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Maryam Oskoui

pediatrics and neurology and neurosurgery

44H指数
253论文数
1.0W被引数
收录论文 100
发表时间
Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy7至<18岁杜氏肌营养不良症男孩中vamorolone(VBP15-006)的II期开放标签、多次给药研究的成果
err2026-03-03
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errOAAI
errHanns Lochmüller; Hernan Gonorazky; Elisa Nigro; Jean K. Mah; Alberto Alemán; Amanda Yaworski; Maryam Oskoui; Anne Marie Sbrocchi; Kathryn Selby; Ana de Vera; Laura McAdam; Ekaterina Gresko; Aki Linden; Catherine Dutreix; Eric P. Hoffman
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Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial鞘内注射onasemnogene abeparvovec治疗经治脊髓性肌萎缩症患者:一项3b期、开放标签试验
err2025-12-08
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errOAAI
errJennifer M. Kwon; Francina Munell; Laure Le Goff; Kotaro Yuge; Tamaki Kato; Claude Cances; Liesbeth De Waele; Ian R. Woodcock; Eugenio M. Mercuri; Crystal M. Proud; Basil T. Darras; Leslie H. Hayes; Maryam Oskoui; Jeannie Visootsak; Gemma Williams; Andreja Ilić; Lina Yang; W. Ludo van der Pol
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Quebec Spinal Muscular Atrophy Newborn Screening Program: The First Year Experience魁北克脊髓性肌萎缩症新生儿筛查项目:第一年经验
err2025-10-05
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errEmilie Groulx-Boivin; Ariane Belzile; Cam-Tu Émilie Nguyen; Amélie Gauthier; Nicolas Chrestian; Catherine Michaud-Gosselin; Yves Giguère; Marie-Thérèse Berthier; Jean-François Soucy; Anne-Marie Laberge; Maryam Oskoui
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Feasibility of a Home-Based Exergaming Intervention for Youth With Spinal Muscular Atrophy居家运动游戏干预对脊髓性肌萎缩症青少年的可行性
err2025-09-01
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errOAAI
errIraqi, Ihsane; Ng, Pamela; Chen, Xing; Cushen, Niamh; Gottowik, Juergen; Herzig, David; Karthigesu, Shaainthabie; Levac, Danielle; MacKenzie, Alex; Mah, Jean K.; Opalka, Slawomir; Potter, Beth; Selby, Kathryn; Sheriko, Jordan; Smith, Maureen; Turgeon-Desilets, Sarah; Woof, Angelina; Oskoui, Maryam
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Cerebral palsy characteristics in term-born children with and without detectable perinatal risk factors: A cross-sectional study
err2024-10-15
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errOAAI
errSuzuki, Kai; Husein, Nafisa; Oskoui, Maryam; Fehlings, Darcy; Shevell, Michael; Kirton, Adam; Dunbar, Mary J.
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Macrostructural Brain Abnormalities in Spinal Muscular Atrophy脊髓性肌萎缩症的宏观结构脑异常
err2024-10-01
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errGroulx-Boivin, Emilie; Oliveira-Carneiro, Andrea; Carlson, Helen; Floer, Amalia; Kirton, Adam; Mah, Jean; Saint-Martin, Christine; La Piana, Roberta; Oskoui, Maryam
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Association of Gestational Age at Birth and Changes on MRI With Prevalence and Spectrum of Comorbidities in Children With Cerebral Palsy
err2024-07-23
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PREAI
errPekeles, Heather; Husein, Nafisa; Kirton, Adam; Oskoui, Maryam; Fehlings, Darcy L.; Dunbar, Mary; Shevell, Michael I.
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A Systematic Literature Review of the Natural History of Respiratory, Swallowing, Feeding, and Speech Functions in Spinal Muscular Atrophy (SMA)
err2024-06-26
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errMarti, Yasmina; Ribero, Valerie Aponte; Batson, Sarah; Mitchell, Stephen; Gorni, Ksenija; Gusset, Nicole; Oskoui, Maryam; Servais, Laurent; Deconinck, Nicolas; Mcgrattan, Katlyn Elizabeth; Mercuri, Eugenio; Sutherland, C. Simone
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Treatment Options in Spinal Muscular Atrophy: A Pragmatic Approach for Clinicians
errDRUGS
IF14.4
err2024-06-15
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PREAI
errRamdas, Sithara; Oskoui, Maryam; Servais, Laurent
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Teratogenesis, Perinatal, and Neurodevelopmental Outcomes After In Utero Exposure to Antiseizure Medication
err2024-06-11
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PREAI
errPack, Alison M.; Oskoui, Maryam; Roberson, Shawniqua Williams; Donley, Diane K.; French, Jacqueline; Gerard, Elizabeth E.; Gloss, David; Miller, Wendy R.; Clary, Heidi M. Munger; Osmundson, Sarah S.; McFadden, Brandy; Parratt, Kaitlyn; Pennell, Page B.; Saade, George; Smith, Don B.; Sullivan, Kelly; Thomas, Sanjeev V.; Tomson, Torbjorn; O'Brien, Mary Dolan; Botchway-Doe, Kylie; Silsbee, Heather M.; Keezer, Mark R.
