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Dolan Sondhi

Cornell University

36H指数
114论文数
4.9K被引数
收录论文 43
发表时间
Prime Editing of Alzheimer's Disease High-Risk APOE4 Allele by Brain-Directed Adeno-Associated Virus Vectors
err2025-12-01
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PREAI
errGunaydin, Caner; Hackett, Neil R.; Wakim, Victor; Sondhi, Dolan; Kaminsky, Stephen M.; Crystal, Ronald G.
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Expression and processing of mature human frataxin after gene therapy in mice
err2024-04-10
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errRojsajjakul, Teerapat; Selvan, Nithya; De, Bishnu; Rosenberg, Jonathan B.; Kaminsky, Stephen M.; Sondhi, Dolan; Janki, Peter; Crystal, Ronald G.; Mesaros, Clementina; Khanna, Richie; Blair, Ian A.
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Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2通过直接脑实质给药表达CLN2的rh.10腺相关病毒来减缓晚期婴儿Batten病
err2020-12-02
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errSondhi, Dolan; Kaminsky, Stephen M.; Hackett, Neil R.; Pagovich, Odelya E.; Rosenberg, Jonathan B.; De, Bishnu P.; Chen, Alvin; Van de Graaf, Benjamin; Mezey, Jason G.; Mammen, Grace W.; Mancenido, Denesy; Xu, Fang; Kosofsky, Barry; Yohay, Kaleb; Worgall, Stefan; Kaner, Robert J.; Souwedaine, Mark; Greenwald, Bruce M.; Kaplitt, Michael; Dyke, Jonathan P.; Ballon, Douglas J.; Heier, Linda A.; Kiss, Szilard; Crystal, Ronald G.
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Gene therapy for C1 esterase inhibitor deficiency in a Murine Model of Hereditary angioedema
err2019-03-19
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errQiu, Ting; Chiuchiolo, Maria J.; Whaley, Adele S.; Russo, Anthony R.; Sondhi, Dolan; Kaminsky, Stephen M.; Crystal, Ronald G.; Pagovich, Odelya E.
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Untargeted Metabolite Profiling of Cerebrospinal Fluid Uncovers Biomarkers for Severity of Late Infantile Neuronal Ceroid Lipofuscinosis (CLN2, Batten Disease)
err2018-10-15
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errSindelar, Miriam; Dyke, Jonathan P.; Deeb, Ruba S.; Sondhi, Dolan; Kaminsky, Stephen M.; Kosofsky, Barry E.; Ballon, Douglas J.; Crystal, Ronald G.; Gross, Steven S.
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Disease characteristics and progression in patients with late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease: an observational cohort study
err2018-08-01
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errNickel, Miriam; Simonati, Alessandro; Jacoby, David; Lezius, Susanne; Kilian, Dirk; Van de Graaf, Benjamin; Pagovich, Odelya E.; Kosofsky, Barry; Yohay, Kaleb; Downs, Matthew; Slasor, Peter; Aiayi, Temitayo; Crystal, Ronald G.; Kohlschuetter, Alfried; Sondhi, Dolan; Schulz, Angela
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Intracerebral gene therapy in children with metachromatic leukodystrophy: Results of a phase I/II trial
err2018-02-01
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PREAI
errSevin, Caroline; Roujeau, Thomas; Cartier, Nathalie; Baugnon, Thomas; Adamsbaum, Catherine; Piraud, Monique; Martino, Sabata; Mouiller, Philippe; Couzinie, Celia; Bellesme, Celine; Lalande, Clemence Castaignede; Cormary, Carine; Souweidane, Mark M.; Colle, Marie-Anne; Adjali, Oumeya; Sondhi, Dolan; Crystal, Ronald G.; Aubourg, Patrick; Zerah, Michel
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Asymptotic neurodegeneration in CLN2 disease assessed by MRI cortical thickness histograms
err2018-02-01
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PREAI
errDyke, Jonathan P.; Voss, Henning U.; Sondhi, Dolan; Kaminsky, Stephen M.; Blatteis, Jacqlyn; Heier, Linda; Kosofsky, Barry; Casey, B. J.; Crystal, Ronald G.; Ballon, Douglas
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Radioiodinated Capsids Facilitate In Vivo Non-Invasive Tracking of Adeno-Associated Gene Transfer Vectors
err2017-01-06
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errKothari, P.; De, B. P.; He, B.; Chen, A.; Chiuchiolo, M. J.; Kim, D.; Nikolopoulou, A.; Amor-Coarasa, A.; Dyke, J. P.; Voss, H. U.; Kaminsky, S. M.; Foley, C. P.; Vallabhajosula, S.; Hu, B.; DiMagno, S. G.; Sondhi, D.; Crystal, R. G.; Babich, J. W.; Ballon, D.
