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A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID Cesana, Daniela; Cicalese, Maria Pia; Calabria, Andrea; Merli, Pietro; Caruso, Roberta; Volpin, Monica; Rudilosso, Laura; Migliavacca, Maddalena; Barzaghi, Federica; Fossati, Claudia; Gazzo, Francesco; Pizzi, Simone; Ciolfi, Andrea; Bruselles, Alessandro; Tucci, Francesca; Spinozzi, Giulio; Pais, Giulia; Benedicenti, Fabrizio; Barcella, Matteo; Merelli, Ivan; Gallina, Pierangela; Giannelli, Stefania; Dionisio, Francesca; Scala, Serena; Casiraghi, Miriam; Strocchio, Luisa; Vinti, Luciana; Pacillo, Lucia; Draghi, Eleonora; Cesana, Marcella; Riccardo, Sara; Colantuono, Chiara; Six, Emmanuelle; Cavazzana, Marina; Carlucci, Filippo; Schmidt, Manfred; Cancrini, Caterina; Ciceri, Fabio; Vago, Luca; Cacchiarelli, Davide; Gentner, Bernhard; Naldini, Luigi; Tartaglia, Marco; Montini, Eugenio; Locatelli, Franco; Aiuti, Alessandro 分享 收藏
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Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study Kanter, Julie; Thompson, Alexis A.; Pierciey, Francis J., Jr.; Hsieh, Matthew; Uchida, Naoya; Leboulch, Philippe; Schmidt, Manfred; Bonner, Melissa; Guo, Ruiting; Miller, Alex; Ribeil, Jean-Antoine; Davidson, David; Asmal, Mohammed; Walters, Mark C.; Tisdale, John F. 分享 收藏
Betibeglogene Autotemcel Gene Therapy for Non-β0/β0 Genotype β-Thalassemia Betibeglogene Autotemcel基因治疗非 β0/β0基因型 β 地中海贫血 Locatelli, Franco; Thompson, Alexis A.; Kwiatkowski, Janet L.; Porter, John B.; Thrasher, Adrian J.; Hongeng, Suradej; Sauer, Martin G.; Thuret, Isabelle; Lal, Ashutosh; Algeri, Mattia; Schneiderman, Jennifer; Olson, Timothy S.; Carpenter, Ben; Amrolia, Persis J.; Anurathapan, Usanarat; Schambach, Axel; Chabannon, Christian; Schmidt, Manfred; Labik, Ivan; Elliot, Heidi; Guo, Ruiting; Asmal, Mohammed; Colvin, Richard A.; Walters, Mark C. 分享 收藏
Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial Magrin, Elisa; Semeraro, Michaela; Hebert, Nicolas; Joseph, Laure; Magnani, Alessandra; Chalumeau, Anne; Gabrion, Aurelie; Roudaut, Cecile; Marouene, Jouda; Lefrere, Francois; Diana, Jean-Sebastien; Denis, Adeline; Neven, Benedicte; Funck-Brentano, Isabelle; Negre, Olivier; Renolleau, Sylvain; Brousse, Valentine; Kiger, Laurent; Touzot, Fabien; Poirot, Catherine; Bourget, Philippe; El Nemer, Wassim; Blanche, Stephane; Treluyer, Jean-Marc; Asmal, Mohammed; Walls, Courtney; Beuzard, Yves; Schmidt, Manfred; Hacein-Bey-Abina, Salima; Asnafi, Vahid; Guichard, Isabelle; Poiree, Maryline; Monpoux, Fabrice; Touraine, Philippe; Brouzes, Chantal; de Montalembert, Mariane; Payen, Emmanuel; Six, Emmanuelle; Ribeil, Jean-Antoine; Miccio, Annarita; Bartolucci, Pablo; Leboulch, Philippe; Cavazzana, Marina 分享 收藏
Interleukin-10 receptor signaling promotes the maintenance of a PD-1int TCF-1+ CD8+ T cell population that sustains anti-tumor immunity Hanna, Bola S.; Llao-Cid, Laura; Iskar, Murat; Roessner, Philipp M.; Klett, Lara C.; Wong, John K. L.; Paul, Yashna; Ioannou, Nikolaos; Ozturk, Selcen; Mack, Norman; Kalter, Verena; Colomer, Dolors; Campo, Elias; Bloehdorn, Johannes; Stilgenbauer, Stephan; Dietrich, Sascha; Schmidt, Manfred; Gabriel, Richard; Rippe, Karsten; Feuerer, Markus; Ramsay, Alan G.; Lichter, Peter; Zapatka, Marc; Seiffert, Martina 分享 收藏
Comprehensive genomic characterization of gene therapy-induced T-cell acute lymphoblastic leukemia (vol 34, pg 2785, 2020) Horak, Peter; Uhrig, Sebastian; Witzel, Maximilian; Gil-Farina, Irene; Hutter, Barbara; Rath, Tim; Gieldon, Laura; Balasubramanian, Gnana Prakash; Pastor, Xavier; Heilig, Christoph E.; Richter, Daniela; Schrock, Evelin; Ball, Claudia R.; Brors, Benedikt; Braun, Christian J.; Albert, Michael H.; Scholl, Claudia; von Kalle, Christof; Schmidt, Manfred; Frohling, Stefan; Klein, Christoph; Glimm, Hanno 分享 收藏
Spatially clustered loci with multiple enhancers are frequent targets of HIV-1 integration (vol 10, 4059, 2019) Lucic, Bojana; Chen, Heng-Chang; Kuzman, Maja; Zorita, Eduard; Wegner, Julia; Minneker, Vera; Wang, Wei; Fronza, Raffaele; Laufs, Stefanie; Schmidt, Manfred; Stadhouders, Ralph; Roukos, Vassilis; Vlahovicek, Kristian; Filion, Guillaume J.; Lusic, Marina 分享 收藏
