Not logged in Frailty phenotype in adults with sickle cell disease Oyedeji, Charity, I; Mohamed, Rania E.; Faldowski, Richard; Callaway, Teagan; Poole, Tamara; Oliva, Francyess Denis; Mathis, Veronica; Subramaniam, Arvind; Whitson, Heather; Reeve, Bryce B.; Pieper, Carl; Telen, Marilyn J.; Ashley-Koch, Allison; Cohen, Harvey J.; Hall, Katherine; Strouse, John J. Share Save
Targeting PIEZO1-TMEM16F Coupling to Mitigate Sickle Cell Disease Complications Liang, Pengfei; Wan, Yui-Chun S.; Shan, Ke Z.; Chou, Ryan; Zhang, Yang; Delahunty, Martha; Khandelwal, Sanjay; Francis, Samuel J.; Arepally, Gowthami M.; Telen, Marilyn J.; Yang, Huanghe Share Save
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A replication study of novel fetal hemoglobin-associated genetic variants in sickle cell disease-only cohorts Ilboudo, Yann; Brosseau, Nicolas; Lo, Ken Sin; Belhaj, Hicham; Moutereau, Stephane; Marshall, Kwesi; Reid, Marvin; Kutlar, Abdullah; Ashley-Koch, Allison E.; Telen, Marilyn J.; Joly, Philippe; Galacteros, Frederic; Bartolucci, Pablo; Lettre, Guillaume Share Save
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Whole-genome sequencing in 333,100 individuals reveals rare non-coding single variant and aggregate associations with height Hawkes, Gareth; Beaumont, Robin N.; Li, Zilin; Mandla, Ravi; Li, Xihao; Albert, Christine M.; Arnett, Donna K.; Ashley-Koch, Allison E.; Ashrani, Aneel A.; Barnes, Kathleen C.; Boerwinkle, Eric; Brody, Jennifer A.; Carson, April P.; Chami, Nathalie; Chen, Yii-Der Ida; Chung, Mina K.; Curran, Joanne E.; Darbar, Dawood; Ellinor, Patrick T.; Fornage, Myrian; Gordeuk, Victor R.; Guo, Xiuqing; He, Jiang; Hwu, Chii-Min; Kalyani, Rita R.; Kaplan, Robert; Kardia, Sharon L. R.; Kooperberg, Charles; Loos, Ruth J. F.; Lubitz, Steven A.; Minster, Ryan L.; Naseri, Take; Viali, Satupa'itea; Mitchell, Braxton D.; Murabito, Joanne M.; Palmer, Nicholette D.; Psaty, Bruce M.; Redline, Susan; Shoemaker, M. Benjamin; Silverman, Edwin K.; Telen, Marilyn J.; Weiss, Scott T.; Yanek, Lisa R.; Zhou, Hufeng; Liu, Ching-Ti; North, Kari E.; Justice, Anne E.; Locke, Jonathan M.; Owens, Nick; Murray, Anna; Patel, Kashyap; Frayling, Timothy M.; Wright, Caroline F.; Wood, Andrew R.; Lin, Xihong; Manning, Alisa; Weedon, Michael N. Share Save
Black Americans With Sickle Cell Disease (SCD) Demonstrate Accelerated Epigenetic Pace of Aging Compared to Black Americans Without SCD Garrett, Melanie E.; Le, Brandon; Bourassa, Kyle J.; Dennis, Michelle F.; Hatch, Daniel; Yang, Qing; Tanabe, Paula; Shah, Nirmish; Luyster, Faith S.; Oyedeji, Charity; Strouse, John J.; Cohen, Harvey J.; Kimbrel, Nathan A.; Beckham, Jean C.; Knisely, Mitchell R.; Telen, Marilyn J.; Ashley-Koch, Allison E.; Aurora, Pallavi; Calhoun, Patrick S.; Dedert, Eric; Elbogen, Eric B.; Halverson, Tate F.; Hurley, Robin A.; Kilts, Jason D.; Kirby, Angela; Magnante, Anna T.; Martindale, Sarah L.; Martinez, Brandy S.; Marx, Christine E.; McDonald, Scott D.; Moore, Scott D.; O'Connor, Victoria; Morey, Rajendra A.; Naylor, Jennifer C.; Rowland, Jared; Shura, Robert D.; Swinkels, Cindy; Van Voorhees, Elizabeth E.; Wagner, H. Ryan Share Save