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Anti-hIgE gene therapy of peanut-induced anaphylaxis in a humanized murine model of peanut allergy
err2016-12-01
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errPagovich, Odelya E.; Wang, Bo; Chiuchiolo, Maria J.; Kaminsky, Stephen M.; Sondhi, Dolan; Jose, Clarisse L.; Price, Christina C.; Brooks, Sarah F.; Mezey, Jason G.; Crystal, Ronald G.
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Intracerebral adeno-associated virus gene delivery of apolipoprotein E2 markedly reduces brain amyloid pathology in Alzheimer's disease mouse models
err2016-08-01
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PREAI
errZhao, Lingzhi; Gottesdiener, Andrew J.; Parmar, Mayur; Li, Mingjie; Kaminsky, Stephen M.; Chiuchiolo, Maria J.; Sondhi, Dolan; Sullivan, Patrick M.; Holtzman, David M.; Crystal, Ronald G.; Paul, Steven M.
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In Vivo Potency Assay for AAV-Based Gene Therapy Vectors
err2016-05-01
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errDe, Bishnu P.; Chen, Alvin; Rosenberg, Jonathan B.; Chiuchiolo, Maria; Van de Graaf, Benjamin; Pagovich, Odelya E.; Sondhi, Dolan; Russo, Carlo; Kaminsky, Stephen M.; Crystal, Ronald G.
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Optimization of Production of AAVrh.10 Viral Vectors
err2016-05-01
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errLee, Hyunmi; Quach, Lucy; Fan, Fan; Cram, Sara; Sondhi, Dolan; Crystal, Ronald; Kaminsky, Stephen
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Consequences of Infusion Time on Efficiency of Intravenous Delivery of Vector Genomes to the Liver
err2016-05-01
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errRosenberg, Jonathan B.; De, Bishnu P.; Quach, Lucy; Russo, Carol; Kaminsky, Stephen M.; Sondhi, Dolan; Crystal, Ronald G.
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Translation of an Adenovirus-Based Cocaine Vaccine dAd5GNE to a Clinical Trial
err2016-05-01
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errHavlicek, David F.; De, Bishnu; Rosenberg, Jonathan; Pagovich, Odelya; Sondhi, Dolan; Kaminsky, Stephen; Crystal, Ronald
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Long-Term Toxicology Evaluation of AAVrh.10hARSA Administration to the CNS of Nonhuman Primates to Treat Metachromatic Leukodystrophy
err2016-05-01
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errSondhi, Dolan; Rosenberg, Jonathan B.; De, Bishnu P.; Monette, Sebastien; Chen, Alvin; Flagiello, Thomas; Caffrey, Elisa; Kaminsky, Stephen M.; Aubourg, Patrick; Crystal, Ronald G.
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One-time Gene Therapy for Hereditary Angioedema
err2016-05-01
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errPagovich, Odelya E.; Qiu, Ting; Whaley, Adele S.; Russo, Anthony R.; Rosenberg, Jonathan; De, Bishnu P.; Russo, Carlo; Chiuchiolo, Maria J.; Sondhi, Dolan; Kaminsky, Stephen M.; Crystal, Ronald G.
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Brain Region-Specific Degeneration with Disease Progression in Late Infantile Neuronal Ceroid Lipofuscinosis (CLN2 Disease)
err2016-01-28
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errDyke, J. P.; Sondhi, D.; Voss, H. U.; Yohay, K.; Hollmann, C.; Mancenido, D.; Kaminsky, S. M.; Heier, L. A.; Rudser, K. D.; Kosofsky, B.; Casey, B. J.; Crystal, R. G.; Balton, D.
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