ELEANOR: A multi-national, prospective, non-interventional study (NIS) in patients with human epidermal growth factor receptor (HER2) positive, early breast cancer (eBC) observing real-life extended adjuvant treatment with neratinib and concurrent use of the eHealth solution CANKADO Harbeck, N.; Lueftner, D.; Breitenstein, U.; Jackisch, C.; Mueller, V.; Schmidt, M.; Balic, M.; Rinnerthaler, G.; Schwitter, M.; Zaman, K.; Wrobel, D.; Guth, D.; Terhaag, J.; Zaiss, M.; Schinkoethe, T.; Bartsch, R. 分享 收藏
Longitudinal analyses of CLL in mice identify leukemia-related clonal changes including a Myc gain predicting poor outcome in patients Oeztuerk, Selcen; Paul, Yashna; Afzal, Saira; Gil-Farina, Irene; Jauch, Anna; Bruch, Peter-Martin; Kalter, Verena; Hanna, Bola; Arseni, Lavinia; Roessner, Philipp M.; Schmidt, Manfred; Stilgenbauer, Stephan; Dietrich, Sascha; Lichter, Peter; Zapatka, Marc; Seiffert, Martina 分享 收藏
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency 自体慢病毒基因治疗腺苷脱氨酶缺乏症 Kohn, D. B.; Booth, C.; Shaw, K. L.; Xu-Bayford, J.; Garabedian, E.; Trevisan, V.; Carbonaro-Sarracino, D. A.; Soni, K.; Terrazas, D.; Snell, K.; Ikeda, A.; Leon-Rico, D.; Moore, T. B.; Buckland, K. F.; Shah, A. J.; Gilmour, K. C.; De Oliveira, S.; Rivat, C.; Crooks, G. M.; Izotova, N.; Tse, J.; Adams, S.; Shupien, S.; Ricketts, H.; Davila, A.; Uzowuru, C.; Icreverzi, A.; Barman, P.; Fernandez, B. Campo; Hollis, R. P.; Coronel, M.; Yu, A.; Chun, K. M.; Casas, C. E.; Zhang, R.; Arduini, S.; Lynn, F.; Kudari, M.; Spezzi, A.; Zahn, M.; Heimke, R.; Labik, I.; Parrott, R.; Buckley, R. H.; Reeves, L.; Cornetta, K.; Sokolic, R.; Hershfield, M.; Schmidt, M.; Candotti, F.; Malech, H. L.; Thrasher, A. J.; Gaspar, H. B. 分享 收藏
The balance between the intronic miR-342 and its host gene Evl determines hematopoietic cell fate decision Herbst, Friederike; Lang, Tonio J. L.; Eckert, Elias S. P.; Wunsche, Peer; Wurm, Alexander A.; Kindinger, Tim; Laaber, Karin; Hemmati, Shayda; Hotz-Wagenblatt, Agnes; Zavidij, Oksana; Paruzynski, Anna; Lu, Junyan; von Kalle, Christof; Zenz, Thorsten; Klein, Christoph; Schmidt, Manfred; Ball, Claudia R.; Glimm, Hanno 分享 收藏
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Common clonal origin of conventional T cells and induced regulatory T cells in breast cancer patients Xydia, Maria; Rahbari, Raheleh; Ruggiero, Eliana; Macaulay, Iain; Tarabichi, Maxime; Lohmayer, Robert; Wilkening, Stefan; Michels, Tillmann; Brown, Daniel; Vanuytven, Sebastiaan; Mastitskaya, Svetlana; Laidlaw, Sean; Grabe, Niels; Pritsch, Maria; Fronza, Raffaele; Hexel, Klaus; Schmitt, Steffen; Mueller-Steinhardt, Michael; Halama, Niels; Domschke, Christoph; Schmidt, Manfred; von Kalle, Christof; Schuetz, Florian; Voet, Thierry; Beckhove, Philipp 分享 收藏
A multi-institution study: comparison of the heating patterns of five different MR-guided deep hyperthermia systems using an anthropomorphic phantom 一项多机构研究: 使用拟人化体模比较五种不同的MR引导的深部热疗系统的加热模式 Curto, Sergio; Mulder, Hendrik Thijmen; Aklan, Bassim; Mils, Oliver; Schmidt, Manfred; Lamprecht, Ulf; Peller, Michael; Wessalowski, Ruediger; Lindner, Lars H.; Fietkau, Rainer; Zips, Daniel; van Holthe, Netteke; Franckena, Martine; Paulides, Margarethus M.; van Rhoon, Gerard C. 分享 收藏
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Myelodysplastic syndrome unrelated to lentiviral vector in a patient treated with gene therapy for sickle cell disease Hsieh, Matthew M.; Bonner, Melissa; Pierciey, Francis John, Jr.; Uchida, Naoya; Rottman, James; Demopoulos, Laura; Schmidt, Manfred; Kanter, Julie; Walters, Mark C.; Thompson, Alexis A.; Asmal, Mohammed; Tisdale, John F. 分享 收藏
Comprehensive genomic characterization of gene therapy-induced T-cell acute lymphoblastic leukemia Horak, Peter; Uhrig, Sebastian; Witzel, Maximilian; Gil-Farina, Irene; Hutter, Barbara; Rath, Tim; Gieldon, Laura; Balasubramanian, Gnana Prakash; Pastor, Xavier; Heilig, Christoph E.; Richter, Daniela; Schroeck, Evelin; Ball, Claudia R.; Brors, Benedikt; Braun, Christian J.; Albert, Michael H.; Scholl, Claudia; von Kalle, Christof; Schmidt, Manfred; Froehling, Stefan; Klein, Christoph; Glimm, Hanno 分享 收藏