Not logged in EndoCompass Project: Research Roadmap for Growth Disorders Gevers, Evelien F.; Hokken-Koelega, Anita C.; Tauber, Maithe; Binder, Gerhard; Bochukova, Elena G.; Bouret, Sebastien G.; Caixas, Assumpta; Davies, Justin H.; Dauber, Andrew; Edouard, Thomas; Eggermann, Thomas; Giabicani, Eloise; Netchine, Irene; Nilsson, Ola; Saravinovska, Kristina; van der Steen, Manouk; Tartaglia, Marco; Tatton-Brown, Katrina; Temple, I. Karen; Yart, Armelle; Zenker, Martin Share Save
EndoCompass project: research roadmap for growth disorders Gevers, Evelien F.; Hokken-Koelega, Anita C.; Tauber, Maithe; Binder, Gerhard; Bochukova, Elena G.; Bouret, Sebastien G.; Caixas, Assumpta; Davies, Justin H.; Dauber, Andrew; Edouard, Thomas; Eggermann, Thomas; Giabicani, Eloise; Netchine, Irene; Nilsson, Ola; Saravinovska, Kristina; van der Steen, Manouk; Tartaglia, Marco; Tatton-Brown, Katrina; Temple, I. Karen; Yart, Armelle; Zenker, Martin Share Save
A First-in-Human, phase I/IIa trial of the novel T cell immunotherapy pTTL in patients with advanced colorectal cancer Tarfy, Ahmed; Chabok, Abbas; Nikberg, Maziar; Nilsson, Per; Kordes, Maximilia; Carlsten, Mattias; Joly, Anne-Laure; Berglund, Sofia; Nilsson, Ola; Salmen, Andrea; Svensson, Samuel; Norlen, Per; Gafvelin, Guro; Gronlund, Hans Share Save
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Short stature, brachydactyly and joint contractures associated with novel FBN2 variants in two families Loid, Petra; Wang, Fan; Lennartsson, Otto; Muurinen, Mari; Costantini, Alice; Vats, Sakshi; Lodefalk, Maria; Nilsson, Ola; Makitie, Outi Share Save
Real-world non-interventional post-authorization safety study of long-term use of burosumab in children and adolescents with X-linked hypophosphatemia: first interim analysis Boot, Annemieke M.; Ariceta, Gema; Beck-Nielsen, Signe Sparre; Brandi, Maria Luisa; Briot, Karine; Collantes, Carmen de Lucas; Giannini, Sandro; Haffner, Dieter; Keen, Richard; Levtchenko, Elena; Mughal, M. Zulf; Makitie, Outi; Nilsson, Ola; Schnabel, Dirk; Tripto-Shkolnik, Liana; Zillikens, M. Carola; Liu, Jonathan; Tudor, Alina; Emma, Francesco Share Save
Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period Ward, Leanne M.; Hoegler, Wolfgang; Glorieux, Francis H.; Portale, Anthony A.; Whyte, Michael P.; Munns, Craig F.; Nilsson, Ola; Simmons, Jill H.; Padidela, Raja; Namba, Noriyuki; Cheong, Hae, II; Sochett, Etienne; Muroya, Koji; Tanaka, Hiroyuki; Pitukcheewanont, Pisit; Gottesman, Gary S.; Biggin, Andrew; Perwad, Farzana; Chen, Angel; Merritt, John Lawrence; Imel, Erik A. Share Save
PLS3 Mutations in X-Linked Osteoporosis: Clinical and Genetic Features in Five New Families Costa, Adriana; Martins, Andreia; Machado, Catarina; Lundberg, Elena; Nilsson, Ola; Wang, Fan; Costantini, Alice; Tournis, Symeon; Hoeppner, Jakob; Grasemann, Corinna; Maekitie, Outi Share Save
The International X-Linked Hypophosphatemia (XLH) Registry: first interim analysis of baseline demographic, genetic and clinical data Ariceta, Gema; Beck-Nielsen, Signe Sparre; Boot, Annemieke M.; Brandi, Maria Luisa; Briot, Karine; Collantes, Carmen de Lucas; Emma, Francesco; Giannini, Sandro; Haffner, Dieter; Keen, Richard; Levtchenko, Elena; Makitie, Outi; Mughal, M. Zulf; Nilsson, Ola; Schnabel, Dirk; Tripto-Shkolnik, Liana; Liu, Jonathan; Williams, Angela; Wood, Sue; Zillikens, M. Carola Share Save