Multicenter, phase 1 study of etavopivat (FT-4202) treatment for up to 12 weeks in patients with sickle cell disease Saraf, Santosh L.; Hagar, Robert; Idowu, Modupe; Osunkwo, Ifeyinwa; Cruz, Kimberly; Kuypers, Frans A.; Brown, R. Clark; Geib, James; Ribadeneira, Maria; Schroeder, Patricia; Wu, Eric; Forsyth, Sanjeev; Kelly, Patrick F.; Kalfa, Theodosia A.; Telen, Marilyn J. Share Save
Standard Compared With Extended Red Blood Cell Antigen Matching for Prevention of Subsequent Hemolytic Disease of the Fetus and Newborn Sugrue, Ronan P.; Olsen, Jaxon; Abi Antoun, Marie Elise; Skalla, Lesley A.; Cate, Jennifer; James, Andra H.; Stonehill, Alexandra; Watkins, Virginia; Telen, Marilyn J.; Federspiel, Jerome J. Share Save
Validation of human telomere length multi-ancestry meta-analysis association signals identifies POP5 and KBTBD6 as human telomere length regulation genes Keener, Rebecca; Chhetri, Surya B.; Connelly, Carla J.; Taub, Margaret A.; Conomos, Matthew P.; Weinstock, Joshua; Ni, Bohan; Strober, Benjamin; Aslibekyan, Stella; Auer, Paul L.; Barwick, Lucas; Becker, Lewis C.; Blangero, John; Bleecker, Eugene R.; Brody, Jennifer A.; Cade, Brian E.; Celedon, Juan C.; Chang, Yi-Cheng; Cupples, L. Adrienne; Custer, Brian; Freedman, Barry I.; Gladwin, Mark T.; Heckbert, Susan R.; Hou, Lifang; Irvin, Marguerite R.; Isasi, Carmen R.; Johnsen, Jill M.; Kenny, Eimear E.; Kooperberg, Charles; Minster, Ryan L.; Naseri, Take; Viali, Satupa'itea; Nekhai, Sergei; Pankratz, Nathan; Peyser, Patricia A.; Taylor, Kent D.; Telen, Marilyn J.; Wu, Baojun; Yanek, Lisa R.; Yang, Ivana V.; Albert, Christine; Arnett, Donna K.; Ashley-Koch, Allison E.; Barnes, Kathleen C.; Bis, Joshua C.; Blackwell, Thomas W.; Boerwinkle, Eric; Burchard, Esteban G.; Carson, April P.; Chen, Zhanghua; Chen, Yii-Der Ida; Darbar, Dawood; de Andrade, Mariza; Ellinor, Patrick T.; Fornage, Myriam; Gelb, Bruce D.; Gilliland, Frank D.; He, Jiang; Islam, Talat; Kaab, Stefan; Kardia, Sharon L. R.; Kelly, Shannon; Konkle, Barbara A.; Kumar, Rajesh; Loos, Ruth J. F.; Martinez, Fernando D.; McGarvey, Stephen T.; Meyers, Deborah A.; Mitchell, Braxton D.; Montgomery, Courtney G.; North, Kari E.; Palmer, Nicholette D.; Peralta, Juan M.; Raby, Benjamin A.; Redline, Susan; Rich, Stephen S.; Roden, Dan; Rotter, Jerome I.; Ruczinski, Ingo; Schwartz, David; Sciurba, Frank; Shoemaker, M. Benjamin; Silverman, Edwin K.; Sinner, Moritz F.; Smith, Nicholas L.; Smith, Albert V.; Tiwari, Hemant K.; Vasan, Ramachandran S.; Weiss, Scott T.; Williams, L. Keoki; Zhang, Yingze; Ziv, Elad; Raffield, Laura M.; Reiner, Alexander P.; Arvanitis, Marios; Greider, Carol W.; Mathias, Rasika A.; Battle, Alexis Share Save
Riociguat in patients with sickle cell disease and hypertension or proteinuria (STERIO-SCD): a randomised, double-blind, placebo controlled, phase 1-2 trial Gladwin, Mark T.; Gordeuk, Victor R.; Desai, Payal C.; Minniti, Caterina; Novelli, Enrico M.; Morris, Claudia R.; Ataga, Kenneth, I; De Castro, Laura; Curtis, Susanna A.; El Rassi, Fuad; Ford, Hubert James; Harrington, Thomas; Klings, Elizabeth S.; Lanzkron, Sophie; Liles, Darla; Little, Jane; Nero, Alecia; Smith, Wally; Taylor, James G.; Baptiste, Ayanna; Hagar, Ward; Kanter, Julie; Kinzie, Amy; Martin, Temeia; Rafique, Amina; Telen, Marilyn J.; Lalama, Christina M.; Kato, Gregory J.; Abebe, Kaleab Z. Share Save
