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Optimizing liver health before and after gene therapy for hemophilia A Ragni, Margaret V.; Mead, Henry; de Jong, Ype P.; Kaczmarek, Radoslaw; Leavitt, Andrew D.; Long, Brian; Nugent, Diane J.; Sabatino, Denise E.; Fong, Sylvia; von Drygalski, Annette; Walsh, Christopher E.; Luxon, Bruce A. 分享 收藏
Costs and impact of disease in adults with sickle cell disease: a pilot study Lanzkron, Sophie; Crook, Nicole; Wu, Joanne; Hussain, Sarah; Curtis, Randall G.; Robertson, Derek; Baker, Judith R.; Nugent, Diane; Soni, Amit; Roberts, Jonathan C.; Ullman, Megan M.; Kanter, Julie; Nichol, Michael B. 分享 收藏
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Understanding COVID-19-associated coagulopathy Conway, Edward M.; Mackman, Nigel; Warren, Ronald Q.; Wolberg, Alisa S.; Mosnier, Laurent O.; Campbell, Robert A.; Gralinski, Lisa E.; Rondina, Matthew T.; van de Veerdonk, Frank L.; Hoffmeister, Karin M.; Griffin, John H.; Nugent, Diane; Moon, Kyung; Morrissey, James H. 分享 收藏
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The Hemophilia Joint Health Score version 2.1 Validation in Adult Patients Study: A multicenter international study St-Louis, Jean; Abad, Audrey; Funk, Sharon; Tilak, Merlyn; Classey, Stephen; Zourikian, Nichan; McLaughlin, Paul; Lobet, Sebastien; Hernandez, Grace; Akins, Stacie; Wells, Anna J.; Manco-Johnson, Marilyn; John, Judy; Austin, Steve; Chowdhary, Pratima; Hermans, Cedric; Nugent, Diane; Bakeer, Nihal; Mangles, Sarah; Hilliard, Pamela; Blanchette, Victor S.; Feldman, Brian M. 分享 收藏
Patient preferences and priorities for haemophilia gene therapy in the US: A discrete choice experiment Witkop, Michelle; Morgan, George; O'Hara, Jamie; Recht, Michael; Buckner, Tyler W.; Nugent, Diane; Curtis, Randall; O'Mahony, Brian; Skinner, Mark W.; Mulhern, Brendan; Cawson, Matthew; Ali, Talaha M.; Sawyer, Eileen K.; Li, Nanxin 分享 收藏
Patient-relevant health outcomes for hemophilia care: Development of an international standard outcomes set 血友病护理的患者相关健康结果: 国际标准结果集的开发 van Balen, Erna C.; O'Mahony, Brian; Cnossen, Marjon H.; Dolan, Gerard; Blanchette, Victor S.; Fischer, Kathelijn; Gue, Deborah; O'Hara, Jamie; Iorio, Alfonso; Jackson, Shannon; Konkle, Barbara A.; Nugent, Diane J.; Coffin, Donna; Skinner, Mark W.; Smit, Cees; Srivastava, Alok; van Eenennaam, Fred; van der Bom, Johanna G.; Gouw, Samantha C. 分享 收藏
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Evidence of a disability paradox in patient-reported outcomes in haemophilia 血友病患者报告结局中残疾悖论的证据 O'Hara, Jamie; Martin, Antony P.; Nugent, Diane; Witkop, Michelle; Buckner, Tyler W.; Skinner, Mark W.; O'Mahony, Brian; Mulhern, Brendan; Morgan, George; Li, Nanxin; Sawyer, Eileen K. 分享 收藏
When Screening for Severe Combined Immunodeficiency (SCID) with T Cell Receptor Excision Circles Is Not SCID: a Case-Based Review 当筛查具有T细胞受体切除环的严重联合免疫缺陷 (SCID) 时不是SCID: 基于病例的综述 Buchbinder, David; Walter, Jolan E.; Butte, Manish J.; Chan, Wan-Yin; Chitty Lopez, Maria; Dimitriades, Victoria R.; Dorsey, Morna J.; Nugent, Diane J.; Puck, Jennifer M.; Singh, Jasjit; Collins, Cathleen A. 分享 收藏
Building access to care in adult sickle cell disease: defining models of care, essential components, and economic aspects Kanter, Julie; Smith, Wally R.; Desai, Payal C.; Treadwell, Marsha; Andemariam, Biree; Little, Jane; Nugent, Diane; Claster, Susan; Manwani, Deepa G.; Baker, Judith; Strouse, John J.; Osunkwo, Ifeyinwa; Stewart, Rosalyn W.; King, Allison; Shook, Lisa M.; Roberts, John D.; Lanzkron, Sophie 分享 收藏
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Parent proxy assessment of sibling quality of life following pediatric hematopoietic cell transplantation 儿童造血细胞移植后同胞生活质量的父母代理评估 Buchbinder, David; Patel, Sunita K.; Casillas, Jacqueline N.; Nugent, Diane J.; Neudorf, Steven; Sender, Leonard S.; Torno, Lilibeth; Huszti, Heather; Zeltzer, Lonnie K.; Parsons, Susan K. 分享 收藏
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Rubella Virus-Associated Cutaneous Granulomatous Disease: a Unique Complication in Immune-Deficient Patients, Not Limited to DNA Repair Disorders Buchbinder, David; Hauck, Fabian; Albert, Michael H.; Rack, Anita; Bakhtiar, Shahrzad; Shcherbina, Anna; Deripapa, Elena; Sullivan, Kathleen E.; Perelygina, Ludmila; Eloit, Marc; Neven, Benedicte; Perot, Philippe; Moshous, Despina; Suarez, Felipe; Bodemer, Christine; Bonilla, Francisco A.; Vaz, Louise E.; Krol, Alfons L.; Klein, Christoph; Seppanen, Mikko; Nugent, Diane J.; Singh, Jasjit; Ochs, Hans D. 分享 收藏
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