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Prime Editing for p47phox-Deficient Chronic Granulomatous Disease Gori, Jennifer L.; Haddad, Elie; Frangoul, Haydar; Kohn, Donald B.; Morris, Emma C.; Martin, Bradley N.; Deary, Briana A.; Nickerson, McKinley; Scholz, Rebecca L.; Fernandez, Isabel; Leveille, Karine; De Ravin, Suk See; Kang, Elizabeth M.; Pierzynski, Marie; Estwick, Tyra; Littel, Patricia; Kuhns, Douglas B.; Long Priel, Debra A.; Teira, Pierre; Turvey, Stuart; Arnold, Jordyn; Evans, Misty D.; McManus, Meghann; Carpenter, Ben; Waterman, David P.; Anzalone, Andrew V.; Petrusich, Alexandria; Osuna, Christa E.; O'Malley, Tiernan T.; Stewart-Ornstein, Jacob; Heath, Jack M.; Nehilla, Barrett J.; Asmal, Mohammed; Malech, Harry L. Share Save
Real-World Effectiveness of Nirmatrelvir-Ritonavir in Preventing Coronavirus Disease 2019-Associated Hospitalization: A Population-Based Cohort Study in the Province of Québec, Canada Kabore, Jean-Luc; Laffont, Benoit; Diop, Mamadou; Tardif, Melanie R.; Turgeon, Alexis F.; Dumaresq, Jeannot; Luong, Me-Linh; Cauchon, Michel; Chapdelaine, Hugo; Claveau, David; Brosseau, Marc; Haddad, Elie; Benigeri, Mike Share Save
Early-onset systemic lupus erythematosus-ANCA-associated vasculitis overlap syndrome caused by DNASE1L3 deficiency Triaille, Clement; Makita, Sohei; Cote, Kevin; Benoit, Genevieve; Campeau, Philippe M.; De Bruycker, Jean Jacques; Ra, Ai; McCord, Jon J.; Sayasith, Khampoun; Sutton, R. Bryan; Touzot, Fabien; Haddad, Elie; Reizis, Boris; Morin, Marie-Paule Share Save
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Pediatric COVID-19 severity by SARS-CoV-2 lineage and vaccine status in Canada: an IMPACT study Farrar, Daniel S.; Bettinger, Julie A.; Campigotto, Aaron J.; Deeks, Shelley L.; Drouin, Olivier; Embree, Joanne E.; Haddad, Elie; Halperin, Scott A.; Jadavji, Tajdin; Kazmi, Kescha; King, Melanie; Hepburn, Charlotte Moore; Papenburg, Jesse; Purewal, Rupeena; Sadarangani, Manish; Sauve, Laura; Yeung, Rae S. M.; Top, Karina A.; Kakkar, Fatima; Morris, Shaun K. Share Save
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Therapeutic Inducers of Natural Killer cell Killing (ThINKK): preclinical assessment of safety and efficacy in allogeneic hematopoietic stem cell transplant settings Poirier, Nicolas; Paquin, Valerie; Leclerc, Severine; Lisi, Veronique; Marmolejo, Carolina; Affia, Hicham; Cordeiro, Paulo; Theoret, Yves; Haddad, Elie; Andelfinger, Gregor; Lavallee, Vincent Philippe; Duval, Michel; Herblot, Sabine Share Save
Homozygous variant in TKFC abolishing triokinase activities is associated with isolated immunodeficiency Tremblay-Laganiere, Camille; Michaud, Coralie; Abourjaili-Bilodeau, Raphael; Cabezas, Alicia; Canales, Jose; Costas, Maria Jesus; Ribeiro, Joao M.; Leclerc-Blain, Jessica; Touzot, Fabien; Haddad, Elie; Teira, Pierre; Duval, Michel; Onoufriadis, Alexandros; Meunier, Brigitte; Cameselle, Jose Carlos; Campeau, Philippe M. Share Save
Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: A Primary Immune Deficiency Treatment Consortium study Grunebaum, Eyal; Arnold, Danielle E.; Logan, Brent; Parikh, Suhag; Marsh, Rebecca A.; Griffith, Linda M.; Mallhi, Kanwaldeep; Chellapandian, Deepak; Lim, Stephanie Si; Deal, Christin L.; Kapoor, Neena; Murguia-Favela, Luis; Falcone, Emilia Liana; Prasad, Vinod K.; Touzot, Fabien; Bleesing, Jack J.; Chandrakasan, Shanmuganathan; Heimall, Jennifer R.; Bednarski, Jeffrey J.; Broglie, Larisa A.; Chong, Hey Jin; Kapadia, Malika; Prockop, Susan; Saldana, Blachy J. Davila; Schaefer, Edo; Bauchat, Andrea L.; Teira, Pierre; Chandra, Sharat; Parta, Mark; Cowan, Morton J.; Dvorak, Christopher C.; Haddad, Elie; Kohn, Donald B.; Notarangelo, Luigi D.; Pai, Sung-Yun; Puck, Jennifer M.; Pulsipher, Michael A.; Torgerson, Troy R.; Malech, Harry L.; Kang, Elizabeth M.; Leiding, Jennifer W. Share Save
