未登录 分享 收藏
The regulatory role of ACP5 in the diesel exhaust particle-induced AHR inflammatory signaling pathway in a human bronchial epithelial cell line (vol 15, 8826, 2025) ACP5在柴油尾气颗粒诱导的AHR炎症信号通路中的调控作用(卷15,8826,2025) Yu, Aaron; Yoon, Dankyu; An, Hye Bin; Choi, Uimook; Heo, Hye-Ryeon; Chae, Dong-Hoon; Park, Hyun Sung; Park, Jae Han; Han, Myoung Hee; Heo, Jiyoung; Cho, Keonwoo; Park, Ki-Sun; Yoo, Hee Min; Kim, Hyung-Sik; Kang, Kyung-Sun; Oh, Mi-Kyung; Lim, Hyun Joung 分享 收藏
The regulatory role of ACP5 in the diesel exhaust particle-induced AHR inflammatory signaling pathway in a human bronchial epithelial cell line Yu, Aaron; Yoon, Dankyu; An, Hye Bin; Choi, Uimook; Heo, Hye-Ryeon; Chae, Dong-Hoon; Park, Hyun Sung; Park, Jae Han; Han, Myoung Hee; Heo, Jiyoung; Cho, Keonwoo; Park, Ki-Sun; Yoo, Hee Min; Kim, Hyung-Sik; Kang, Kyung-Sun; Oh, Mi-Kyung; Lim, Hyun Joung; Yu, Kyung-Rok 分享 收藏
High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease 造血干细胞的高保真无PAMless碱基编辑治疗慢性肉芽肿病 Bzhilyanskaya, Vera; Ma, Linyuan; Liu, Siyuan; Fox, Lauren R.; Whittaker, Madelynn N.; Meis, Ronald J.; Choi, Uimook; Lawson, Amanda; Ma, Michelle; Theobald, Narda; Burkett, Sandra; Sweeney, Colin L.; Lazzarotto, Cicera R.; Tsai, Shengdar Q.; Lack, Justin B.; Wu, Xiaolin; Dahl, Gary A.; Malech, Harry L.; Kleinstiver, Benjamin P.; De Ravin, Suk See 分享 收藏
Impact of CRISPR/HDR editing versus lentiviral transduction on long-term engraftment and clonal dynamics of HSPCs in rhesus macaques (vol 31, pg 455, 2024) Lee, Byung-Chul; Gin, Ashley; Wu, Chuanfeng; Singh, Komudi; Grice, Max; Mortlock, Ryland; Abraham, Diana; Fan, Xing; Zhou, Yifan; AlJanahi, Aisha; Choi, Uimook; DeRavin, Suk See; Shin, Taehoon; Hong, Sogun; Dunbar, Cynthia E. 分享 收藏
Impact of CRISPR/HDR editing versus lentiviral transduction on long-term engraftment and clonal dynamics of HSPCs in rhesus macaques Lee, Byung-Chul; Gin, Ashley; Wu, Chuanfeng; Singh, Komudi; Grice, Max; Mortlock, Ryland; Abraham, Diana; Fan, Xing; Zhou, Yifan; AlJanahi, Aisha; Choi, Uimook; DeRavin, Suk See; Shin, Taehoon; Hong, Sogun; Dunbar, Cynthia E. 分享 收藏
Self-organized yolk sac-like organoids allow for scalable generation of multipotent hematopoietic progenitor cells from induced pluripotent stem cells 自组织的卵黄囊样类器官允许从诱导的多能干细胞可扩展地生成多能造血祖细胞 Tamaoki, Naritaka; Siebert, Stefan; Maeda, Takuya; Ha, Ngoc-Han; Good, Meghan L.; Huang, Yin; Vodnala, Suman K.; Haro-Mora, Juan J.; Uchida, Naoya; Tisdale, John F.; Sweeney, Colin L.; Choi, Uimook; Brault, Julie; Koontz, Sherry; Malech, Harry L.; Yamazaki, Yasuhiro; Isonaka, Risa; Goldstein, David S.; Kimura, Masaki; Takebe, Takanori; Zou, Jizhong; Stroncek, David F.; Robey, Pamela G.; Kruhlak, Michael J.; Restifo, Nicholas P.; Vizcardo, Raul 分享 收藏
