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Pediatric adapted risk index to predict 2-year transplant-related mortality post-HSCT in children Elfeky, Reem; Builes, Natalia; Pearce, Rachel; Kania, Soumya; Nademi, Zohreh; Lucchini, Giovanna; Chiesa, Robert; Amrolia, Persis; Sorror, Mohamed; Veys, Paul; Rao, Kanchan 分享 收藏
Phase 1 clinical trial of CRISPR-engineered CAR19 universal T cells for treatment of children with refractory B cell leukemia CRISPR基因CAR19通用T细胞治疗儿童难治性b细胞白血病的1期临床试验 Ottaviano, Giorgio; Georgiadis, Christos; Gkazi, Soragia Athina; Syed, Farhatullah; Zhan, Hong; Etuk, Annie; Preece, Roland; Chu, Jan; Kubat, Agnieszka; Adams, Stuart; Veys, Paul; Vora, Ajay; Rao, Kanchan; Qasim, Waseem 分享 收藏
Epstein-Barr Virus Reactivation After Paediatric Haematopoietic Stem Cell Transplantation: Risk Factors and Sensitivity Analysis of Mathematical Model Kania, Soumya P.; Silva, Juliana M. F.; Charles, Oscar J.; Booth, John; Cheung, S. Y. Amy; Yates, James W. T.; Worth, Austen; Breuer, Judith; Klein, Nigel; Amrolia, Persis J.; Veys, Paul; Standing, Joseph F. 分享 收藏
Linking gastrointestinal microbiota and metabolome dynamics to clinical outcomes in paediatric haematopoietic stem cell transplantation Vaitkute, Gintare; Panic, Gordana; Alber, Dagmar G.; Faizura-Yeop, Intan; Cloutman-Green, Elaine; Swann, Jonathan; Veys, Paul; Standing, Joseph F.; Klein, Nigel; Bajaj-Elliott, Mona 分享 收藏
Retrospective, Landmark Analysis of Long-term Adult Morbidity Following Allogeneic HSCT for Inborn Errors of Immunity in Infancy and Childhood Day, James W.; Elfeky, Reem; Nicholson, Bethany; Goodman, Rupert; Pearce, Rachel; Fox, Thomas A.; Worth, Austen; Booth, Claire; Veys, Paul; Carpenter, Ben; Hough, Rachael; Gaspar, H. Bobby; Titman, Penny; Ridout, Deborah; Workman, Sarita; Hernandes, Fernando; Sandford, Kit; Laurence, Arian; Campbell, Mari; Burns, Siobhan O.; Morris, Emma C. 分享 收藏
Hematopoietic cell transplantation in severe combined immunodeficiency: The SCETIDE 2006-2014 European cohort 严重联合免疫缺陷的造血细胞移植: SCETIDE 2006 2014的欧洲队列 Lankester, Arjan C.; Neven, Benedicte; Mahlaoui, Nizar; von Asmuth, Erik G. J.; Courteille, Virginie; Alligon, Mikael; Albert, Michael H.; Serra, Isabelle Badell; Bader, Peter; Balashov, Dmitry; Beier, Rita; Bertrand, Yves; Blanche, Stephane; Bordon, Victoria; Bredius, Robbert G.; Cant, Andrew; Cavazzana, Marina; Diaz-de-Heredia, Cristina; Dogu, Figen; Ehlert, Karoline; Entz-Werle, Natacha; Fasth, Anders; Ferrua, Francesca; Ferster, Alina; Formankova, Renata; Friedrich, Wilhelm; Gonzalez-Vicent, Marta; Gozdzik, Jolanta; Gungor, Tayfun; Hoenig, Manfred; Ikinciogullari, Aydan; Kalwak, Krzysztof; Kansoy, Savas; Kupesiz, Alphan; Lanfranchi, Arnalda; Lindemans, Caroline A.; Meisel, Roland; Michel, Gerard; Miranda, Nuno A. A.; Moraleda, Jose; Moshous, Despina; Pichler, Herbert; Rao, Kanchan; Sedlacek, Petr; Slatter, Mary; Soncini, Elena; Speckmann, Carsten; Sundin, Mikael; Toren, Amos; Vettenranta, Kim; Worth, Austen; Yesilipek, Mehmet A.; Zecca, Marco; Porta, Fulvio; Schulz, Ansgar; Veys, Paul; Fischer, Alain; Gennery, Andrew R. 分享 收藏
