reid, Carol; Darton, Eddie; Wandel, Christoph; Lewis, Sarah; Malhotra, Jyoti; Griffin, Danielle A.; Potter, Rachael A.; Rodino-Klapac, Louise R.; Mendell, Jerry R.
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Safety and Efficacy of Ataluren in nmDMD Patients from Study 041, a Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial
err2023-04-25
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PREAI
errMcDonald, Craig M.; Wu, Shiwen; Gulati, Sheffali; Komaki, Hirofumi; Escobar, Rosa E.; Kostera-Pruszczyk, Anna; Vlodavets, Dmitry; Chae, Jong-Hee; Jong, Yuh-Jyh; Karachunski, Peter; Statland, Jeffrey; Lorentzos, Michelle; Penematsa, Vinay; Chou, Connie; Lin, Min; Werner, Christian; Trifillis, Panayiota; Gordon, Gregory; Koladicz, Karyn; Mastrandrea, Nicholas; Klein, Matthew
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Ataluren Preserves Upper Limb Function in nmDMD Patients from Study 041, a Phase 3 Placebo-Controlled Trial, and the STRIDE Registry
err2023-04-25
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PREAI
errMcDonald, Craig M.; Mercuri, Eugenio; Muntoni, Francesco; Gordish-Dressman, Heather; Morgenroth, Lauren P.; De Resende, Maria Bernadete Dutra; Zhou, Shuizhen; Neeharika, Mathukumalli Lakshmi; Haginoya, Kazuhiro; Ramos-Platt, Leigh; Williams, Paula; Penematsa, Vinay; Chou, Connie; Lin, Min; Johnson, Shelley; Koladicz, Karyn; Mastrandrea, Nicholas; Werner, Christian; Trifillis, Panayiota
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