Real-world evidence in achondroplasia: considerations for a standardized data set Alanay, Yasemin; Mohnike, Klaus; Nilsson, Ola; Alves, Ines; AlSayed, Moeenaldeen; Appelman-Dijkstra, Natasha M.; Baujat, Genevieve; Ben-Omran, Tawfeg; Breyer, Sandra; Cormier-Daire, Valerie; Gregersen, Pernille Axel; Guillen-Navarro, Encarna; Hoegler, Wolfgang; Maghnie, Mohamad; Mukherjee, Swati; Cohen, Shelda; Pimenta, Jeanne; Selicorni, Angelo; Semler, J. Oliver; Sigaudy, Sabine; Popkov, Dmitry; Sabir, Ian; Noval, Susana; Sessa, Marco; Irving, Melita Share Save
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Burosumab vs Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Subgroup Analysis by Dose Level Imel, Erik A.; Glorieux, Francis H.; Whyte, Michael P.; Portale, Anthony A.; Munns, Craig F.; Nilsson, Ola; Simmons, Jill H.; Padidela, Raja; Namba, Noriyuki; Cheong, Hae Il; Pitukcheewanont, Pisit; Sochett, Etienne; Hoegler, Wolfgang; Muroya, Koji; Tanaka, Hiroyuki; Gottesman, Gary S.; Biggin, Andrew; Perwad, Farzana; Chen, Angel; Roberts, Mary Scott; Ward, Leanne M. Share Save
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Burosumab for X-linked hypophosphatemia in children and adolescents: Opinion based on early experience in seven European countries Mughal, M. Zulf; Baroncelli, Giampiero I.; de Lucas-Collantes, Carmen; Linglart, Agnes; Magnolato, Andrea; Raimann, Adalbert; Santos, Fernando; Schnabel, Dirk; Shaw, Nick; Nilsson, Ola Share Save
The synovial microenvironment suppresses chondrocyte hypertrophy and promotes articular chondrocyte differentiation Chau, Michael; Dou, Zelong; Baroncelli, Marta; Landman, Ellie B.; Bendre, Ameya; Kanekiyo, Masaru; Gkourogianni, Alexandra; Barnes, Kevin; Ottosson, Lars; Nilsson, Ola Share Save
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Post-authorisation safety study of burosumab use in paediatric, adolescent and adult patients with X-Linked hypophosphataemia: rationale and description Brandi, Maria Luisa; Ariceta, Gema; Beck-Nielsen, Signe Sparre; Boot, Annemieke M.; Briot, Karine; de Lucas Collantes, Carmen; Emma, Francesco; Giannini, Sandro; Haffner, Dieter; Keen, Richard; Levtchenko, Elena; Makitie, Outi; Nilsson, Ola; Schnabel, Dirk; Tripto-Shkolnik, Liana; Zillikens, M. Carola; Liu, Jonathan; Tudor, Alina; Mughal, M. Zulf Share Save
Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia Ward, Leanne M.; Glorieux, Francis H.; Whyte, Michael P.; Munns, Craig F.; Portale, Anthony A.; Hoegler, Wolfgang; Simmons, Jill H.; Gottesman, Gary S.; Padidela, Raja; Namba, Noriyuki; Cheong, Hae Il; Nilsson, Ola; Mao, Meng; Chen, Angel; Skrinar, Alison; Roberts, Mary Scott; Imel, Erik A. Share Save
The Proteomic Signature of Intestinal Acute Rejection in the Mouse Oltean, Mihai; Bagge, Jasmine; Dindelegan, George; Kenny, Diarmuid; Molinaro, Antonio; Hellstrom, Mats; Nilsson, Ola; Sihlbom, Carina; Casselbrant, Anna; Davila, Marcela; Olausson, Michael Share Save