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Pharmacokinetics, Pharmacodynamics, and Safety of Subcutaneous Belimumab in Pediatric Patients With Systemic Lupus Erythematosus: A Multicenter, Open-Label Trial 系统性红斑狼疮儿科患者皮下注射贝利木单抗的药代动力学、药效学和安全性:一项多中心、开放标签试验 Brunner, Hermine I.; Anton, Jordi; Calvo-Penades, Inmaculada; Dimelow, Richard; Horneff, Gerd; Kamphuis, Sylvia; Marino, Rebecca; van Maurik, Andre; Minden, Kirsten; Mori, Masaaki; Ocran-Appiah, Josephine; Wilkinson, Christel; Yamasaki, Yuichi; Assudani, Deepak 分享 收藏
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Identification of strengths and weaknesses of the healthcare system for persons living with rare diseases in Catalonia (Spain), and recommendations to improve its comprehensive attention: the acERca las enfermedades raras project Hernandez-Rodriguez, Jose; Martinez-Valle, Fernando; Acebes, Xenia; Alerany, Carmen; Anton, Jordi; Calvo, Gonzalo; Corral, Marian; Cruz, Jordi; Mangues-Bafalluy, M. Antonia; Mateo, Jose; Rivera, Josefa; Salazar, Albert; Francisco, Roser; Mallol, Cristina; Reig-Viader, Rita; Tigri-Santina, Ariadna; Ricart, Assumpta; Palau, Francesc 分享 收藏
Non-Classical Complications of Adult-Onset Still's Disease: A Multicenter Spanish Study 成人斯蒂尔病的非经典并发症: 西班牙多中心研究 Narvaez, Javier; Palacios-Olid, Judith; de Yebenes, Maria Jesus Garcia; Holgado, Susana; Olive, Alejandro; Casafont-Sole, Ivette; Castaneda, Santos; Valero-Martinez, Cristina; Martin-Lopez, Maria; Carreira, Patricia E.; Mora-Liminana, Maribel; Nuno-Nuno, Laura; Robles-Marhuenda, Angel; Bernabeu, Pilar; Campos, Jose; Grana, Jenaro; Ortiz-Santamaria, Vera; Camacho-Lovillo, Marisol; Vargas, Carmen; Sanchez-Manubens, Judith; Anton, Jordi 分享 收藏
Pharmacokinetics, Efficacy, and Safety of Upadacitinib in Pediatric Patients With Polyarticular-Course Juvenile Idiopathic Arthritis: An Interim Analysis of an Open-Label, Phase 1 Trial Upadacitinib在多关节型幼年特发性关节炎患儿中的药代动力学、疗效和安全性: 一项开放标签1期试验的中期分析 Brunner, Hermine I.; Shmagel, Anna; Horneff, Gerd; Foeldvari, Ivan; Anton, Jordi; Ramanan, Athimalaipet V.; Qian, Yuli; Unnebrink, Kristina; Hao, Shuai; Camp, Heidi S.; Khan, Nasser; Liu, Wei; Mohamed, Mohamed-Eslam F. 分享 收藏
Recommendations for Transitioning Young People with Primary Immunodeficiency Disorders and Autoinflammatory Diseases to Adult Care 将患有原发性免疫缺陷病和自身炎症性疾病的年轻人转变为成人护理的建议 Israni, Muskan; Alderson, Eliska; Mahlaoui, Nizar; Obici, Laura; Rossi-Semerano, Linda; Lachmann, Helen; Avramovic, Mojca Zajc; Guffroy, Aurelien; Dalm, Virgil; Rimmer, Rachel; Solis, Leire; Villar, Carlota; Gennery, Andrew R.; Skeffington, Stephanie; Nordin, Julia; Warnatz, Klaus; Korganow, Anne-Sophie; Anton, Jordi; Cattalini, Marco; Berg, Stefan; Soler-Palacin, Pere; Campbell, Mari; Burns, Siobhan O.; ESID Clinical Working Party, Ann; ERN RITA Transition Working Grp Consortium, Anna 分享 收藏
Characterizing Protracted Febrile Myalgia: Fasciitis and Vasculitis of the Fascia and Muscle as Novel Histopathological Features Hernandez-Rodriguez, Jose; Mestre-Trabal, Lola; Gomez-Caverzaschi, Veronica; Araujo, Olga; Terenas, Magda; Robaina, Ricardo; Bolanos, Julio; Prieto-Gonzalez, Sergio; Anton, Jordi; Yague, Jordi; Tomas, Xavier; Aldecoa, Iban; Grau, Josep M. 分享 收藏
Mevalonate kinase deficiency: an updated clinical overview and revision of the SHARE recommendations Lengvari, Lilla; Takacs, Kata; Lengyel, Anna; Palinkas, Annamaria; Wouters, Carine Helena; Kone-Paut, Isabelle; Kuemmerte-Deschner, Jasmin; Jeyaratnam, Jerold; Anton, Jordi; Lachmann, Helen Jane; Gattorno, Marco; Hofer, Michael; Toplak, NataSa; Weiser, Peter; Kallinich, Tilmann; Ozen, Seza; Hentgen, Veronique; Uziel, Yosef; Horvath, Zsuzsanna; Szabados, Marton; Brogan, Paul; Constantin, Tamas; Frenkel, Joost 分享 收藏