CRISPR-Cas9-AAV versus lentivector transduction for genome modification of X-linked severe combined immunodeficiency hematopoietic stem cells Brault, Julie; Liu, Taylor; Liu, Siyuan; Lawson, Amanda; Choi, Uimook; Kozhushko, Nikita; Bzhilyanskaya, Vera; Pavel-Dinu, Mara; Meis, Ronald J.; Eckhaus, Michael A.; Burkett, Sandra S.; Bosticardo, Marita; Kleinstiver, Benjamin P.; Notarangelo, Luigi D.; Lazzarotto, Cicera R.; Tsai, Shengdar Q.; Wu, Xiaolin; Dahl, Gary A.; Porteus, Matthew H.; Malech, Harry L.; De Ravin, Suk See 分享 收藏
Lentivector cryptic splicing mediates increase in CD34+clones expressing truncated HMGA2 in human X-linked severe combined immunodeficiency De Ravin, Suk See; Liu, Siyuan; Sweeney, Colin L.; Brault, Julie; Whiting-Theobald, Narda; Ma, Michelle; Liu, Taylor; Choi, Uimook; Lee, Janet; O'Brien, Sandra Anaya; Quackenbush, Priscilla; Estwick, Tyra; Karra, Anita; Docking, Ethan; Kwatemaa, Nana; Guo, Shuang; Su, Ling; Sun, Zhonghe; Zhou, Sheng; Puck, Jennifer; Cowan, Morton J.; Notarangelo, Luigi D.; Kang, Elizabeth; Malech, Harry L.; Wu, Xiaolin 分享 收藏
分享 收藏
Extracellular Vesicles from Thapsigargin-Treated Mesenchymal Stem Cells Ameliorated Experimental Colitis via Enhanced Immunomodulatory Properties 来自Thapsigargin处理的间充质干细胞的细胞外囊泡通过增强的免疫调节特性改善了实验性结肠炎 Joo, Hansol; Oh, Mi-Kyung; Kang, Ji Yeon; Park, Hyun Sung; Chae, Dong-Hoon; Kim, Jieun; Lee, Jong-Hee; Yoo, Hee Min; Choi, Uimook; Kim, Do-Kyun; Lee, Hakmo; Kim, Sungjoo; Yu, Kyung-Rok 分享 收藏
NADPH oxidase correction by mRNA transfection of apheresis granulocytes in chronic granulomatous disease De Ravin, Suk See; Brault, Julie; Meis, Ronald J.; Li, Linhong; Theobald, Narda; Bonifacino, Aylin C.; Lei, Hong; Liu, Taylor Q.; Koontz, Sherry; Corsino, Cristina; Zarakas, Marissa A.; Desai, Jigar, V; Clark, Aaron B.; Choi, Uimook; Metzger, Mark E.; West, Kamille; Highfill, Steven L.; Kang, Elizabeth; Kuhns, Douglas B.; Lionakis, Michail S.; Stroncek, David F.; Dunbar, Cynthia E.; Tisdale, John F.; Donahue, Robert E.; Dahl, Gary A.; Malech, Harry L. 分享 收藏
Defining a new immune deficiency syndrome: MAN2B2-CDG Verheijen, Jan; Wong, Sunnie Y.; Rowe, Jared H.; Raymond, Kimiyo; Stoddard, Jennifer; Delmonte, Ottavia M.; Bosticardo, Marita; Dobbs, Kerry; Niemela, Julie; Calzoni, Enrica; Pai, Sung-Yun; Choi, Uimook; Yamazaki, Yasuhiro; Comeau, Anne Marie; Janssen, Erin; Henderson, Lauren; Hazen, Melissa; Berry, Gerard; Rosenzweig, Sergio D.; Aldhekri, Hasan Hamdan; He, Miao; Notarangelo, Luigi D.; Morava, Eva 分享 收藏
