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Brigitte C. Widemann

national cancer institute

71H指数
679论文数
1.6W被引数
收录论文 118
发表时间
New Approaches to Clinical Trials for Rare Diseases: Decentralized Trial Design for Neurofibromatosis Type 1 and Schwannomatosis罕见病临床试验的新方法:神经纤维瘤病1型和施万瘤的分散式试验设计
errCancers
IF4.4
err2026-08-01
err0
errOAAI
errVanessa L. Merker; Shivani Ahlawat; Robert A. Avery; Diana Bradford; Andrea M. Gross; Jennifer Janusz; Andrés J. Lessing; Linda Manth; Miranda L. McManus; Beverly Oberlander; Dominique C. Pichard; William Riter; Kavita Y. Sarin; Steven Sheard; Russell Taylor Sundby; Karin S. Walsh; Pamela L. Wolters; Brigitte C. Widemann; Scott R. Plotkin
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Malignant peripheral nerve sheath tumor development during MEK inhibitor treatment: A pre-clinical study and a clinical case seriesMEK抑制剂治疗期间恶性周围神经鞘瘤的发展:一项预临床研究和临床病例系列
err2026-07-11
err0
errOAAI
errAndrea M Gross; Steven D Rhodes; Anne Dufek; Eva Dombi; Andrea Baldwin; John F Shern; Russell Taylor Sundby; Xiyuan Zhang; Melike Pekmezci; D Wade Clapp; Joseph G Pressey; Brian D Weiss; Miriam Bornhorst; AeRang Kim; Michael J Fisher; Brigitte C Widemann; null
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Trabectedin and low-dose irinotecan to target EWS::FLI1 in Ewing sarcoma: a phase 1/2 trialTra贝替丁和低剂量伊立替康靶向EWS::FLI1在尤因肉瘤中的作用: 1/2期试验
err2026-04-16
err0
PREAI
errPatrick J. Grohar; Rachel Heise; Mary Frances Wedekind; Karla Ballman; Leo Mascarenhas; Steven G. DuBois; Robert G. Maki; Elissa A. Boguslawski; Jenna M. Gedminas; Elizabeth R. Wilson; Elaine Thomas; Blair Segers; Lea F. Surrey; Cora Ricker; Kelly Klega; Fariba Navid; Gretchen Y. Lam; Stephanie The; Rebecca Kaufman; Ryan D. Roberts; Masanori Hayashi; Esther Mena; Lindsey Overman; Cody Peer; Keith Schmidt; Mark S. Diamond; William D. Figg; Rochelle Bagatell; M. Liza Lindenberg; Peter L. Choyke; Brian D. Crompton; Brigitte C. Widemann; John W. Glod; Theodore W. Laetsch; Denise K. Reinke; Rashmi Chugh
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The prostate is a common site of disease in patients with MEN2B and medullary thyroid carcinomaMEN2B和髓样甲状腺癌患者中前列腺是常见的疾病部位
err2026-01-01
err0
PREAI
errKraft, Ira L.; Akshintala, Srivandana; Gross, Andrea; Dombi, Eva; Turkbey, Baris; Bednarova, Sandra; Ward, John F.; Yedururi, Sireesha; Merino, Maria; Pinto, Peter A.; Widemann, Brigitte C.; Shern, Jack F.; Waguespack, Steven G.; Glod, John
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The impact of focused federal initiatives on pediatric cancer research
errCANCER
IF5.1
err2025-11-15
err0
errOAAI
errJagu, Subhashini; Smith, Malcolm A.; Seibel, Nita L.; Tonorezos, Emily S.; Widemann, Brigitte C.; Gibbons, Holly A.; Holohan, Mary K.; Ababiya, Ziky A.; Guidry Auvil, Jaime M.; Lowy, Douglas R.; Doroshow, James H.; Lubenow, Anne E.; Reaman, Gregory H.