CRISPR Screens Identify Key Regulators of NK Cell Cytotoxicity in Cancer Therapy Rethacker, Louise; Romero, Hugo; Dulong, Joshua; Sasseville, Marc; Lalonde, Marie-Eve; Gadoury, Christine; Beland, Kathie; Beausejour, Christian; Marcotte, Richard; Haddad, Elie Share Save
Developmental role of macrophages modeled in human pluripotent stem cell-derived intestinal tissue Song, Andrew T.; Sindeaux, Renata H. M.; Li, Yuanyi; Affia, Hicham; Agnihotri, Tapan; Leclerc, Severine; van Vliet, Patrick Piet; Colas, Mathieu; Guimond, Jean-Victor; Patey, Natalie; Feulner, Lara; Joyal, Jean-Sebastien; Haddad, Elie; Barreiro, Luis; Andelfinger, Gregor Share Save
Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study Eissa, Hesham; Thakar, Monica S.; Shah, Ami J.; Logan, Brent R.; Griffith, Linda M.; Dong, Huaying; Parrott, Roberta E.; O'Reilly, Richard J.; Dara, Jasmeen; Kapoor, Neena; Satter, Lisa Forbes; Chandra, Sharat; Kapadia, Malika; Chandrakasan, Shanmuganathan; Knutsen, Alan; Jyonouchi, Soma C.; Molinari, Lyndsay; Rayes, Ahmad; Ebens, Christen L.; Teira, Pierre; Saldana, Blachy J. Davila; Burroughs, Lauri M.; Chaudhury, Sonali; Chellapandian, Deepak; Gillio, Alfred P.; Goldman, Fredrick; Malech, Harry L.; DeSantes, Kenneth; Cuvelier, Geoff D. E.; Rozmus, Jacob; Quinones, Ralph; Yu, Lolie C.; Broglie, Larisa; Aquino, Victor; Shereck, Evan; Moore, Theodore B.; Vander Lugt, Mark T.; Mousallem, Talal I.; Oved, Joeseph H.; Dorsey, Morna; Abdel-Azim, Hisham; Martinez, Caridad; Bleesing, Jacob H.; Prockop, Susan; Kohn, Donald B.; Bednarski, Jeffrey J.; Leiding, Jennifer; Marsh, Rebecca A.; Torgerson, Troy; Notarangelo, Luigi D.; Pai, Sung-Yun; Pulsipher, Michael A.; Puck, Jennifer M.; Dvorak, Christopher C.; Haddad, Elie; Buckley, Rebecca H.; Cowan, Morton J.; Heimall, Jennifer Share Save
Intestinal microbiome and metabolome signatures in patients with chronic granulomatous disease Chandrasekaran, Prabha; Han, Yu; Zerbe, Christa S.; Heller, Theo; DeRavin, Suk See; Kreuzberg, Samantha A.; Marciano, Beatriz E.; Siu, Yik; Jones, Drew R.; Abraham, Roshini S.; Stephens, Michael C.; Tsou, Amy M.; Snapper, Scott; Conlan, Sean; Subramanian, Poorani; Quinones, Mariam; Grou, Caroline; Calderon, Virginie; Deming, Clayton; Leiding, Jennifer W.; Arnold, Danielle E.; Logan, Brent R.; Griffith, Linda M.; Petrovic, Aleksandra; Mousallem, Talal I.; Kapoor, Neena; Heimall, Jennifer R.; Barnum, Jessie L.; Kapadia, Malika; Wright, Nicola; Rayes, Ahmad; Chandra, Sharat; Broglie, Larisa A.; Chellapandian, Deepak; Deal, Christin L.; Grunebaum, Eyal; Lim, Stephanie Si; Mallhi, Kanwaldeep; Marsh, Rebecca A.; Murguia-Favela, Luis; Parikh, Suhag; Touzot, Fabien; Cowan, Morton J.; Dvorak, Christopher C.; Haddad, Elie; Kohn, Donald B.; Notarangelo, Luigi D.; Pai, Sung-Yun; Puck, Jennifer M.; Pulsipher, Michael A.; Torgerson, Troy R.; Kang, Elizabeth M.; Malech, Harry L.; Segre, Julia A.; Bryant, Clare E.; Holland, Steven M.; Falcone, Emilia Liana Share Save
Case report: Success of allogeneic hematopoietic stem cell transplantation for refractory systemic-onset juvenile idiopathic arthritis Beaufils, Camille; Proulx, Catherine; Blincoe, Annaliesse; Teira, Pierre; Bittencourt, Henrique; Cellot, Sonia; Duval, Michel; Morin, Marie-Paule; De Bruycker, Jean Jacques; Couture, Julie; Samaan, Kathryn; Decaluwe, Helene; Kleiber, Niina; El-Jalbout, Ramy; Touzot, Fabien; Haddad, Elie; Barsalou, Julie Share Save
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