Preferences for potential benefits and risks for gene therapy in the treatment of sickle cell disease Sepulveda, Juan Marcos Gonzalez; Yang, Jui-Chen; Reed, Shelby D.; Lee, Ting-Hsuan; Ng, Xinyi; Stothers, Sarah; Irony, Telba; Ho, Martin; Rothman, Jennifer A.; Badawy, Sherif; Rowley, Carolyn; Little, Jane; Shah, Nirmish R.; Li, Kaiwen; Telen, Marilyn J. Share Save
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Differences in the Circulating Proteome in Individuals with versus without Sickle Cell Trait Cai, Yanwei; Franceschini, Nora; Surapaneni, Aditya; Garrett, Melanie E.; Tahir, Usman A.; Hsu, Li; Telen, Marilyn J.; Yu, Bing; Tang, Hua; Li, Yun; Liu, Simin; Gerszten, Robert E.; Coresh, Josef; Manson, JoAnn E.; Wojcik, Genevieve L.; Kooperberg, Charles; Auer, Paul L.; Foster, Matthew W.; Grams, Morgan E.; Ashley-Koch, Allison E.; Raffield, Laura M.; Reiner, Alex P. Share Save
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Multi-ancestry transcriptome-wide association analyses yield insights into tobacco use biology and drug repurposing Chen, Fang; Wang, Xingyan; Jang, Seon-Kyeong; Quach, Bryan C.; Weissenkampen, J. Dylan; Khunsriraksakul, Chachrit; Yang, Lina; Sauteraud, Renan; Albert, Christine M.; Allred, Nicholette D. D.; Arnett, Donna K.; Ashley-Koch, Allison E.; Barnes, Kathleen C.; Barr, R. Graham; Becker, Diane M.; Bielak, Lawrence F.; Bis, Joshua C.; Blangero, John; Boorgula, Meher Preethi; Chasman, Daniel I.; Chavan, Sameer; Chen, Yii-Der I.; Chuang, Lee-Ming; Correa, Adolfo; Curran, Joanne E.; David, Sean P.; de las Fuentes, Lisa; Deka, Ranjan; Duggirala, Ravindranath; Faul, Jessica D.; Garrett, Melanie E.; Gharib, Sina A.; Guo, Xiuqing; Hall, Michael E.; Hawley, Nicola L.; He, Jiang; Hobbs, Brian D.; Hokanson, John E.; Hsiung, Chao A.; Hwang, Shih-Jen; Hyde, Thomas M.; Irvin, Marguerite R.; Jaffe, Andrew E.; Johnson, Eric O.; Kaplan, Robert; Kardia, Sharon L. R.; Kaufman, Joel D.; Kelly, Tanika N.; Kleinman, Joel E.; Kooperberg, Charles; Lee, I-Te; Levy, Daniel; Lutz, Sharon M.; Manichaikul, Ani W.; Martin, Lisa W.; Marx, Olivia; McGarvey, Stephen T.; Minster, Ryan L.; Moll, Matthew; Moussa, Karine A.; Naseri, Take; North, Kari E.; Oelsner, Elizabeth C.; Peralta, Juan M.; Peyser, Patricia A.; Psaty, Bruce M.; Rafaels, Nicholas; Raffield, Laura M.; Reupena, Muagututi'a Sefuiva; Rich, Stephen S.; Rotter, Jerome I.; Schwartz, David A.; Shadyab, Aladdin H.; Sheu, Wayne H-H.; Sims, Mario; Smith, Jennifer A.; Sun, Xiao; Taylor, Kent D.; Telen, Marilyn J.; Watson, Harold; Weeks, Daniel E.; Weir, David R.; Yanek, Lisa R.; Young, Kendra A.; Young, Kristin L.; Zhao, Wei; Hancock, Dana B.; Jiang, Bibo; Vrieze, Scott; Liu, Dajiang J. Share Save
Sex differences in progression of kidney disease in sickle cell disease Ataga, Kenneth I.; Zhou, Qingning; Saraf, Santosh L.; Hankins, Jane S.; Ciccone, Emily J.; Loehr, Laura R.; Garrett, Melanie E.; Ashley-Koch, Allison E.; Cai, Jianwen; Telen, Marilyn J.; Derebail, Vimal K. Share Save
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Design, Synthesis, and Investigation of Novel Nitric Oxide (NO)-Releasing Aromatic Aldehydes as Drug Candidates for the Treatment of Sickle Cell Disease Huang, Boshi; Ghatge, Mohini S.; Donkor, Akua K.; Musayev, Faik N.; Deshpande, Tanvi M.; Al-Awadh, Mohammed; Alhashimi, Rana T.; Zhu, Hongmei; Omar, Abdelsattar M.; Telen, Marilyn J.; Zhang, Yan; McMahon, Tim J.; Abdulmalik, Osheiza; Safo, Martin K. Share Save