未登录 Small-molecule inhibition of glycogen synthase 1 for the treatment of Pompe disease and other glycogen storage disorders Ullman, Julie C.; Mellem, Kevin T.; Xi, Yannan; Ramanan, Vyas; Merritt, Hanne; Choy, Rebeca; Gujral, Tarunmeet; Young, Lyndsay E. A.; Blake, Kerrigan; Tep, Samnang; Homburger, Julian R.; O'Regan, Adam; Ganesh, Sandya; Wong, Perryn; Satterfield, Terrence F.; Lin, Baiwei; Situ, Eva; Yu, Cecile; Espanol, Bryan; Sarwaikar, Richa; Fastman, Nathan; Tzitzilonis, Christos; Lee, Patrick; Reiton, Daniel; Morton, Vivian; Santiago, Pam; Won, Walter; Powers, Hannah; Cummings, Beryl B.; Hoek, Maarten; Graham, Robert R.; Chandriani, Sanjay J.; Bainer, Russell; DePaoli-Roach, Anna A.; Roach, Peter J.; Hurley, Thomas D.; Sun, Ramon C.; Gentry, Matthew S.; Sinz, Christopher; Dick, Ryan A.; Noonberg, Sarah B.; Beattie, David T.; Morgans Jr, David J.; Green, Eric M. 分享 收藏
Small molecule inhibition of glycogen synthase 1 restores autophagolysosomal and metabolic pathway dysfunction in a mouse model of Pompe disease Ullman, Julie C.; Xi, Yannan; Mellem, Kevin T.; Merritt, Hanne; Choy, Rebeca; Gujral, Taru; Blake, Kerrigan; Tep, Samnang; O'Regan, Adam; Wong, Perryn; Wong, Casper; Pang, Lisa; Satterfield, Terrence F.; Lin, Baiwei; Situ, Eva; Hoek, Maarten; Chandriani, Sanjay J.; Bainer, Russell; Sinz, Christopher; Dick, Ryan; Noonberg, Sarah B.; Beattie, David; Morgans, David J., Jr.; Green, Eric M. 分享 收藏
Functional characterization of SMARCA4 variants identified by targeted exome-sequencing of 131,668 cancer patients Fernando, Tharu M.; Piskol, Robert; Bainer, Russell; Sokol, Ethan S.; Trabucco, Sally E.; Zhang, Qing; Trinh, Huong; Maund, Sophia; Kschonsak, Marc; Chaudhuri, Subhra; Modrusan, Zora; Januario, Thomas; Yauch, Robert L. 分享 收藏
Characterization and therapeutic implications of SMARCA4 mutations in cancer Fernando, Tharu M.; Piskol, Robert; Bainer, Russell; Sokol, Ethan; Trabucco, Sally; Zhang, Qing; Huong Trinh; Maund, Sophia; Kschonsak, Marc; Chaudhuri, Subhra; Januario, Tom; Modrusan, Zora; Yauch, Robert L. 分享 收藏
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A tension-mediated glycocalyx-integrin feedback loop promotes mesenchymal-like glioblastoma Barnes, J. Matthew; Kaushik, Shelly; Bainer, Russell O.; Sa, Jason K.; Woods, Elliot C.; Kai, FuiBoon; Przybyla, Laralynne; Lee, Mijeong; Lee, Hye Won; Tung, Jason C.; Maller, Ori; Barrett, Alexander S.; Lu, Kan V.; Lakins, Jonathon N.; Hansen, Kirk C.; Obernier, Kirsten; Alvarez-Buylla, Arturo; Bergers, Gabriele; Phillips, Joanna J.; Nam, Do-Hyun; Bertozzi, Carolyn R.; Weaver, Valerie M. 分享 收藏
Enhancer Activity Requires CBP/P300 Bromodomain-Dependent Histone H3K27 Acetylation 增强子活性需要CBP/P300溴结构域依赖性组蛋白H3K27乙酰化 Raisner, Ryan; Kharbanda, Samir; Jin, Lingyan; Jeng, Edwin; Chan, Emily; Merchant, Mark; Haverty, Peter M.; Bainer, Russell; Cheung, Tommy; Arnott, David; Flynn, E. Megan; Romero, F. Anthony; Magnuson, Steven; Gascoigne, Karen E. 分享 收藏
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Functional coding and noncoding drivers of EMT-mediated acquired drug resistance Bainer, Russell O.; Wilson, Catherine; Callow, Marinella; Feng, Siyu; Costa, Michael; Watanabe, Colin; Mayba, Oleg; Lin, Eva; Martin, Scott; Yauch, Bob; Bourgon, Richard; Klijn, Christiaan 分享 收藏
CRISPR whole-genome screening identifies new necroptosis regulators and RIPK1 alternative splicing Callow, Marinella G.; Watanabe, Colin; Wickliffe, Katherine E.; Bainer, Russell; Kummerfield, Sarah; Weng, Julie; Cuellar, Trinna; Janakiraman, Vasantharajan; Chen, Honglin; Chih, Ben; Liang, Yuxin; Haley, Benjamin; Newton, Kim; Costa, Michael R. 分享 收藏
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PRC2 mediated repression of SMARCA2 predicts for EZH2 inhibitor activity in tumors with SWI/SNF mutations Januario, Thomas; Ye, Xiaofen; Bainer, Russell; Alicke, Bruno; Solon, Margaret; Haley, Benjamin; Modrusan, Zora; Gould, Stephen; Koeppen, Hartmut; Yauch, Robert L. 分享 收藏
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