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Children’S Hospital of Philadelphia

学者数658
论文数242
被引数1
关联论文 (240)
发表时间
Lung tropic dual AAV-SP-C and microRNA gene therapy attenuates lung injury in mutant Sftpc mice肺趋向性双AAV-SP-C和microRNA基因疗法减轻突变Sftpc小鼠的肺损伤
err2025-12-24
err0
errOAAI
errPauline Bardin; Liqun Xu; Yanlong Pei; Adithya Achuthan Vineeth; Kennedy Nangle; Shumei Zhong; Chanèle Cyr-Depauw; Arul Vadivel; Emily Martin; Timothy E. Weaver; Sneha Sitaraman; Sarah K. Wootton; Bernard Thébaud
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Defining apnea of prematurity is messy定义早产儿呼吸暂停很复杂。
err2025-12-23
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errOAAI
errDavid M. Rub; Eric C. Eichenwald; Richard J. Martin
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Neonatal Resuscitation Practices and Outcomes: Establishing the DRIVE Network Registry新生儿复苏实践与结局:建立DRIVE网络注册系统
err2025-12-22
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errOAAI
errElizabeth E. Foglia; Beena D. Kamath-Rayne; Arun Gupta; Heidi M. Herrick; Justin B. Josephsen; Vishal Kapadia; Henry C. Lee; Birju A. Shah; Myra H. Wyckoff; Sura Lee; Paul Wildenhain; Joseph G. Reiter; Kathryn Lander; Elizabeth Goins; Tina A. Leone
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ASO Visual Abstract: Surgical Management and Outcomes in Pediatric Adrenocortical Carcinoma: A Pediatric Surgical Oncology Research Collaborative StudyASO视觉摘要:儿童肾上腺皮质癌的手术治疗与管理及预后:一项儿童肿瘤外科研究协作组研究
err2025-12-21
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PREAI
errShachi Srivatsa; Jennifer H. Aldrink; Md Rejuan Haque; Andrew Murphy; Daniel Gehle; Huma Halepota; Erika A. Newman; Keyonna Williams; Peter Mattei; William R. Johnston; Rosa Hwang; Timothy B. Lautz; Samantha A. Ayala; Nelson Piché; Caroline P. Lemoine; Julia Debertin; Stephanie F. Polites; David H. Rothstein; Kimberly J. Riehle; Nzuekoh Nchinda; Marcus M. Malek; Hannah N. Rinehardt; Catherine Gestrich; Shannon L. Castle; Adriana Lopez; Matthew S. Mayes; Emily K. Myers; Jonathan P. Roach; Brian T. Craig; Dave R. Lal; Jennifer Schuh; Barrett P. Cromeens; Sindhu V. Mannava; Mary T. Austin; Lauren K. Mayon; Zachary J. Kastenberg; Marshall Wallace; Abigail Alexander; Michael A. Stellon; Hau D. Le; Devashish S. Joshi; Charbel Chidiac; Daniel S. Rhee; Danielle Cameron; Alyssa Stetson; Barrie S. Rich; Richard D. Glick; Elizabeth A. Fialkowski; Kathryn Fowler; Rukaya Fareh; Erin G. Brown; Kathleen Doyle; Paige Abril; Christa Grant; Roshni Dasgupta; Chloé Boehmer; Sara A. Mansfield
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Thrombopoietin increases susceptibility for EVI1 + KMT2A-MLLT3-driven AML expressing stem cell genes linked to poor outcome血小板生成素增加EVI1     KMT2A-MLLT3-driven AML表达与不良预后相关的干细胞基因的易感性
err2025-12-19
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errOAAI
errHugues-Étienne Châtel-Soulet; Sabine Juge; Ana Luisa Pereira; Jonathan Seguin; Athimed El Taher; Federica Valigi; Zivojin Jevtic; Rathick Sivalingam; Frederik Otzen Bagger; Paul Büschl; Marwa Almosailleakh; Alexander Tzankov; Wei Tong; Mineo Kurokawa; César Nombela Arrieta; Juerg Schwaller
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The Impact of POLR3-related Leukodystrophy on Non-Affected Family Members: A Qualitative StudyPOLR3相关脑白质营养不良对未受影响的家庭成员的影响:一项定性研究
err2025-12-16
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errOAAI
errAdam Le; Kelly-Ann Thibault; Pouneh Amir Yazdani; Alexandra Chapleau; Romy J. van Voorst; Enrico Bertini; Francesco Nicita; Daniela Pohl; Sunita Venkateswaran; Stephanie Keller; Deborah Renaud; Dolores Gonzalez Moron; Marcelo Kauffman; Danilo De Assis Pereira; Adeline Vanderver; Marjo S. van der Knaap; Maxime Morsa; Geneviève Bernard