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Investigating fatigue in adults with neuroendocrine neoplasms using a biopsychosocial model采用生物-心理-社会模型调查神经内分泌肿瘤成年患者中的疲劳情况
err2025-10-17
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PREAI
errSarah W. Peters; Pamela L. Wolters; Jaydira Del Rivero; Mary Frances Wedekind; Karlyne M. Reilly; Crystal Flowers; Brigitte Widemann; Robin Lockridge
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The spectrum of pathogenic NF1 variants in participants enrolling on clinical trials of MEK inhibitors for plexiform neurofibroma参与者在进行MEK抑制剂临床试验的丛状神经纤维瘤中致病性NF1变异的谱系
err2025-10-15
err0
PREAI
errChelsea Kotch; Alicia Gomes; Krista S. Schatz; Eva Dombi; Symone Brown; Andrea M. Gross; Mélanie Alves; Sébastien Perreault; Sabine Mueller; Alyssa T. Reddy; Carlos Romo; Miriam Bornhorst; James Tonsgard; Brian D. Weiss; Brigitte Widemann; Michael J. Fisher
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Long-term Ocular Safety in Children Treated with MAPK Pathway Inhibitor Therapy接受MAPK通路抑制剂治疗儿童的长期眼部安全性
err2025-10-10
err0
PREAI
errRobert A. Avery; Andrea M. Gross; Chantal Cousineau-Krieger; Tiarnán D.L. Keenan; Taylor McManus; Connor J. Dallas; Christopher Hampton; Andrea Baldwin; Fangming Jin; Kara Heisey; Kristen Zeller; Grant T. Liu; Chinwe Okeagu; Rachel Bishop; Michael J. Fisher; Brigitte C. Widemann; M.Teresa Magone
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How to foster new treatment development in ultra-rare tumours? Joint EMA-EORTC multi-stakeholder workshops on ultra-rare sarcomas as a model for rare cancers如何促进超罕见肿瘤的新疗法开发?EMA-EORTC多利益相关方联合研讨会以超罕见肉瘤作为罕见癌症的模型
err2025-08-06
err0
PREAI
errSilvia Stacchiotti; Pan Pantziarka; Hugh Leonard; Caroline Voltz; Laura Abatedaga; Gauthier Bouche; Christelle Bouygues; Judith V.M.G. Bovee; Winette T.A. Van der Graaf; Teresa De Rojas; Lorenzo D’Ambrosio; Martha Donoghue; Harald Enzmann; Gerry Feeney; Paolo Foggi; Anna Maria Frezza; Ralf Herold; Robin L. Jones; Bernd Kasper; Kit Roes; Sandrine Marreaud; Rosalba Miceli; Denise Robinson; Josh Sommer; William D. Tap; Caitlin Tydings; Annalisa Trama; Winan Van Houdt; Gerard van Oortmerssen; Andrew J. Wagner; Brigitte Widemann; Hans Gelderblom; Alessandro Gronchi; Andrea Napolitano; Armelle Dufresne; Elena R. Fumagalli; Giacomo Baldi; Gloria Marquina; Hanna Koseła-Paterczyk; Javier Broto Martin Javier; Niels Junker; Piotr Rutkowski; Wim J.G. Oyen; Denis Lacombe; Francesco Pignatti; Pierre Demolis
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Treatment of Cutaneous Neurofibromas in Neurofibromatosis Type 1 With MEK Inhibitor Selumetinib A Nonrandomized Clinical Trial神经纤维瘤病1型皮肤神经纤维瘤的MEK抑制剂Selumetinib治疗:一项非随机临床试验
err2025-02-26
err0
PREAI
errGross, Andrea M.; Reid, Olivia H.; Baldwin, Lauren A.; Cannon, Ashley; Choo-Wosoba, Hyoyoung; Steinberg, Seth M.; Lobbous, Mina; Wolters, Pamela L.; Pichard, Dominique C.; Tibery, Cecilia M.; Dombi, Eva; Derdak, Joanne; Widemann, Brigitte C.; Korf, Bruce R.
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Anthropometric measurements of children with neurofibromatosis type I: impact of plexiform neurofibroma volume and treatment
err2024-08-28
err1
PREAI
errLemberg, Kathryn M.; Gross, Andrea M.; Sproule, Lauren M.; Liewehr, David J.; Dombi, Eva; Baldwin, Andrea; Steinberg, Seth M.; Bornhorst, Miriam; Lodish, Maya; Blakeley, Jaishri O.; Widemann, Brigitte C.
