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National Center for Advancing Translational Sciences

学者数98
论文数32
被引数2.0K
关联论文 (32)
发表时间
Pathogenic NLGN4X variants reveal dual roles in synaptic connectivity and cortical development致病性NLGN4X变异揭示其在突触连接和皮质发育中的双重作用
err2026-09-19
err0
errOAAI
errEunhye Hong; Miriam Reyes Mendez; Claire Guissart; Khaoula Zaafrane-Khachnaoui; Abhijeet Kapoor; Patrycja Brzdąk; John D. Badger; Wei Lu; Katherine W. Roche
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err2026-09-17
err0
PREAI
errNichole Reisdorph; Corey D Broeckling; Rafael Brüschweiler; Clary B Clish; Valérie Copié; Timothy MD Ebbels; Arthur S Edison; Facundo M Fernández; Ulrich L Günther; Ewy A Mathé; Vanessa V Phelan; Robert Powers; Daniel Raftery; Tracey B Schock; Dajana Vuckovic; David S Wishart; Min Zhang; Elizabeth Want
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New Approaches to Clinical Trials for Rare Diseases: Decentralized Trial Design for Neurofibromatosis Type 1 and Schwannomatosis罕见病临床试验的新方法:神经纤维瘤病1型和施万瘤的分散式试验设计
errCancers
IF4.4
err2026-08-01
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errOAAI
errVanessa L. Merker; Shivani Ahlawat; Robert A. Avery; Diana Bradford; Andrea M. Gross; Jennifer Janusz; Andrés J. Lessing; Linda Manth; Miranda L. McManus; Beverly Oberlander; Dominique C. Pichard; William Riter; Kavita Y. Sarin; Steven Sheard; Russell Taylor Sundby; Karin S. Walsh; Pamela L. Wolters; Brigitte C. Widemann; Scott R. Plotkin
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Prophylactic inhibition of LATS1/2 before high-dose irradiation promotes the regeneration of the damaged intestinal epithelium高剂量照射前预防性抑制LATS1/2促进受损肠上皮的再生
err2026-07-20
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errOAAI
errLucy M. Driver; Frances Anne Tosto; Bridget S. Scherer; Lixia Luo; Katy Harbaugh; Olivia White; Ayra Charania; Jordan Tran; Rebecca Bacon; Patrick J. Morris; Michele Ceribelli; Damien Y. Duveau; Lale Evsen; Scott B. Hoyt; Keerthana Kurapati; Koravit Poysungnoen; John W. Hickey; Jatin Roper; Christine E. Eyler; Craig J. Thomas; Chang-Lung Lee
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Biofabrication and biomedical manufacturing research frontiers in the United States美国生物制造和生物医学制造研究前沿
err2026-07-17
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errOAAI
errYunxia Chen; Kyle R. Phillips; Eben Alsberg; Thomas E. Angelini; Nasim Annabi; Anthony Atala; Amit Bandyopadhyay; Leon M. Bellan; Luiz E. Bertassoni; Adriana Blazeski; Thomas Boland; Susmita Bose; Jason A. Burdick; Robert C. Chang; Christopher S. Chen; Roland K. Chen; Douglas B. Chrisey; Elizabeth Cosgriff-Hernandez; Paul D. Dalton; David Dean; Aixiang Ding; Bin Duan; Marc Ferrer; John P. Fisher; Gabor Forgacs; Debolina Ghosh; Warren L. Grayson; Murat Guvendiren; MD Ahasan Habib; Sarah C. Heilshorn; Ashley Hicks; Scott J. Hollister; Congrui Jin; Yifei Jin; Roger D. Kamm; Bashir Khoda; Robert Langer; Cato T. Laurencin; Sang Jin Lee; Kam W. Leong; Ming C. Leu; Wei Li; Michael Mak; Amir K. Miri; Roger J. Narayan; Liqun Ning; Brenda M. Ogle; Ibrahim T. Ozbolat; Zhijian Pei; Peihua Qiu; Krishanu Saha; Jayant Saksena; Vahid Serpooshan; Albert Shih; Rohan A. Shirwaiker; Pranav Soman; Ali Tamayol; Mark W. Tibitt; Changxue Xu; Yunzhi Peter Yang; Lijie Grace Zhang; James J. Yoo; Shaochen Chen; Yu Shrike Zhang; Yong Huang
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Uncovering the isoform-resolution kinetic landscape of nonsense-mediated mRNA decay with EZbakR利用EZbakR揭示无义介导的mRNA降解的异构体分辨率动力学景观
err2026-07-15
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errOAAI
errJustin W. Mabin; Isaac W. Vock; Martin Machyna; Nazmul Haque; Poonam Thakran; Alexandra Zhang; Ganesha Rai; Isabelle Nathalie-Marie Leibler; James Inglese; Matthew D. Simon; J. Robert Hogg
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Translational assessment instruments for preclinical to first-in-human decision-making: a scoping review从临床前到首次人体试验决策的转化评估工具:一项范围综述
err2026-07-13
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errOAAI
errMarco Straccia; David Mawufemor Azilagbetor; Celean Camp; Guilherme S. Ferreira; Maria Laura Garcia-Bermejo; Annalisa Gastaldello; Kurinchi Gurusamy; Francesco Pappalardo; Merel J. Ritskes-Hoitinga; Fabrizio Rossi; Danilo Tagle; Martin Wehling; Francesca Pistollato
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Phenotypic screening for small molecules that lower PrP in cultured cells筛选降低培养细胞中PrP的小分子药物
err2026-07-09
err0
errOAAI
