Not logged in Pathways to Leadership in Plastic Surgery: A Cross-sectional Study Villalvazo, Yadira; Zhang, Casey; Douglas, Nerone; Katana, Dzana; Humar, Pooja; Bengur, Fuat Baris; Vagonis, Alexandra; Glenney, Anne; Marra, Kacey G.; Huston, Tara L.; Butler, Paris D.; Myers, Paige L.; Rubin, J. Peter; Amalfi, Ashley; de la Cruz, Carolyn Share Save
Early Adversity and Socioeconomic Factors in Pediatric Multiple Sclerosis: A Case-Control Study Jensen, Sarah K. G.; Camposano, Susana; Berens, Anne; Waltz, Michael; Krupp, Lauren B.; Charvet, Leigh; Belman, Anita L.; Aaen, Gregory S.; Benson, Leslie A.; Candee, Meghan; Casper, Theron C.; Chitnis, Tanuja; Graves, Jennifer; Wheeler, Yolanda S.; Kahn, Ilana; Lotze, Timothy E.; Mar, Soe S.; Rensel, Mary; Rodriguez, Moses; Rose, John W.; Rubin, Jennifer P.; Tillema, Jan-Mendelt; Waldman, Amy T.; Weinstock-Guttman, Bianca; Barcellos, Lisa F.; Waubant, Emmanuelle; Gorman, Mark P. Share Save
Consensus guidelines for the monitoring and management of metachromatic leukodystrophy in the United States Adang, Laura A.; Bonkowsky, Joshua L.; Boelens, Jaap Jan; Mallack, Eric; Ahrens-Nicklas, Rebecca; Bernat, John A.; Bley, Annette; Burton, Barbara; Darling, Alejandra; Eichler, Florian; Eklund, Erik; Emrick, Lisa; Escolar, Maria; Fatemi, Ali; Fraser, Jamie L.; Gaviglio, Amy; Keller, Stephanie; Patterson, Marc C.; Orchard, Paul; Orthmann-Murphy, Jennifer; Santoro, Jonathan D.; Schoels, Ludger; Sevin, Caroline; Srivastava, Isha N.; Rajan, Deepa; Rubin, Jennifer P.; Van Haren, Keith; Wasserstein, Melissa; Zerem, Ayelet; Fumagalli, Francesca; Laugwitz, Lucia; Vanderver, Adeline Share Save
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Early transgene expression of GALC enzyme in a phase I/II safety, tolerability and efficacy study of PBKR03 in infants with early infantile Krabbe disease (EIKD) (GALax-C) Al-Zaidy, Samiah A.; Wolf, Nicole I.; Jones, Simon; Mallack, Eric J.; Waldman, Amy; Rubin, Jennifer P.; Bonkowsky, Joshua L.; Aran, Adi; Nii, Yan G.; Nagilla, Pruthvi; Donahue, Dan; Giugliani, Roberto; Forman, Mark S.; Bernard, Genevieve Share Save
Benefits of newborn screening and hematopoietic cell transplant in infantile Krabbe disease Page, Kristin M.; Ream, Margie A.; Rangarajan, Hemalatha G.; Galindo, Rafael; Mian, Ali Y.; Ho, Mai-Lan; Provenzale, James; Gustafson, Kathryn E.; Rubin, Jennifer; Shenoy, Shalini; Kurtzberg, Joanne Share Save
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A phase 1/2 open-label, multicenter, dose ranging and confirmatory study to assess the safety, tolerability and efficacy of PBKR03 administered to pediatric subjects with early infantile Krabbe disease (globoid cell leukodystrophy; GALax-C) Mallack, Eric J.; Jones, Simon A.; Aran, Adi; Bernard, Genevieve; Bonkowsky, Joshua L.; Giugliani, Roberto; Rubin, Jennifer P.; Waldman, Amy T.; Wolf, Nicole I.; de Wall, Steve; McNeil, Elizabeth Share Save
Association Between Time Spent Outdoors and Risk of Multiple Sclerosis Sebastian, Prince; Cherbuin, Nicolas; Barcellos, Lisa F.; Roalstad, Shelly; Casper, Charles; Hart, Janace; Aaen, Gregory S.; Krupp, Lauren; Benson, Leslie; Gorman, Mark; Candee, Meghan; Chitnis, Tanuja; Goyal, Manu; Greenberg, Benjamin; Mar, Soe; Rodriguez, Moses; Rubin, Jennifer; Schreiner, Teri; Waldman, Amy; Weinstock-Guttman, Bianca; Graves, Jennifer; Waubant, Emmanuelle; Lucas, Robyn Share Save