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snRNA-seq of human cutaneous neurofibromas before and after selumetinib treatment implicates role of altered Schwann cell states, inter-cellular signaling, and extracellular matrix in treatment response
err2024-06-21
err1
errOAAI
errChurch, Cameron; Fay, Christian X.; Kriukov, Emil; Liu, Hui; Cannon, Ashley; Baldwin, Lauren Ashley; Crossman, David K.; Korf, Bruce; Wallace, Margaret R.; Gross, Andrea M.; Widemann, Brigitte C.; Kesterson, Robert A.; Baranov, Petr; Wallis, Deeann
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MANAGEMENT TRENDS OF MEK INHIBITOR DERMATOLOGIC ADVERSE EVENTS FOR NEUROFIBROMATOSIS PATIENTS
err2024-06-18
err0
errOAAI
errParisi, Rose; Dhulipalla, Sanjana; Widemann, Brigitte; Pichard, Dominique C.; Gross, Andrea; Weintraub, Lauren
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LOWER BODY SURFACE AREA IS ASSOCIATED WITH INCREASED LIKELIHOOD OF PLEXIFORM NEUROFIBROMA RESPONSE TO MEK INHIBITION
err2024-06-18
err0
errOAAI
errKotch, Chelsea; Dombi, Eva; Gross, Andrea; Weiss, Brian; Mueller, Sabine; Reddy, Alyssa T.; Perreault, Sebastien; Alves, Melanie; Brown, Symone; Li, Yimei; Widemann, Brigitte C.; Fisher, Michael J.
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Virtual multi-institutional tumor board: a strategy for personalized diagnoses and management of rare CNS tumors虚拟多机构肿瘤委员会: 罕见中枢神经系统肿瘤的个性化诊断和管理策略
err2024-03-01
err1
errOAAI
errRogers, James L.; Wall, Thomas; Acquaye-Mallory, Alvina A.; Boris, Lisa; Kim, Yeonju; Aldape, Kenneth; Quezado, Martha M.; Butman, John A.; Smirniotopoulos, James G.; Chaudhry, Huma; Tsien, Christina I.; Chittiboina, Prashant; Zaghloul, Kareem; Aboud, Orwa; Avgeropoulos, Nicholas G.; Burton, Eric C.; Cachia, David M.; Dixit, Karan S.; Drappatz, Jan; Dunbar, Erin M.; Forsyth, Peter; Komlodi-Pasztor, Edina; Mandel, Jacob; Ozer, Byram H.; Lee, Eudocia Q.; Ranjan, Surabhi; Lukas, Rimas V.; Raygada, Margarita; Salacz, Michael E.; Smith-Cohn, Matthew A.; Snyder, James; Soldatos, Ariane; Theeler, Brett J.; Widemann, Brigitte C.; Camphausen, Kevin A.; Heiss, John D.; Armstrong, Terri S.; Gilbert, Mark R.; Penas-Prado, Marta
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Imaging as an early biomarker to predict sensitivity to everolimus for progressive NF2-related vestibular schwannoma成像作为预测依维莫司对进行性NF2-related前庭神经鞘瘤敏感性的早期生物标志物
err2024-02-19
err2
errOAAI
errNghiemphu, Phioanh Leia; Vitte, Jeremie; Dombi, Eva; Nguyen, Thien; Wagle, Naveed; Ishiyama, Akira; Sepahdari, Ali R.; Cachia, David; Widemann, Brigitte C.; Brackmann, Derald E.; Doherty, Joni K.; Kalamarides, Michel; Giovannini, Marco
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Understanding rare cancers in Hispanic/Latinx populations: Insights from the MyPART natural history study of rare solid tumors
err2023-12-01
err0
PREAI
errPineda, Juan C. Fierro; Ahmed, Shadin; Reilly, Karlyne; Lockridge, Robin; Raygada, Margarita; Thomas, Barbara; Glod, John; Sandier, Abby; Widemann, Brigitte; Malone, Mary Frances Wedekind
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