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Eric P. Hoffman

pharmacy and pharmaceutical sciences

113H-index
1.3KPaper Count
5.4WCitation Count
Published Papers 273
Publication Date
Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy
err2026-03-03
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errHanns Lochmüller; Hernan Gonorazky; Elisa Nigro; Jean K. Mah; Alberto Alemán; Amanda Yaworski; Maryam Oskoui; Anne Marie Sbrocchi; Kathryn Selby; Ana de Vera; Laura McAdam; Ekaterina Gresko; Aki Linden; Catherine Dutreix; Eric P. Hoffman
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Mineralocorticoid receptor antagonism of vamorolone: Evidence from LIONHEART and VISION-DMD clinical trials
err2025-11-01
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errde Vera, Ana; Clemens, Paula R.; Dang, Utkarsh J.; Dutreix, Catherine; Gresko, Ekaterina; Guglieri, Michela; Hagerty, Laura; Hasham, Shabir; Damsker, Jesse; Hathout, Yetrib; Linden, Aki; Berglund, Anders; Tobin, Rebecca; Wahbi, Karim; Hoffman, Eric P.
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Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4-to <7-year children
err2025-11-01
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errMummidivarpu, Swati; Dang, Utkarsh J.; Ziemba, Michael; Hathout, Yetrib; Clemens, Paula R.; Damsker, Jesse; Hagerty, Laura; Jusko, William J.; Smith, Edward C.; Mah, Jean K.; Guglieri, Michela; Nevo, Yoram; Kuntz, Nancy; Mcdonald, Craig M.; Ryan, Monique M.; Castro, Diana; Finkel, Richard S.; Conklin, Laurie S.; Mccall, John M.; Nagaraju, Kanneboyina; Van Den Anker, John; Hoffman, Eric P.
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Test-Retest Reliability of Motor Function and Myometry Outcomes From the Vamorolone Trials in Duchenne Muscular Dystrophy
err2025-10-01
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errTobin, Rebecca A.; Hoffman, Eric P.; Johnson, Linda; James, Meredith K.; Clemens, Paula R.; Dang, Utkarsh J.
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Association of DMD Gene Variant Classes With Motor Outcomes in a Drug Registration Clinical Trial Setting
err2025-04-01
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PREAI
errFang, Yuan; Dang, Utkarsh J.; Illei, Katherine I.; Clemens, Paula; Hoffman, Eric P.
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The effect of IL-1β inhibitor canakinumab (Ilaris®) on IL-6 production in human skeletal muscle cells
err2025-03-06
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errCordeiro-Santanach, Anna; Morales, Fiorella; Parquet, Maria del Carmen; Uaesoontrachoon, Kitipong; Rowsell, Joyce; Warford, Jordan; Wu, Wilson; Elustondo, Pia; Hoffman, Eric P.; Nagaraju, Kanneboyina
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Serum metabolomic signatures of patients with rare neurogenetic diseases: an insight into potential biomarkers and treatment targets
err2025-01-10
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errWijekoon, Nalaka; Gonawala, Lakmal; Ratnayake, Pyara; Sirisena, Darshana; Gunasekara, Harsha; Dissanayake, Athula; Amaratunga, Dhammika; Steinbusch, Harry W. M.; Hathout, Yetrib; Hoffman, Eric P.; Dalal, Ashwin; Mohan, Chandra; de Silva, K. Ranil D.
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Lung Cancer Burden in the SPIROMICS Cohort.
err2024-10-30
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PREAI
errBarjaktarevic, Igor; Bateman, Lori; Abtin, Fereidoun; Dubinett, Steven; Barr, R. Graham; Bhatt, Surya P.; Comellas, Alejandro; Cooper, Christopher B.; Curtis, Jeffrey; Dransfiend, Mark; Han, Meilan; Hansel, Nadia; Hoffman, Eric; Krishnan, Jerry A.; Marchetti, Nathaniel; Martinez, Fernando J.; Ohar, Jill; Ortega, Victor E.; Paine, Robert; Woodruff, Prescott; Tashkin, Donald P.; Bowler, Russell; Couper, David
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Adrenal Suppression From Vamorolone and Prednisone in Duchenne Muscular Dystrophy: Results From the Phase 2b Clinical Trial
err2024-08-04
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errAhmet, Alexandra; Tobin, Rebecca; Dang, Utkarsh J.; Rooman, Raoul; Guglieri, Michela; Clemens, Paula R.; Hoffman, Eric P.; Ward, Leanne M.