Similarities and differences between systemic juvenile idiopathic arthritis and adult-onset Still's disease: a multicenter Spanish study Anton, Jordi; Mosquera, Juan Manuel; Calzada, Joan; Iglesias, Estibaliz; Zacarias, Andrea; Olive, Alejandro; Bittermann, Violeta; Lorenzo, Tania Rodriguez; Remesal, Agustin; Quintana-Ortega, Cristian; Nuno-Nuno, Laura; Robles-Marhuenda, Angel; de Inocencio, Jaime; Martin-Lopez, Maria; Carreira, Patricia E.; Brandy-Garcia, Anahy M.; Holgado, Susana; Camacho-Lovillo, Marisol; Ruiz-Roman, Alberto; Clemente, Daniel; Narvaez, Javier; Campos, Jose; Sanchez-Manubens, Judith; Bernabeu, Pilar; Grana, Jenaro; Vargas, Carmen; Ortiz-Santamaria, Vera; Castaneda, Santos; de Yebenes, Maria Jesus Garcia; Carmona, Loreto 分享 收藏
Enrichment of Rare Variants of Hemophagocytic Lymphohistiocytosis Genes in Systemic Juvenile Idiopathic Arthritis Marques, Mariana Correia; Rubin, Danielle; Shuldiner, Emily G.; Datta, Mallika; Schmitz, Elizabeth; Cruz, Gustavo Gutierrez; Patt, Andrew; Bennett, Elizabeth; Grom, Alexei; Foell, Dirk; Gattorno, Marco; Bohnsack, John; Yeung, Rae S. M.; Prahalad, Sampath; Mellins, Elizabeth; Anton, Jordi; Len, Claudio A.; Oliveira, Sheila; Woo, Patricia; Ozen, Seza; Deng, Zuoming; Ombrello, Michael J. 分享 收藏
THE EUROFEVER FMF LONGITUDINAL COHORT: FIRST LONGITUDINAL DATA 欧洲热FMF纵向队列研究:首次纵向数据 Bustaffa, M.; Amaryan, G.; Gallizzi, R.; Papadopoulou-Alataki, E.; Carrabba, M.; Anton, J.; Simonini, G.; Alessio, M.; Breda, L.; Kuemmerle-Deschner, J. B.; Rigante, D.; Obici, L.; Insalaco, A.; Legger, E.; Caorsi, R.; Ruperto, N.; Gattorno, M.; Ozen, S. 分享 收藏
IS GROWTH ADVERSELY AFFECTED IN CHILDREN WITH CHRONIC NON-BACTERIAL OSTEOMYELITIS? 慢性非细菌性骨髓炎患儿的生长发育是否受到不利影响? Miettunen, P.; Carlini, L.; Insalaco, A.; Anton, J.; Brunner, J.; Legger, E.; Cattalini, M.; Hoppenreijs, E.; Alessio, M.; Mosci, E.; Caorsi, R.; Ruperto, N.; Gattorno, M. 分享 收藏
INCREASED INCIDENCE OF ADVERSE EVENTS AND EVENTS OF SPECIAL INTEREST WITH TREATMENT INTENSIFICATION IN NON-SYSTEMIC JUVENILE IDIOPATHIC ARTHRITIS 治疗强化在非系统性幼年特发性关节炎中不良事件和特别关注事件发生率的增加 Miettunen, P.; Gimenez, A. Rebollo; Carlini, L.; Pistorio, A.; Panaviene, V.; Anton, J.; Kamphuis, S.; Herlin, T.; Dolezalova, P.; Cattalini, M.; Susic, G.; Sanner, H.; Maggio, M. C.; Hashad, S.; Abdwani, R.; Rigante, D.; Lorzano, A. Rodriquez; Pallotti, C.; Swart, J. F.; Ruperto, N. 分享 收藏
DIFFERENCES IN CLINICAL PRESENTATION BETWEEN JUVENILE SYSTEMIC SCLEROSIS PATIENTS WITH DIFFUSE AND LIMITED SUBTYPE. RESULTS FROM THE JUVENILE SCLERODERMA INCEPTION COHORT 弥漫型和局限型青少年系统性硬化症患者临床表现差异。青少年硬皮病起始队列研究结果。 Foeldvari, I.; Klotsche, J.; Torok, K.; Kasapcopur, O.; Adrovic, A.; Feldman, B.; Anton, J.; Johnson, S. R.; Sztajnbok, F. R.; Terreri, M. T.; Sakamoto, A. P.; Khubchandani, R.; Stanevicha, V.; Schonenberg, D.; Al-Abadi, E.; Alexeeva, E.; Katsikas, M.; Sawhney, S.; Smith, V.; Appenzeller, S.; Avcin, T.; Kostik, M.; Lehman, T.; Malcova, H.; Marrani, E.; Pain, C.; Patwardhan, A.; Sifuentes-Giraldo, W. A.; Vasquez-Canizares, N.; Al Saoud, S. Abu; Reis, P. Costa; Janarthanan, M.; Moll, M.; Nemcova, D.; Santos, M. J.; Battagliotti, C.; Berntson, L.; Bica, B.; Brunner, J.; Eleftheriou, D.; Harel, L.; Horneff, G.; Kaiser, D.; Kallinich, T.; Lazarevic, D.; Minden, K.; Nuruzzaman, F.; Hetlevik, S. Opsahl; Sparchez, M.; Uziel, Y.; Helmus, N. 分享 收藏