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J

James Signorovitch

utmd anderson cancer center

44H指数
434论文数
8.3K被引数
收录论文 123
发表时间
Five-Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: A Phase 1/2a Study达兰尼斯特罗根 Moxeparvovec 治疗杜氏肌营养不良症的五年结果:一项 1/2a 期研究
err2026-06-03
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errOAAI
errJerry R. Mendell; Zarife Sahenk; Linda P. Lowes; Megan A. Iammarino; Lindsay N. Alfano; Craig M. McDonald; James E. Signorovitch; Jim Jin; Jing Li; Stefanie Mason; Louise R. Rodino-Klapac
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Disease burden of ATTR amyloidosis based on the SF-36® health survey基于SF-36®健康调查的ATTR淀粉样变性疾病负担
err2026-04-15
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errOAAI
errVaishali Sanchorawala; Alexandra Greatsinger; Andrew Staron; John L. Berk; Lisa M. Mendelson; Tracy Joshi; Natasha J. Burke; Nadia Tabatabaeepour; Jess Smith; James Signorovitch
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Motor Function and Growth Outcomes With Early Corticosteroid Initiation in Duchenne Muscular Dystrophy: An Adjusted Cross-Trial Comparison杜氏肌营养不良症早期糖皮质激素启动对运动功能和生长结局的影响:一项调整后的跨试验比较
err2026-03-01
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PREAI
errCiafaloni, Emma; Zion, Abigail; Donovan, Joanne; Freed, Megan; Anderson, Katherine; Guglieri, Michela; Finkel, Richard S.; Griggs, Robert C.; Akbarnejad, Hanane; Signorovitch, James
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Real-World Analysis of Patients With C3 Glomerulopathy in the United States美国C3肾小球病患者真实世界分析
err2026-01-14
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errOAAI
errBriana C. Ndife; Carolina Aldworth; Jennifer Nguyen; Irina Pivneva; Marie Louise Edwards; Annika Anderson; James Signorovitch; Pietro A. Canetta
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Descriptive characterization of ambulatory health states in Duchenne muscular dystrophy: Motor function trajectories and times to loss of ambulation杜氏肌营养不良症中非卧床健康状态的描述性特征:运动功能轨迹及丧失行走能力的时间
err2025-09-23
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errOAAI
errFrancesco Muntoni; James Signorovitch; Michaela Johnson; Andres Gomez-Lievano; Nate Posner; Patricia Dorling; Katherine Beaverson; Jose Alvir; Matthias Mahn; Susan J Ward; Nathalie Goemans; Krista Vandenborne; Eugenio Mercuri; Craig M McDonald
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Cardiologist-Reported Reasons for Not Titrating Guideline-Directed Medical Therapy for Heart Failure with Reduced Ejection Fraction心脏病专家报告的不调整针对射血分数降低的心力衰竭的指南导向药物治疗的原因
err2025-05-11
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PREAI
errSTEPHEN J. GREENE; HANNA K. GAGGIN; LORI D. BASH; DOMINIK LAUTSCH; YAN SONG; MO ZHOU; JAMES SIGNOROVITCH; ANDRA S. STEVENSON; ROBERT O. BLAUSTEIN; JAVED BUTLER
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Visualizing ambulatory performance by age and rates of decline among patients with Duchenne muscular dystrophy按年龄和下降率可视化杜氏肌营养不良症患者的步行表现
err2025-03-17
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PREAI
errMayhew, Anna G.; Signorovitch, James; Johnson, Michaela; Frean, Molly; Ward, Susan J.; Posner, Nate; Merla, Valeria; Mahn, Matthias; Stimpson, Georgia; Guglieri, Michela; Straub, Volker; Muni-Lofra, Robert; Manzur, Adnan; Baranello, Giovanni; Muntoni, Francesco; North Star Clinical Network
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Cluster Analysis of Clinical Remission and Relapse Patterns in Chronic Urticaria: Results from the PREDICT-CU Study
err2025-03-01
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errBalp, Maria-Magdalena; Pivneva, Irina; Danyliv, Andrii; Chen, Kathleen; Cornwall, Tom; Royer, Jimmy; Signorovitch, James; Patil, Dhaval; Kohli, Ravneet K.; Severin, Thomas; Soong, Weily; Marsland, Alexander M.
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Clinical burden, treatment, and disease control in patients with chronic spontaneous urticaria Real-world evidence慢性自发性荨麻疹患者的临床负担、治疗及疾病控制:真实世界证据
err2024-12-01
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errRiedl, Marc A.; Patil, Dhaval; Rodrigues, Jonathan; Kuruvilla, Merin; Raftery, Tara; Pivneva, Irina; Doran, Jason; Voegel, Arthur; Signorovitch, James; Yosipovitch, Gil
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Transfusion-related cost offsets and time burden in patients with myelofibrosis on momelotinib vs. danazol from MOMENTUM
err2024-07-29
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errOAAI
errMasarova, Lucia; Verstovsek, Srdan; Liu, Tom; Rao, Sumati; Sajeev, Gautam; Fillbrunn, Mirko; Simpson, Ryan; Li, Weilong; Yang, Joseph; Le Lorier, Yvette; Gorsh, Boris; Signorovitch, James
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Real-World Neoadjuvant Treatment Patterns and Outcomes in Resected Non-Small-Cell Lung Cancer
err2024-07-01
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PREAI
errDonington, Jessica; Hu, Xiaohan; Zhang, Su; Song, Yan; Arunachalam, Ashwini; Chirovsky, Diana; Gao, Chi; Lerner, Ari; Jiang, Anya; Signorovitch, James; Samkari, Ayman
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Renal Response Criteria for Clinical Trials in Amyloid Light Chain Amyloidosis
err2024-07-01
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errOAAI
errLeung, Nelson; Comenzo, Raymond; Gillmore, Julian; Havasi, Andrea; Kastritis, Efstathios; Guthrie, Spencer; Signorovitch, James; Heath, Dena; Lousada, Isabelle
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Advancing Transthyretin Amyloidosis Drug Development in an Evolving Treatment Landscape: Amyloidosis Forum Meeting Proceedings
err2024-06-04
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PREAI
errMaurer, Mathew S.; Soman, Prem; Hernandez, Adrian; Garcia-Pavia, Pablo; Signorovitch, James; Wei, L. J.; Hanna, Mazen; Ruberg, Frederick L.; Kittleson, Michelle; Kazi, Dhruv; Dorbala, Sharmila; Hsu, Kristen; Lousada, Isabelle; Adigun, Rosalyn; Dunnmon, Preston; Kelly, Jeffery; Gillmore, Julian
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