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Dabrafenib in pediatric patients with BRAF V600 mutation-positive high-grade glioma: Results from a phase 1/2a single-arm study Geoerger, Birgit; Moreno, Lucas; Bouffet, Eric; Upadhyaya, Santhosh A.; Andre, Nicolas; Aerts, Isabelle; Plant-Fox, Ashley S.; Roughton, Michael; Russo, Mark; Hargrave, Darren Share Save
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Patient-derived models of ER+HER2-metastatic breast cancers reveal KRAS-MAPK signalling pathway as therapeutic target for overcoming resistance to trastuzumab-deruxtecan Marangoni, E.; El-Botty, L.; Montaudon, E.; Darrien, H.; Dahmani, A.; Sourd, L.; Champenois, G.; Nicolas, A.; Dutertre, G.; Vincent-Salomon, A.; Courtois, L.; Planchon, J. Masliah; Bieche, I.; Coussy, F.; Cabel, L. Share Save
Precision cancer medicine platform trials: Concepts and design of AcSe-ESMART Geoerger, Birgit; Bautista, Francisco; Andre, Nicolas; Berlanga, Pablo; Gatz, Susanne A.; Marshall, Lynley V.; Rubino, Jonathan; Archambaud, Baptiste; Marchais, Antonin; Rubio-San-Simon, Alba; Ducassou, Stephane; Zwaan, C. Michel; Casanova, Michela; Nysom, Karsten; Pellegrino, Sophie; Hoog-Labouret, Natalie; Buzyn, Agnes; Blanc, Patricia; Paoletti, Xavier; Vassal, Gilles Share Save
Postzygotic mosaicism of SMARCB1 variants in patients with rhabdoid tumors: A not-so-rare condition exposing to successive tumors Thomson, Gregory; Filser, Mathilde; Guerrini-Rousseau, Lea; Tauziede-Espariat, Arnault; Bourneix, Christine; Gauthier-Villars, Marion; Simaga, Fatoumata; Beccaria, Kevin; Faure-Conter, Cecile; Maureille, Aurelien; Zattara-Cannoni, Helene; Andre, Nicolas; Entz-Werle, Natacha; Brugieres, Laurence; Mansuy, Ludovic; Denizeau, Philippe; Julia, Sophie; Ingster, Olivier; Lejeune, Sophie; Brahimi, Afane; Coupier, Isabelle; Bonadona, Valerie; Delattre, Olivier; Masliah-Planchon, Julien; Bourdeaut, Franck Share Save
ETMR-27. ANTI-ANGIOGENIC METRONOMIC THERAPY OF RARE TUMOURS OF THE CENTRAL NERVOUS SYSTEM Schned, Hannah; Haberler, Christine; Peyrl, Andreas; Azizi, Amedeo; Mayr, Lisa; Aistleitner, Barbara; von Hoff, Katja; Kool, Marcel; Kjaersgaard, Mimi; Trkova, Katerina; Andre, Nicolas; Lippolis, Maria Aliotti; Hedrich, Cora; Koeller, Clara; Stepien, Natalia; Slavc, Irene; Gojo, Johannes Share Save
EFFICACY AND SAFETY OF ENTRECTINIB IN CHILDREN WITHNTRK ORROS1 FUSION-POSITIVE (FP) PRIMARY CENTRAL NERVOUS SYSTEM (CNS) TUMORS Bagchi, Aditi; Robinson, Giles W.; Desai, Ami, V; Wu, Yeming; Wang, Huanmin; Basu, Ellen M.; Casanova, Michela; van Tilburg, Cornelis M.; Campbell-Hewson, Quentin; Armstrong, Amy E.; Andre, Nicolas; Devlin, Clare; Wulff, Jade; Cardenas, Alison; Hutchinson, Katherine E.; Lian, Qinshu; Ryklansky, Carolina; Harmach, Vesna Sneller; Fox, Elizabeth; Gajjar, Amar Share Save
RETROSPECTIVE ANALYSIS OF 271 RELAPSED AND REFRACTORY ATYPICAL TERATOID RHABDOID TUMORS - COMBING DATA FROM INTERNATIONAL COHORTS IN A COLLABORATIVE EFFORT Steinbuegl, Mona; Rosenberg, Tom; Desai, Kavita; Govender, Dinisha; Liu, Anthony Pak Yin; Andre, Nicolas; O'Hare, Patricia; Nysom, Karsten; Bourdeaut, Franck; Fisher, Michael J.; Margol, Ashley; Reddy, Alyssa T.; Fruehwald, Michael C. Share Save
