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Sweat chloride reflects CFTR function and correlates with clinical outcomes following CFTR modulator treatment 汗氯离子水平反映CFTR功能,并与CFTR调节剂治疗后的临床结局相关。 Zemanick, Edith T.; Ramsey, Bonnie; Sands, Dorota; McKone, Edward F.; Taylor-Cousar, Jennifer L.; Mall, Marcus A.; Konstan, Michael W.; Nair, Nitin; Zhu, Jiaqiang; Arteaga-Solis, Emilio; Van Goor, Fredrick; McGarry, Lisa; Prieto-Centurion, Valentin; Sosnay, Patrick R.; Bozic, Carmen; Waltz, David; Mayer-Hamblett, Nicole 分享 收藏
Elexacaftor/Tezacaftor/Ivacaftor Treatment and Depression-related Events Ramsey, Bonnie; Correll, Christoph U.; DeMaso, David R.; McKone, Edward; Tullis, Elizabeth; Taylor-Cousar, Jennifer L.; Chu, Chenghao; Volkova, Nataliya; Ahluwalia, Neil; Waltz, David; Tian, Simon; Mall, Marcus A. 分享 收藏
Long-term safety and efficacy of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis and at least one F508del allele: 144-week interim results from a 192-week open-label extension study Daines, Cori L.; Tullis, Elizabeth; Costa, Stefano; Linnemann, Rachel W.; Mall, Marcus A.; McKone, Edward F.; Polineni, Deepika; Quon, Bradley S.; Ringshausen, Felix C.; Rowe, Steven M.; Selvadurai, Hiran; Taylor-Cousar, Jennifer L.; Withers, Nicholas J.; Ahluwalia, Neil; Moskowitz, Samuel M.; Prieto-Centurion, Valentin; Tan, Yaoyuan Vincent; Tian, Simon; Weinstock, Tanya; Xuan, Fengjuan; Zhang, Yaohua; Ramsey, Bonnie; Griese, Matthias 分享 收藏
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Upper airway microbiota development in infants with cystic fibrosis diagnosed by newborn screen Harris, J. Kirk; Wagner, Brandie D.; Robertson, Charles E.; Stevens, Mark J.; Lingard, Conor; Borowitz, Drucy; Leung, Daniel H.; Heltshe, Sonya L.; Ramsey, Bonnie W.; Zemanick, Edith T. 分享 收藏
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Safety and efficacy of vanzacaftor-tezacaftor-deutivacaftor in adults with cystic fibrosis: randomised, double-blind, controlled, phase 2 trials Uluer, Ahmet Z.; MacGregor, Gordon; Azevedo, Pilar; Indihar, Veronica; Keating, Claire; Mall, Marcus A.; McKone, Edward F.; Ramsey, Bonnie W.; Rowe, Steven M.; Rubenstein, Ronald C.; Taylor-Cousar, Jennifer L.; Tullis, Elizabeth; Yonker, Lael M.; Chu, Chenghao; Lam, Anna P.; Nair, Nitin; Sosnay, Patrick R.; Tian, Simon; Van Goor, Fredrick; Viswanathan, Lakshmi; Waltz, David; Wang, Linda T.; Xi, Yingmei; Billings, Joanne; Horsley, Alexander 分享 收藏
Access to Chimeric Antigen Receptor T Cell Clinical Trials in Underrepresented Populations: A Multicenter Cohort Study of Pediatric and Young Adult Acute Lymphobastic Leukemia Patients 在代表性不足的人群中获得嵌合抗原受体T细胞临床试验: 儿童和年轻成人急性淋巴细胞白血病患者的多中心队列研究 Hall, Anurekha G.; Winestone, Lena E.; Sullivan, Erin M.; Wu, Qian; Lamble, Adam J.; Walters, Mark C.; Aguayo-Hiraldo, Paibel; Conde, Lourdes Baez; Coker, Tumaini R.; Dornsife, Dana; Keating, Amy K.; Merino, Diana M.; Ramsey, Bonnie; Park, Julie R.; Agrawal, Anurag K. 分享 收藏
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Triple Therapy for Cystic Fibrosis Phe508del-Gating and -Residual Function Genotypes Barry, Peter J.; Mall, Marcus A.; Alvarez, Antonio; Colombo, Carla; de Winter-de Groot, Karin M.; Fajac, Isabelle; McBennett, Kimberly A.; McKone, Edward F.; Ramsey, Bonnie W.; Sutharsan, Sivagurunathan; Taylor-Cousar, Jennifer L.; Tullis, Elizabeth; Ahluwalia, Neil; Jun, Lucy S.; Moskowitz, Samuel M.; Prieto-Centurion, Valentin; Tian, Simon; Waltz, David; Xuan, Fengjuan; Zhang, Yaohua; Rowe, Steven M.; Polineni, Deepika 分享 收藏