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The International Pediatric Stroke Study: Insight into Childhood Stroke from a Developmental Perspective国际儿童卒中研究:从发育角度对儿童卒中的见解
err2025-12-16
err0
PREAI
errMichael J. Rivkin; Alexandra Linds; Mahmoud Slim; Ann-Marie Surmava; Lauren A. Beslow; Michael M. Dowling; Mark Mackay; Adam Kirton; Lori C. Jordan; Christine K. Fox; Ryan Felling; Nomazulu Dlamini; Tim Bernard; Catherine Amlie-Lefond; Gabrielle deVeber
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A New Era in Advocacy Training: Promoting Safety and Resilience倡导培训的新时代:促进安全与韧性
err2025-12-10
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PREAI
errElizabeth S. Barnert; Lauren Gambill; Sheela Gavvala; Molly K. Krager; Lauren VonHoltz; Lois K. Lee; Lenore Jarvis
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3D chromatin-based variant-to-gene maps across 57 human cell types reveal the cellular and genetic architecture of autoimmune disease susceptibility基于3D染色质的变异-基因图谱在57种人类细胞类型中的研究揭示了自身免疫性疾病易感性的细胞和遗传架构
err2025-12-08
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errOAAI
errKhanh B. Trang; Prabhat Sharma; Laura Cook; Zachary Mount; Rajan M. Thomas; Nikhil N. Kulkarni; Emylette Cruz Cabrera; Suzanna Rachimi; Matthew C. Pahl; James A. Pippin; Chun Su; Klaus H. Kaestner; Joan M. O’Brien; Yadav Wagley; Kurt D. Hankenson; Ashley Jermusyk; Jason W. Hoskins; Laufey T. Amundadottir; Mai Xu; Kevin M. Brown; Stewart A. Anderson; Wenli Yang; Paul M. Titchenell; Patrick Seale; Babette S. Zemel; Alessandra Chesi; Neil Romberg; Megan K. Levings; Struan F. A. Grant; Andrew D. Wells
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Clonal cell states link gastroesophageal junction tissues with metaplasia and cancer克隆细胞状态将胃食管连接部组织与化生和癌症联系起来
err2025-12-08
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errOAAI
errRodrigo A. Gier; Sydney A. Bracht; Jiazhen Rong; Raúl A. Reyes Hueros; Madison L. Wahlsten; Christopher Cote; Maureen DeMarshall; Tatiana A. Karakasheva; Alexandra Strauss Starling; Amanda B. Muir; Gary W. Falk; Nancy R. Zhang; Sydney M. Shaffer
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Healthcare professionals’ experiences returning monogenic, polygenic, and integrated risk results in the eMERGE study医疗专业人员返馈单基因、多基因和综合风险结果在eMERGE研究中的经验
err2025-12-06
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errSabrina A. Suckiel; Laura Golfinopoulos; Courtney L. Scherr; Brenna M. Boyd; Wendy K. Chung; Hakon Hakonarson; Ingrid A. Holm; Iftikhar J. Kullo; Nita A. Limdi; Michael F. Murray; Melanie F. Myers; Cynthia A. Prows; Maya Sabatello; Georgia L. Wiesner; Eimear E. Kenny; Noura S. Abul-Husn
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STREAMS guidelines: standards for technical reporting in environmental and host-associated microbiome studiesSTREAMS指南:环境与宿主相关微生物组研究技术报告的标准
err2025-12-01
err0
PREAI
errJulia M. Kelliher; Chloe Mirzayi; Sarah R. Bordenstein; Aaron Oliver; Christina A. Kellogg; Eneida L. Hatcher; Maureen Berg; Petr Baldrian; Mashael Aljumaah; Cassandra Maria Luz Miller; Christopher Mungall; Vlastimil Novak; Alexis Palucki; Ethan Smith; Nazifa Tabassum; Gregory Bonito; J. Rodney Brister; Patrick S. G. Chain; Mingfei Chen; Samuel Degregori; Jose Pablo Dundore-Arias; Joanne B. Emerson; Vanessa Moreira C. Fernandes; Roberto Flores; Antonio Gonzalez; Zoe A. Hansen; Scott A. Jackson; Ahmed M. Moustafa; Trent R. Northen; Nonia Pariente; Jennifer Pett-Ridge; Sydne Record; Linta Reji; Anna-Louise Reysenbach; Virginia I. Rich; Lorna Richardson; Simon Roux; Lynn M. Schriml; Reed S. Shabman; Maria A. Sierra; Matthew B. Sullivan; Punithavathi Sundaramurthy; Katherine M. Thibault; Luke R. Thompson; Scott Tighe; Ethell Vereen; Emiley A. Eloe-Fadrosh
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