Lentiviral gene therapy for X-linked chronic granulomatous disease Kohn, Donald B.; Booth, Claire; Kang, Elizabeth M.; Pai, Sung-Yun; Shaw, Kit L.; Santilli, Giorgia; Armant, Myriam; Buckland, Karen F.; Choi, Uimook; De Ravin, Suk See; Dorsey, Morna J.; Kuo, Caroline Y.; Leon-Rico, Diego; Rivat, Christine; Izotova, Natalia; Gilmour, Kimberly; Snell, Katie; Dip, Jinhua Xu-Bayford; Darwish, Jinan; Morris, Emma C.; Terrazas, Dayna; Wang, Leo D.; Bauser, Christopher A.; Paprotka, Tobias; Kuhns, Douglas B.; Gregg, John; Raymond, Hayley E.; Everett, John K.; Honnet, Geraldine; Biasco, Luca; Newburger, Peter E.; Bushman, Frederic D.; Grez, Manuel; Gaspar, H. Bobby; Williams, David A.; Malech, Harry L.; Galy, Anne; Thrasher, Adrian J.; Buckland, Karen F.; Bauser, Christopher A.; Honnet, Geraldine; Grez, Manuel; Gaspar, H. Bobby; Galy, Anne; Thrasher, Adrian J. 分享 收藏
Myeloid Conditioning with c-kit-Targeted CAR-T Cells Enables Donor Stem Cell Engraftment Arai, Yasuyuki; Choi, Uimook; Corsino, Cristina I.; Koontz, Sherry M.; Tajima, Masaki; Sweeney, Colin L.; Black, Mary A.; Feldman, Steven A.; Dinauer, Mary C.; Malech, Harry L. 分享 收藏
分享 收藏
Targeted Repair of CYBB in X-CGD iPSCs Requires Retention of Intronic Sequences for Expression and Functional Correction Sweeney, Colin L.; Zou, Jizhong; Choi, Uimook; Merling, Randall K.; Liu, Alexander; Bodansky, Aaron; Burkett, Sandra; Kim, Jung-Woong; De Ravin, Suk See; Malech, Harry L. 分享 收藏
CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease De Ravin, Suk See; Li, Linhong; Wu, Xiaolin; Choi, Uimook; Allen, Cornell; Koontz, Sherry; Lee, Janet; Theobald-Whiting, Narda; Chu, Jessica; Garofalo, Mary; Sweeney, Colin; Kardava, Lela; Moir, Susan; Viley, Angelia; Natarajan, Pachai; Su, Ling; Kuhns, Douglas; Zarember, Kol A.; Peshwa, Madhusudan V.; Malech, Harry L. 分享 收藏
Gene-edited pseudogene resurrection corrects p47phox-deficient chronic granulomatous disease Merling, Randall K.; Kuhns, Douglas B.; Sweeney, Colin L.; Wu, Xiaolin; Burkett, Sandra; Chu, Jessica; Lee, Janet; Koontz, Sherry; Di Pasquale, Giovanni; Afione, Sandra A.; Chiorini, John A.; Kang, Elizabeth M.; Choi, Uimook; De Ravin, Suk See; Malech, Harry L. 分享 收藏
Therapeutic Level CRISPR-Oligomer-Mediated Correction of X-CGD Patient Hematopoietic Stem Cells Using Non-Viral, cGMP Compliant, Scalable, and Closed System Li, Linhong; De Ravin, Suk See; Allen, Cornell; Choi, Uimook; Koontz, Sherry; Theobald, Narda; Lee, Janet; Viley, Angelia; Natarajan, Pachai; NewCombe, Hannah; McMichael, Ashley; Wu, Xiaolin; Malech, Harry L.; Peshwa, Madhusudan V. 分享 收藏