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Partners in vaccination: A community-based intervention to promote COVID-19 vaccination among low-income homebound and disabled adults
err2024-07-01
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PREAI
errKim, Sue E.; Turner, Barbara J.; Steinberg, Jane; Solano, Laura; Hoffman, Eric; Saluja, Sonali
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Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy
err2024-03-12
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errDang, Utkarsh J.; Damsker, Jesse M.; Guglieri, Michela; Clemens, Paula R.; Perlman, Seth J.; Smith, Edward C.; Horrocks, Iain; Finkel, Richard S.; Mah, Jean K.; Deconinck, Nicolas; Goemans, Nathalie M.; Haberlova, Jana; Straub, Volker; Mengle-Gaw, Laurel; Schwartz, Benjamin D.; Harper, Amy; Shieh, Perry B.; De Waele, Liesbeth; Castro, Diana; Yang, Michele L.; Ryan, Monique M.; McDonald, Craig M.; Tulinius, Mar; Webster, Richard I.; Mcmillan, Hugh J.; Kuntz, Nancy; Rao, Vamshi K.; Baranello, Giovanni; Spinty, Stefan; Childs, Anne-Marie; Sbrocchi, Annie M.; Selby, Kathryn A.; Monduy, Migvis; Nevo, Yoram; Vilchez, Juan J.; Nascimento-Osorio, Andres; Niks, Erik H.; De Groot, Imelda J. M.; Katsalouli, Marina; van den Anker, John N.; Ward, Leanne M.; Leinonen, Mika; D'Alessandro, Andrea L.; Hoffman, Eric P.
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Diagnostic outcome of pro bono neurogenetic diagnostic service in Sri Lanka: A wealth creation
err2024-01-23
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errGonawala, Lakmal; Wijekoon, Nalaka; Attanayake, Darshika; Ratnayake, Pyara; Sirisena, Darshana; Gunasekara, Harsha; Dissanayake, Athula; Keshavaraj, Ajantha; Mohan, Chandra; Steinbusch, Harry W. M.; Hoffman, Eric P.; Dalal, Ashwin; de Silva, K. Ranil D.
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A population-based study of children suggests blunted morning cortisol rhythms are associated with alterations of the systemic inflammatory state
err2024-01-01
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errRoy, Runia; Dang, Utkarsh J.; Huffman, Kim M.; Alayi, Tchilabalo; Hathout, Yetrib; Nagaraju, Kanneboyina; Visich, Paul S.; Hoffman, Eric P.
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Moving Beyond the 2018 Minimum International Care Considerations for Osteoporosis Management in Duchenne Muscular Dystrophy (DMD): Meeting Report from the 3rd International Muscle-Bone Interactions Meeting 7th and 14th November 2022
err2023-11-16
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errPhung, Kim; Crabtree, Nicola; Connolly, Anne M.; Furlong, Pat; Hoffman, Eric P.; Jackowski, Stefan A.; Jayash, Soher Nagi; Johnson, Alex; Koujok, Khaldoun; Munns, Craig F.; Niks, Erik; Rauch, Frank; Schrader, Rachel; Turner, Cathy; Vroom, Elizabeth; Weber, David R.; Wong, Brenda L.; Guglieri, Michela; Ward, Leanne M.; Wong, Sze Choong
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Duchenne Muscular Dystrophy from Brain to Muscle: The Role of Brain Dystrophin Isoforms in Motor Functions
err2023-08-29
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errWijekoon, Nalaka; Gonawala, Lakmal; Ratnayake, Pyara; Amaratunga, Dhammika; Hathout, Yetrib; Mohan, Chandra; Steinbusch, Harry W. M.; Dalal, Ashwin; Hoffman, Eric P.; de Silva, K. Ranil D.
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Integrated genomic, proteomic and cognitive assessment in Duchenne Muscular Dystrophy suggest astrocyte centric pathology
errHELIYON
IF3.6
err2023-08-01
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errWijekoon, Nalaka; Gonawala, Lakmal; Ratnayake, Pyara; Dissanayaka, Pulasthi; Gunarathne, Isuru; Amaratunga, Dhammika; Liyanage, Roshan; Senanayaka, Sunethra; Wijesekara, Saraji; Gunasekara, Hemal H.; Vanarsa, Kamala; Castillo, Jessica; Hathout, Yetrib; Dalal, Ashwin; Steinbusch, Harry W. M.; Hoffman, Eric; Mohan, Chandra; de Silva, K. Ranil D.
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