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Moira Cheung

Great Ormond Street Hospital for Children NHS Foundation Trust

24H指数
109论文数
2.0K被引数
收录论文 38
发表时间
Safety, tolerability, pharmacokinetics, and efficacy of burosumab in infants with X-linked hypophosphataemia: an open-label, multicentre, non-randomised study布罗索单抗在X连锁低磷酸盐血症婴儿中的安全性、耐受性、药代动力学和疗效:一项开放标签、多中心、非随机研究
err2026-04-24
err0
PREAI
errAgnès Linglart; Francesco Emma; Justine Bacchetta; Francisco de la Cerda; Wesley Hayes; Moira Cheung; Alessandra Cocca; Wolfgang Högler; Raja Padidela; Lucy Henderson; Alina Tudor; Hiroki Okada; Wei Sun; Emilia Quattrocchi
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EndoCompass Project: Research Roadmap for Calcium and Bone EndocrinologyEndoCompass 项目:钙与骨骼内分泌学研究路线图
err2025-12-01
err0
PREAI
errJahn-Rickert, Katharina; Tomsic, Karin Zibar; Anastasilakis, Athanasios D.; Bertocchio, Jean-Philippe; Brandi, Maria Luisa; Fassnacht, Martin; Cheung, Moira Shang-Mei; Gevers, Evelien; Gittoes, Neil; Makitie, Outi; Martos-Moreno, Gabriel Angel; Milovanovic, Petar; Raimann, Adalbert; Tencerova, Michaela; Tsourdi, Elena; Vlug, Annegreet G.; Hogler, Wolfgang; Kamenicky, Peter
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EndoCompass project: research roadmap for calcium and bone endocrinologyEndoCompass项目:钙与骨内分泌学的研究路线图
err2025-10-01
err1
PREAI
errJahn-Rickert, Katharina; Zibar Tomsic, Karin; Anastasilakis, Athanasios D.; Bertocchio, Jean-Philippe; Brandi, Maria Luisa; Fassnacht, Martin; Cheung, Moira Shang-Mei; Gevers, Evelien; Gittoes, Neil; Makitie, Outi; Martos-Moreno, Gabriel Angel; Milovanovic, Petar; Raimann, Adalbert; Tencerova, Michaela; Tsourdi, Elena; Vlug, Annegreet G.; Hogler, Wolfgang; Kamenicky, Peter
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XLH Matters 2024: expert insights and practical tools for enhancing care of people living with X-linked hypophosphataemiaXLH Matters 2024:提升X-linked hypophosphataemia患者护理质量的专家见解与实践工具
err2025-09-29
err0
errOAAI
errLothar Seefried; Ali S. Alzahrani; Carsten A. Wagner; Damian Eade; Danilo Fintini; Dieter Haffner; Hasan Frookh Jamal; Judith S. Bubbear; Laura Guazzarotti; Moira S. Cheung; Noina Abid; Patrícia Costa-Reis; Rui Ferreira Santos; Signe Sparre Beck-Nielsen; Agnès Linglart
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Bone health in a U.K. cohort of youth living with perinatally acquired HIV-1: a longitudinal study英国队列中通过围产期获得HIV-1的青少年骨健康:一项纵向研究
err2025-09-04
err0
errOAAI
errMerle Henderson; Alexandra Blenkinsop; Oliver Ratmann; Moira Cheung; Hermione Lyall; Sarah Fidler; Caroline Foster; the BONDY study group
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Optic neuropathy associated with vitamin A deficiency in children: a case series儿童维生素A缺乏相关的视神经病变:一个病例系列
err2025-09-01
err0
PREAI
errBourke, Christine; Panteli, Vasiliki; Marmoy, Oliver R.; Thompson, Dorothy A.; Mankad, Kshitij; Sudhakar, Sniya; James, Gregory; Garnham, Jack; Connor, Alan; Cheung, Moira S.; Bowman, Richard
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Limb lengthening in individuals with achondroplasia: Analysis of an international survey
errBONE
IF3.6
err2025-06-01
err0
PREAI
errBeger, Christoph; Alves, Ines; Carl-Innig, Patricia; Sessa, Marco; Mohnike, Klaus; Cheung, Moira S.