errJeannine A. Frei; Andrew G. Reidenbach; Leo M.H. Xu; Raja Mohan Gopalakrishnan; Dominick Casalana; Daniel A. Sprague; Mark-Anthony Bray; Amy Q. Wang; Vanessa Laversenne; Brian Erickson; Craig Braun; Mckenzie Hall; Douglas Auld; Eric Vallabh Minikel; Sonia M. Vallabh
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BDNF-DT and BDNF-AS-DT: novel genes in the BDNF locusBDNF-DT和BDNF-AS-DT:BDNF基因座中的新基因
err2026-06-30
err0
errOAAI
errSvitlana V. Bach; Giovanna Punzi; Nuri E. Smith; Sreya Mukherjee; Joo Heon Shin; Qiang Chen; Geo Pertea; Leonardo Collado-Torres; Kristen R. Maynard; Stephanie C. Page; Joel E. Kleinman; Thomas M. Hyde; Daniel R. Weinberger; Keri Martinowich; Gianluca Ursini
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Combined inhibition of CDK4/6 and PI3K pathways exhibit highly synergistic activity and translational potential in Ewing sarcoma联合抑制CDK4/6和PI3K通路在尤因肉瘤中显示出高度协同活性和转化潜力
err2026-06-18
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errOAAI
errHelen F. Gloege; Maria Ana Isabel C. De Los Santos; Advaita Chakraborty; Madhav Chadha; Alejandra Aguilar-Quintero; Min Shen; Caleb O. Heaslip; Sarah Finstuen-Magro; Brigit McDannell; Mohammad Tanhaemami; Stephanie Meyer; Kelly Klega; Ya-Qin Zhang; David S. Shulman; Steven G. DuBois; Matthew D. Hall; Anne-Florence Blandin; Brian D. Crompton
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Induced pluripotent stem cell–derived models of malignant nerve sheath tumor progression mimic glial to neuro-mesenchymal transition and uncover therapeutic opportunities诱导多能干细胞来源的恶性神经鞘瘤进展模型模拟胶质细胞向神经间充质过渡并揭示治疗机会
err2026-06-17
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errOAAI
errItziar Uriarte-Arrazola; Míriam Magallón-Lorenz; Juana Fernández-Rodríguez; Jiajing Zhang; Emily Lee; Sara Ortega-Bertran; Edgar Creus-Bachiller; Judit Farrés-Casas; Kelli M. Wilson; Crystal McKnight; Katlin Recabo; Ignacio Blanco; Héctor Salvador; Cleofé Romagosa; Conxi Lázaro; Helena Mazuelas; Bernat Gel; Marc Ferrer; Meritxell Carrió; Eduard Serra
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Metformin on the Presence of COVID-19 Symptoms 6 Months after Infection: The ACTIV-6 Randomized Clinical Trial美托洛尔在感染后6个月出现COVID-19症状中的作用:ACTIV-6随机临床试验
err2026-06-04
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errOAAI
errCarolyn T Bramante, MD, MPH; Thomas G Stewart, PhD; David R Boulware, MD, MPH; Matthew W McCarthy, MD; Yue Gao, MS, Med; Russell L Rothman, MD, MPP; Ahmad Mourad, MD; Florence Thicklin; Jonathan B Cohen, MD; Idania T Garcia del Sol, MD; Nirav S Shah, MD, MPH; Manisha Mehta, DPM; Orlando Quintero Cardona, MD; Jake Scott, MD; Adit A Ginde, MD, MPH; Mario Castro, MD, MPH; Dushyantha Jayaweera, MD; Mark Sulkowski, MD; Nina Gentile, MD; Kathleen McTigue, MD; G Michael Felker, MD; Sean Collins, MD, MSci; Sarah E Dunsmore, PhD; Stacey J Adam, PhD; Christopher J Lindsell, PhD; Adrian F Hernandez, MD, MHS; Susanna Naggie, MD, MHS; for the Accelerating COVID-19 Therapeutic Interventions and Vaccines (ACTIV)-6 Study Group and Investigators
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BET inhibitor-based combinations targeting novel dependencies in MECOM-rearranged (r) AMLBET抑制剂为基础的组合,靶向MECOM重排(r) AML中的新型依赖性
errLeukemia
IF13.4
err2025-12-19
err0
errOAAI
errChristine E. Birdwell; Warren Fiskus; Christopher P. Mill; Tapan M. Kadia; Naval Daver; Courtney D. DiNardo; Koji Sasaki; John A. Davis; Kaberi Das; Hanxi Hou; Antrix Jain; Anna Malovannaya; Lauren B. Flores; Rasoul Pourebrahim; Selina Yuan; Xiaoping Su; Michele Ceribelli; Kapil N. Bhalla
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Metabolic engineering and late-stage functionalization expand the chemical space of the antimalarial premarineosin A代谢工程和晚期官能团化扩展了抗疟疾前海洋霉素A的化学空间
err2025-12-05
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errOAAI
errChristina M. McBride; Morgan McCauley; Natalia R. Harris; Sahar Amin; Brian J. Curtis; Linnea Verhey-Henke; Awet A. Teklemichael; Erin N. Oliphant; Patricia Dranchak; Katherine L. Lev; Fengrui Qu; Harrison M. Snodgrass; Jared C. Lewis; James Inglese; Xin-Zhuan Su; Filipa Pereira; David H. Sherman
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Developing Therapeutics for Rare Cardiovascular Diseases开发罕见心血管疾病的疗法
err2025-09-12
err0
PREAI
errJoseph B Lerman; Dwight D. Koeberl; Shilpi Epstein; Lothar Roessig; Rodica Stan; Meghan Halley; Anjali T. Owens; Barry Greenberg; Kevin M. Alexander; Sharlene M. Day; Mathew S. Maurer; Eric D. Adler; Adrian F. Hernandez; Euan A Ashley; G. Michael Felker
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