Clinical trial inclusion in patients with relapsed/refractory neuroblastoma following the European Precision Cancer Medicine trial MAPPYACTS Chaix, Jordane; Schleiermacher, Gudrun; Corradini, Nadege; Andre, Nicolas; Thebaud, Estelle; Gambarth, Marion; Defachelles, Anne-Sophie; Entz-Werlej, Natacha; Chastagner, Pascal; De Carli, Emilie; Ducassou, Stephane; Landman-Parker, Judith; Adam-de-Beaumais, Tiphaine; Larive, Alicia; Michiels, Stefan; Vassal, Gilles; Valteau-Couanet, Dominique; Geoerger, Birgit; Berlanga, Pablo Share Save
A novel bioinformatic approach reveals cooperation between Cancer/Testis genes in basal-like breast tumors Laisne, Marthe; Rodgers, Brianna; Benlamara, Sarah; Wicinski, Julien; Nicolas, Andre; Djerroudi, Lounes; Gupta, Nikhil; Ferry, Laure; Kirsh, Olivier; Daher, Diana; Philippe, Claude; Okada, Yuki; Charafe-Jauffret, Emmanuelle; Cristofari, Gael; Meseure, Didier; Vincent-Salomon, Anne; Ginestier, Christophe; Defossez, Pierre-Antoine Share Save
METRO-PD1: Phase 1 study of nivolumab in combination with metronomic chemotherapy in children and adolescents with relapsing/refractory solid tumors Andre, Nicolas; Le Deley, Marie Cecile; Leguillette, Clemence; Probst, Alicia; Willems, Leen; Travers, Romain; Aerts, Isabelle; Faure-Conter, Cecile; Revond-Riviere, Gabriel; Min, Victoria; Geoerger, Birgit; Chastagner, Pascal; Entz-Werle, Natascha; Leblond, Pierre Share Save
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AcSé-ESMART, a European precision cancer medicine proof-of-concept platform trial Geoerger, Birgit; Paoletti, Xavier; Bautista, Francisco; Gatz, Susanne A.; Marshall, Lynley V.; Andre, Nicolas; Berlanga, Pablo; Ducassou, Stephane; Pasqualini, Claudia; Casanova, Michela; Zwaan, C. Michel; Nysom, Karsten; Rubino, Jonathan; Vuillier-Le Goff, Delphine; Archambaud, Baptiste; Abbou, Samuel; Schleiermacher, Gudrun; Dufour, Christelle; Blanc, Patricia; Hoog-Labouret, Natalie; Buzyn, Agnes; Vassal, Gilles Share Save
Combination drug screen targeting glioblastoma core vulnerabilities reveals pharmacological synergisms Ariey-Bonnet, Jeremy; Berges, Raphael; Montero, Marie-Pierre; Mouysset, Baptiste; Piris, Patricia; Muller, Kevin; Pinna, Guillaume; Failes, Tim W.; Arndt, Greg M.; Morando, Philippe; Baeza-Kallee, Nathalie; Colin, Carole; Chinot, Olivier; Braguer, Diane; Morelli, Xavier; Andre, Nicolas; Carre, Manon; Tabouret, Emeline; Figarella-Branger, Dominique; Le Grand, Marion; Pasquier, Eddy Share Save
Multi-omics comparison of malignant and normal uveal melanocytes reveals molecular features of uveal melanoma Gentien, David; Saberi-Ansari, Elnaz; Servant, Nicolas; Jolly, Ariane; de la Grange, Pierre; Nemati, Fariba; Liot, Geraldine; Saule, Simon; Teissandier, Aurelie; Bourc'his, Deborah; Girard, Elodie; Wong, Jennifer; Masliah-Planchon, Julien; Narmanli, Erkan; Liu, Yuanlong; Torun, Emma; Goulancourt, Rebecca; Rodrigues, Manuel; Gaude, Laure Villoing; Reyes, Cecile; Bazire, Mateo; Chenegros, Thomas; Henry, Emilie; Rapinat, Audrey; Bohec, Mylene; Baulande, Sylvain; M'kacher, Radhia; Jeandidier, Eric; Nicolas, Andre; Ciriello, Giovanni; Margueron, Raphael; Decaudin, Didier; Cassoux, Nathalie; Piperno-Neumann, Sophie; Stern, Marc-Henri; Gibcus, Johan Harmen; Dekker, Job; Heard, Edith; Roman-Roman, Sergio; Waterfall, Joshua J. Share Save