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XLH Matters: an evolving programme to discuss new advances and share clinical experiences to improve patient outcomes
err2025-02-03
err0
errOAAI
errSeefried, Lothar; Aliberti, Ferdinando; Heier, Cathrine Alsaker; Arango-Sancho, Pedro; Biosse Duplan, Martin; Sakka, Sophia D.; Emma, Francesco; Gardiner, Oliver; Javaid, Muhammad Kassim; Ferreira-Santos, Rui M.; Raimann, Adalbert; Rak, Kristen; Bubbear, Judith S.; Cheung, Moira S.; Beck-Nielsen, Signe Sparre; Mindler, Gabriel T.; Linglart, Agnes
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Meeting report from the 3rd ISCBH-ERN BOND Achondroplasia Workshop on Long Bone Pathology in Children with Achondroplasia, Salzburg, Austria 22nd June 2024
errBONE
IF3.6
err2025-01-01
err1
PREAI
errCheung, Moira S.; Alves, Ines; Carl-Innig, Patricia; Eastwood, Deborah; Maghnie, Mohamad; Offiah, Amaka; Paley, Dror; Riganti, Simone; Savarirayan, Ravi; Sessa, Marco; Vogt, Bjoern; Mohnike, Klaus
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Eiken syndrome with parathyroid hormone resistance due to a novel parathyroid hormone receptor type 1 mutation: clinical features and functional analysis
err2024-09-14
err0
PREAI
errCalder, Alistair D.; Allgrove, Jeremy; Hoppner, Jakob; Cheung, Moira; Alexander, Saji; Garagnani, Lorenzo; Thakker, Rajesh; Juppner, Harald; Gardella, Thomas J.; Holder-Espinasse, Muriel
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Comprehensive literature review on the prevalence of comorbid conditions in patients with achondroplasia
errBONE
IF3.6
err2022-09-01
err13
PREAI
errStender, Monika; Pimenta, Jeanne M.; Cheung, Moira; Irving, Melita; Mukherjee, Swati
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Higher rates of non-skeletal complications in achondroplasia compared to the general population: A UK matched cohort study using CPRD-GOLD database
err2022-03-01
err0
errOAAI
errIrving, Melita; Pimenta, Jeanne; Cheung, Moira; Mazzeo, Louise; Landis, Sarah; Mukherjee, Swati
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International Consensus Statement on the diagnosis, multidisciplinary management and lifelong care of individuals with achondroplasia
err2021-11-26
err60
errOAAI
errSavarirayan, Ravi; Ireland, Penny; Irving, Melita; Thompson, Dominic; Alves, Ines; Baratela, Wagner A. R.; Betts, James; Bober, Michael B.; Boero, Silvio; Briddell, Jenna; Campbell, Jeffrey; Campeau, Philippe M.; Carl-Innig, Patricia; Cheung, Moira S.; Cobourne, Martyn; Cormier-Daire, Valerie; Deladure-Molla, Muriel; del Pino, Mariana; Elphick, Heather; Fano, Virginia; Fauroux, Brigitte; Gibbins, Jonathan; Groves, Mari L.; Hagenas, Lars; Hannon, Therese; Hoover-Fong, Julie; Kaisermann, Morrys; Leiva-Gea, Antonio; Llerena, Juan; Mackenzie, William; Martin, Kenneth; Mazzoleni, Fabio; McDonnell, Sharon; Meazzini, Maria Costanza; Milerad, Josef; Mohnike, Klaus; Mortier, Geert R.; Offiah, Amaka; Ozono, Keiichi; Phillips, John A., III; Powell, Steven; Prasad, Yosha; Raggio, Cathleen; Rosselli, Pablo; Rossiter, Judith; Selicorni, Angelo; Sessa, Marco; Theroux, Mary; Thomas, Matthew; Trespedi, Laura; Tunkel, David; Wallis, Colin; Wright, Michael; Yasui, Natsuo; Fredwall, Svein Otto
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Patient-Reported Complications, Symptoms, and Experiences of Living With X-Linked Hypophosphatemia Across the Life-Course
err2021-04-23
err15
errOAAI
errCheung, Moira; Rylands, Angela J.; Williams, Angela; Bailey, Karen; Bubbear, Judith
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Meeting report from the achondroplasia foramen magnum workshop, Salzburg, Austria 22nd June 2019
errBONE
IF3.6
err2019-10-01
err11
PREAI
errCheung, Moira S.; Alves, Ines; Hagenas, Lars; Mohnike, Klaus
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