Primary graft failure, but not relapse, may be identified by early chimerism following double cord blood unit transplantation Hough, Rachael; Lopes, Andre; Patrick, Pip; Russell, Nigel; Raj, Kavita; Tholouli, Eleni; Snowden, John A.; Collin, Matthew; El-Mehidi, Nadjet; Lawrie, Anthony; Clifton-Hadley, Laura; Veys, Paul; Craddock, Charles; Mackinnon, Stephen; Cook, Gordon; Shaw, Bronwen; Marks, David 分享 收藏
Impact of in Vivo Lymphodepletion on Outcome in Children with Nonmalignant Disorders Receiving Peripheral Blood Stem Cell Transplantation Ottaviano, Giorgio; Achini-Gutzwiller, Federica; Kalwak, Krzysztof; Lanino, Edoardo; Faraci, Maura; Rao, Kanchan; Chiesa, Robert; Amrolia, Persis; Bonanomi, Sonia; Rovelli, Attilio; Veys, Paul; Lankester, Arjan; Balduzzi, Adriana; Lucchini, Giovanna 分享 收藏
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CAR T cells with dual targeting of CD19 and CD22 in pediatric and young adult patients with relapsed or refractory B cell acute lymphoblastic leukemia: a phase 1 trial 儿童和年轻成人复发或难治性b细胞急性淋巴细胞白血病患者中CD19和CD22双重靶向的CAR T细胞: 1期试验 Cordoba, Shaun; Onuoha, Shimobi; Thomas, Simon; Pignataro, Daniela Soriano; Hough, Rachael; Ghorashian, Sara; Vora, Ajay; Bonney, Denise; Veys, Paul; Rao, Kanchan; Lucchini, Giovanna; Chiesa, Robert; Chu, Jan; Clark, Liz; Fung, Mei Mei; Smith, Koval; Peticone, Carlotta; Al-Hajj, Muhammad; Baldan, Vania; Ferrari, Mathieu; Srivastava, Saket; Jha, Ram; Vargas, Frederick Arce; Duffy, Kevin; Day, William; Virgo, Paul; Wheeler, Lucy; Hancock, Jeremy; Farzaneh, Farzin; Domning, Sabine; Zhang, Yiyun; Khokhar, Nushmia Z.; Peddareddigari, Vijay G. R.; Wynn, Robert; Pule, Martin; Amrolia, Persis J. 分享 收藏
Standardizing Definitions of Hematopoietic Recovery, Graft Rejection, Graft Failure, Poor Graft Function, and Donor Chimerism in Allogeneic Hematopoietic Cell Transplantation: A Report on Behalf of the American Society for Transplantation and Cellular Therapy 异基因造血细胞移植中造血恢复,移植排斥,移植失败,移植功能不良和供体嵌合的标准化定义: 代表美国移植和细胞治疗学会的报告 Kharfan-Dabaja, Mohamed A.; Kumar, Ambuj; Ayala, Ernesto; Aljurf, Mahmoud; Nishihori, Taiga; Marsh, Rebecca; Burroughs, Lauri M.; Majhail, Navneet; Al-Homsi, A. Samer; Al-Kadhimi, Zaid S.; Bar, Merav; Bertaina, Alice; Boelens, Jaap J.; Champlin, Richard; Chaudhury, Sonali; DeFilipp, Zachariah; Dholaria, Bhagirathbhai; El-Jawahri, Areej; Fanning, Suzanne; Fraint, Ellen; Gergis, Usama; Giralt, Sergio; Hamilton, Betty K.; Hashmi, Shahrukh K.; Horn, Biljana; Inamoto, Yoshihiro; Jacobsohn, David A.; Jain, Tania; Johnston, Laura; Kanate, Abraham S.; Kansagra, Ankit; Kassim, Adetola; Kean, Leslie S.; Kitko, Carrie L.; Knight-Perry, Jessica; Kurtzberg, Joanne; Liu, Hien; MacMillan, Margaret L.; Mahmoudjafari, Zahra; Mielcarek, Marco; Mohty, Mohamad; Nagler, Arnon; Nemecek, Eneida; Olson, Timothy S.; Oran, Betul; Perales, Miguel-Angel; Prockop, Susan E.; Pulsipher, Michael A.; Pusic, Iskra; Riches, Marcie L.; Rodriguez, Cesar; Romee, Rizwan; Rondon, Gabriela; Saad, Ayman; Shah, Nina; Shaw, Peter J.; Shenoy, Shalini; Sierra, Jorge; Talano, Julie; Verneris, Michael R.; Veys, Paul; Wagner, John E.; Savani, Bipin N.; Hamadani, Mehdi; Carpenter, Paul A. 分享 收藏