Familial History of Autoimmune Disorders Among Patients With Pediatric Multiple Sclerosis Greenberg, Benjamin M.; Casper, Theron Charles; Mar, Soe S.; Ness, Jayne M.; Plumb, Patricia; Liang, Shannon; Goyal, Manu; Weinstock-Guttman, Bianca; Rodriguez, Moses; Aaen, Gregory S.; Belman, Anita; Barcellos, Lisa F.; Rose, John W.; Gorman, Mark P.; Benson, Leslie A.; Candee, Meghan; Chitnis, Tanuja; Harris, Yolanda C.; Kahn, Ilana L.; Roalstad, Shelly; Hart, Janace; Lotze, Timothy E.; Rensel, Mary; Rubin, Jennifer P.; Schreiner, Teri L.; Tillema, Jan-Mendelt; Waldman, Amy Tara; Krupp, Lauren; Graves, Jennifer; Drake, Kaylea; Waubant, Emmanuelle Share Save
Consensus recommendations for the classification and long-term follow up of infants who screen positive for Krabbe Disease Thompson-Stone, Robert; Ream, Margie A.; Gelb, Michael; Matern, Dietrich; Orsini, Joseph J.; Levy, Paul A.; Rubin, Jennifer P.; Wenger, David A.; Burton, Barbara K.; Escolar, Maria L.; Kurtzberg, Joanne Share Save
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Aesthetic Surgery in Plastic Surgery Academia Perdikis, Galen; Eaves, Felmont F.; Glassman, Gabriella E.; Walker, Sallie; Huang, Li-Ching; Mast, Bruce; Damitz, Lynn; Rubin, J. Peter; Serletti, Joseph M.; Hansen, Juliana; Potochny, John; Kenkel, Jeffery; Taub, Peter J.; Sobczyk, Sara; Gilman, Robert H.; Saint-Cyr, Michel Hector; Cederna, Paul Share Save
miRNA contributions to pediatric-onset multiple sclerosis inferred from GWAS Rhead, Brooke; Shao, Xiaorong; Graves, Jennifer S.; Chitnis, Tanuja; Waldman, Amy T.; Lotze, Timothy; Schreiner, Teri; Belman, Anita; Krupp, Lauren; Greenberg, Benjamin M.; Weinstock-Guttman, Bianca; Aaen, Gregory; Tillema, Jan M.; Rodriguez, Moses; Hart, Janace; Caillier, Stacy; Ness, Jayne; Harris, Yolanda; Rubin, Jennifer; Candee, Meghan S.; Gorman, Mark; Benson, Leslie; Mar, Soe; Kahn, Ilana; Rose, John; Casper, T. Charles; Quach, Hong; Quach, Diana; Schaefer, Catherine; Waubant, Emmanuelle; Barcellos, Lisa F. Share Save
Admixture mapping reveals evidence of differential multiple sclerosis risk by genetic ancestry Chi, Calvin; Shao, Xiaorong; Rhead, Brooke; Gonzales, Edlin; Smith, Jessica B.; Xiang, Anny H.; Graves, Jennifer; Waldman, Amy; Lotze, Timothy; Schreiner, Teri; Weinstock-Guttman, Bianca; Aaen, Gregory; Tillema, Jan-Mendelt; Ness, Jayne; Candee, Meghan; Krupp, Lauren; Gorman, Mark; Benson, Leslie; Chitnis, Tanuja; Mar, Soe; Belman, Anita; Casper, Theron Charles; Rose, John; Moodley, Manikum; Rensel, Mary; Rodriguez, Moses; Greenberg, Benjamin; Kahn, Llana; Rubin, Jennifer; Schaefer, Catherine; Waubant, Emmanuelle; Langer-Gould, Annette; Barcellos, Lisa F. Share Save
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Several household chemical exposures are associated with pediatric-onset multiple sclerosis Mar, Soe; Liang, Shannon; Waltz, Michael; Casper, T. Charles; Goyal, Manu; Greenberg, Benjamin; Weinstock-Guttman, Bianca; Rodriguez, Moses; Aaen, Gregory; Belman, Anita; Barcellos, Lisa F.; Rose, John; Gorman, Mark; Benson, Leslie; Candee, Meghan; Chitnis, Tanjua; Harris, Yolanda; Kahn, Ilana; Roalsted, Shelly; Hart, Janace; Lotze, Timothy; Moodley, Manikum; Ness, Jayne; Rensel, Mary; Rubin, Jennifer; Schreiner, Teri; Tillema, Jan-Mendelt; Waldman, Amy; Krupp, Lauren; Graves, Jennifer S.; Waubant, Emmanuelle Share Save
Urban air quality and associations with pediatric multiple sclerosis Lavery, Amy M.; Waubant, Emmanuelle; Casper, T. Charles; Roalstad, Shelly; Candee, Meghan; Rose, John; Belman, Anita; Weinstock-Guttman, Bianca; Aaen, Greg; Tillema, Jan-Mendelt; Rodriguez, Moses; Ness, Jayne; Harris, Yolanda; Graves, Jennifer; Krupp, Lauren; Charvet, Leigh; Benson, Leslie; Gorman, Mark; Moodley, Manikum; Rensel, Mary; Goyal, Manu; Mar, Soe; Chitnis, Tanuja; Schreiner, Teri; Lotze, Tim; Greenberg, Benjamin; Kahn, Ilana; Rubin, Jennifer; Waldman, Amy T. Share Save