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Risk Factors for Perinatal Arterial Ischemic Stroke
err2024-06-11
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errOAAI
errSrivastava, Ratika; Cole, Lauran; Amador, Kimberly; Forkert, Nils Daniel; Dunbar, Mary; Shevell, Michael I.; Oskoui, Maryam; Basu, Anna P.; Rivkin, Michael J.; Shany, Eilon; de Vries, Linda S.; Dewey, Deborah; Letourneau, Nicole; Mouches, Pauline; Hill, Michael D.; Kirton, Adam
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Risk Factors for Term-Born Spastic Diplegic Cerebral Palsy: A Case-Control Study足月出生的痉挛性双瘫脑瘫的危险因素: 病例对照研究
err2024-06-01
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errMare, Amaar; Husein, Nafisa; Dunbar, Mary; Dewey, Deborah; Letourneau, Nicole; Oskoui, Maryam; Kirton, Adam; Shevell, Michael
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Universal Newborn Screening for Spinal Muscular Atrophy
err2024-06-01
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PREAI
errOskoui, Maryam; Dangouloff, Tamara; Servais, Laurent
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Comprehensive whole-genome sequence analyses provide insights into the genomic architecture of cerebral palsy全面的全基因组序列分析提供了对脑瘫基因组结构的见解
err2024-03-29
err7
PREAI
errFehlings, Darcy L.; Zarrei, Mehdi; Engchuan, Worrawat; Sondheimer, Neal; Thiruvahindrapuram, Bhooma; MacDonald, Jeffrey R.; Higginbotham, Edward J.; Thapa, Ritesh; Behlim, Tarannum; Aimola, Sabrina; Switzer, Lauren; Ng, Pamela; Wei, John; Danthi, Prakroothi S.; Pellecchia, Giovanna; Lamoureux, Sylvia; Ho, Karen; Pereira, Sergio L.; de Rijke, Jill; Sung, Wilson W. L.; Mowjoodi, Alireza; Howe, Jennifer L.; Nalpathamkalam, Thomas; Manshaei, Roozbeh; Ghaffari, Siavash; Whitney, Joseph; Patel, Rohan V.; Hamdan, Omar; Shaath, Rulan; Trost, Brett; Knights, Shannon; Samdup, Dawa; McCormick, Anna; Hunt, Carolyn; Kirton, Adam; Kawamura, Anne; Mesterman, Ronit; Gorter, Jan Willem; Dlamini, Nomazulu; Merico, Daniele; Hilali, Murto; Hirschfeld, Kyle; Grover, Kritika; Bautista, Nelson X.; Han, Kara; Marshall, Christian R.; Yuen, Ryan K. C.; Subbarao, Padmaja; Azad, Meghan B.; Turvey, Stuart E.; Mandhane, Piush; Moraes, Theo J.; Simons, Elinor; Maxwell, George; Shevell, Michael; Costain, Gregory; Michaud, Jacques L.; Hamdan, Fadi F.; Gauthier, Julie; Uguen, Kevin; Stavropoulos, Dimitri J.; Wintle, Richard F.; Oskoui, Maryam; Scherer, Stephen W.
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Co-developing The Canadian MPS Registry: A longitudinal rare disease patient registry
err2024-02-01
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PREAI
errMitchell, John J.; Inbar-Feigenberg, Michal; Angel, Kim; Chakraborty, Pranesh; Lamoureux, Monica; Adams, John; Potter, Beth K.; Stockler-Ipsirolgu, Sylvia; Howie, Alison H.; Pace, Alex; Butcher, Nancy J.; Greenberg, Cheryl; Hayeems, Robin; Laberge, Anne-Marie; Round, Jeff; Offringa, Martin; Oskoui, Maryam; Ruth, Chelsea; Schulze, Andreas; Speechley, Kathy; Thavorn, Kednapa; Trakadis, Yannis; Wilson, Kumanan; Lacaze, Thierry
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Feasibility of a home-based exergame therapy for youth with spinal muscular atrophy
err2023-12-01
err0
PREAI
errIraqi, Ihsane; Selby, Kathy; Herzig, David; Cardiff, Katrina; Cushen, Niamh; Defosses, Yan; Gonorazky, Hernan; Gottowik, Juergen; Haldenby, Renee; Jurisic, Ivan; Karthigesu, Shaainthabie; Macintyre, Leigh; Mackenzie, Alex; Mah, Jean; Mccullough, James; Ng, Pamela; Opalka, Slawomir; Openchowski, Michal; Petkun, Svetlana; Potter, Beth; Sheriko, Jordan; Smith, Maureen; Strahm, Martin; Desilets, Sarah Turgeon; Woof, Angelina; Chen, Xing; Oskoui, Maryam
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