Hematopoietic Stem Cell Transplantation Resolves the Immune Deficit Associated with STAT3-Dominant-Negative Hyper-IgE Syndrome 造血干细胞移植可解决与STAT3-Dominant-Negative高IgE综合征相关的免疫缺陷 Harrison, Stephanie C.; Tsilifis, Christo; Slatter, Mary A.; Nademi, Zohreh; Worth, Austen; Veys, Paul; Ponsford, Mark J.; Jolles, Stephen; Al-Herz, Waleed; Flood, Terence; Cant, Andrew J.; Doffinger, Rainer; Barcenas-Morales, Gabriela; Carpenter, Ben; Hough, Rachael; Haraldsson, Asgeir; Heimall, Jennifer; Grimbacher, Bodo; Abinun, Mario; Gennery, Andrew R. 分享 收藏
Proceedings From the First International Workshop at Sidra Medicine: Engineered Immune Cells in Cancer Immunotherapy (EICCI): From Discovery to Off-the-Shelf Development, 15th-16th February 2019, Doha, Qatar Sidra Medicine第一届国际研讨会论文集: 癌症免疫治疗中的工程免疫细胞 (EICCI): 从发现到现成的开发,2019年2月15-16日,卡塔尔多哈 Guerrouahen, Bella; Elnaggar, Muhammad; Al-Mohannadi, Anjud; Kizhakayil, Dhanya; Bonini, Chiara; Benjamin, Reuben; Brentjens, Renier; Buchholz, Christian J.; Casorati, Giulia; Ferrone, Soldano; Locke, Frederick L.; Martin, Francisco; Schambach, Axel; Turtle, Cameron; Veys, Paul; van der Vliet, Hans J.; Maccalli, Cristina 分享 收藏
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Genome-edited, donor-derived allogeneic anti-CD19 chimeric antigen receptor T cells in paediatric and adult B-cell acute lymphoblastic leukaemia: results of two phase 1 studies 基因组编辑,供体来源的同种异体anti-CD19嵌合抗原受体T细胞在儿童和成人b细胞急性淋巴细胞白血病中的应用: 两项1期研究的结果 Benjamin, Reuben; Graham, Charlotte; Yallop, Deborah; Jozwik, Agnieszka; Mirci-Danicar, Oana C.; Lucchini, Giovanna; Pinner, Danielle; Jain, Nitin; Kantarjian, Hagop; Boissel, Nicolas; Maus, Marcela V.; Frigault, Matthew J.; Baruchel, Andre; Mohty, Mohamad; Gianella-Borradori, Athos; Binlich, Florence; Balandraud, Svetlana; Vitry, Fabien; Thomas, Elisabeth; Philippe, Anne; Fouliard, Sylvain; Dupouy, Sandra; Marchiq, Ibtissam; Almena-Carrasco, Maria; Ferry, Nicolas; Arnould, Sylvain; Konto, Cyril; Veys, Paul; Qasim, Waseem 分享 收藏
Outcome of Non-hematological Autoimmunity After Hematopoietic Cell Transplantation in Children with Primary Immunodeficiency Lum, Su Han; Elfeky, Reem; Achini, Federica R.; Margarit-Soler, Adriana; Cinicola, Bianca; Perez-Heras, Inigo; Nademi, Zohreh; Flood, Terry; Cheetham, Tim; Worth, Austen; Qasim, Waseem; Amin, Rakesh; Rao, Kanchan; Chiesa, Robert; Bredius, Robbert G. M.; Amrolia, Persis; Abinun, Mario; Hambleton, Sophie; Veys, Paul; Gennery, Andrew R.; Lankester, Arjan; Slatter, Mary 分享 收藏
Haematopoietic Stem Cell Transplantation for DNA Ligase 1 Deficiency Silva, Juliana M. F.; Jones, Alison; Sibson, Keith; Bibi, Shahnaz; Jeggo, Penny; Woodbine, Lisa; Ahsan, Gulrukh; Gilmour, Kimberly C.; Rao, Kanchan; Chiesa, Robert; Lucchini, Giovanna; Veys, Paul; Worth, Austen; Amrolia, Persis J. 分享 收藏
HSCT provides effective treatment for lymphoproliferative disorders in children with primary immunodeficiency Prunotto, Giulia; Offor, Ugonna T.; Samarasinghe, Sujith; Wynn, Robert; Vora, Ajay; Carpenter, Ben; Gowdy, Claire; McHugh, Kieran; Windebank, Kevin P.; Rovelli, Attilio Maria; Slatter, Mary A.; Gennery, Andrew R.; Veys, Paul; Bacon, Chris M.; Bomken, Simon; Lucchini, Giovanna 分享 收藏