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收藏BMN 349, a small molecule inhibitor of Z alpha-1 antitrypsin polymerization, increases secretion and reduces intrahepatic inclusions in a mouse model of diseaseBMN 349,一种Z α-1抗胰蛋白酶聚合的小分子抑制剂,可增加分泌并减少疾病小鼠模型中的肝内包涵体
Handyside, Britta; Wenzel, Heather; Mackenzie, Donald; Chang, Catherine; Greenslade, Annie; Van Vleet, Jeremy; Heglar, Brian; Chen, Joseph C.; Zhang, Lening; Larimore, Kevin; Zhou, Huiyu; Trantcheva, Iva; Sims, Lawrence; Evans, Kristin; Fong, Sylvia; Kumar, Gyanendra; Annu, Kavya; Ronzoni, Riccardo; Irving, James A.; Wang, Bing; Bunting, Stuart; Lomas, David A.
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收藏Sulfonamides as N-Centered Radical Precursors for C-N Coupling Reactions To Generate Amidines
Deng, Guogang; Chen, Zhuo; Bai, Yifeng; Zhang, Lening; Xia, Dazhen; Duan, Shengzu; Chen, Wen; Zhang, Hongbin; Walsh, Patrick J.; Yang, Xiaodong
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收藏Impact of AAVMYBPC3 Gene Transfer on Heart Structure and Function in Human and Mouse Models of Hypertrophic Cardiomyopathy
Vitelli, Catherine; Zhang, Lening; Murphy, Ryan; Blus, Bartlomiej; Christianson, Terri; Giaramita, Alexander; Holtzinger, John; Handyside, Britta; May, Hannah; Ann Pham; Tu Nguyen; Zhou, Huiyu; Ntai, Ioanna; Mearini, Giulia; Ricotti, Valeria; Voit, Thomas; Eschenhagen, Thomas; Carrier, Lucie; Agarwal, Pooja; Bunting, Stuart; Sumandea, Marius
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收藏Of mice and men: Plasma phenylalanine reduction in PKU corrects neurotransmitter pathways in the brain
Berguig, Geoffrey Y.; Martin, Nathan T.; Creer, Athena Y.; Xie, Lin; Zhang, Lening; Murphy, Ryan; Pacheco, Glenn; Bullens, Sherry; Olbertz, Joy; Weng, Haoling H.
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收藏Multidrug resistant tumors-aimed theranostics on the basis of strong electrostatic attraction between resistant cells and nanomaterials
Liu, Shuwei; Wang, Lu; Li, Shuyao; Meng, Xuya; Sun, Bin; Zhang, Xue; Zhang, Lening; Liu, Yi; Lin, Min; Zhang, Hao; Yang, Bai
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收藏Facile Synthesis of Cu-In-S/ZnS Core/Shell Quantum Dots in 1-Dodecanethiol for Efficient Light-Emitting Diodes with an External Quantum Efficiency of 7.8%
Wang, Ze; Zhang, Xiaoyu; Xin, Wei; Yao, Dong; Liu, Yi; Zhang, Lening; Liu, Wenyan; Zhang, Wei; Zheng, Weitao; Yang, Bai; Zhang, Hao
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收藏A new method for comprehensive utilization of wood vinegar by distillation and liquid - liquid extraction一种通过蒸馏和液液萃取综合利用木醋液的新方法
Li, Zhanchao; Zhang, Lening; Chen, Guanyu; Wu, Lijie; Liu, Boyang; Li, Yue; Sun, Shuang; Zhang, Hanqi; Zhang, Zhiquan; Wang, Ziming
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收藏Nanosheet assembled hollow ZnFe2O4 microsphere as anode for lithium-ion batteries纳米片组装中空ZnFe2O4微球作为锂离子电池负极材料
Fang, Zhibo; Zhang, Lening; Qi, Hui; Yue, Huijuan; Zhang, Tong; Zhao, Xiaosen; Chen, Gang; Wei, Yingjin; Wang, Chunzhong; Zhang, Dong
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收藏Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice
Bunting, Stuart; Zhang, Lening; Xie, Lin; Bullens, Sherry; Mahimkar, Rajeev; Fong, Sylvia; Sandza, Krystal; Harmon, Danielle; Yates, Bridget; Handyside, Britta; Sihn, Choong-Ryoul; Galicia, Nicole; Tsuruda, Laurie; O'Neill, Charles A.; Bagri, Anil; Colosi, Peter; Long, Shinong; Vehar, Gordon; Carter, Barrie
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