未登录 Prospective collection of bleeding rate and factor usage in participants with hemophilia A and B in a noninvestigational product study 在非研究性产品研究中对血友病A和B患者出血率和因子使用情况进行前瞻性收集 Kavakli, Kaan; Frenzel, Laurent; Antmen, Ali Bulent; Alzahrani, Hazzaa; Matino, Davide; Leavitt, Andrew D.; Ozelo, Margareth C.; Astermark, Jan; Park, Young-Shil; Klamroth, Robert; Cuker, Adam; Konkle, Barbara A.; McKay, John; Agathon, Delphine; Tseng, Li-Jung; Resa, Maria de los Angeles; Healy, Jasmine; Wilcox, Lisa J.; Plonski, Frank 分享 收藏
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Safety and Efficacy of Damoctocog Alfa Pegol in Previously Treated Children Aged 7 to < 12 Years With Severe Haemophilia A in the Phase 3, Open Label Alfa-PROTECT Main Study 达莫托考单抗alfa pegol在7至<12岁严重A型血友病既往治疗儿童中的安全性与有效性:III期、开放标签Alfa-PROTECT主要研究 Ozelo, Margareth C.; Luciani, Matteo; Glosli, Heidi; Kavakli, Kaan; Samji, Nasrin; Makris, Gregory C.; Tueckmantel, Claudia; Maas Enriquez, Monika; Oliveira, Luciana C.; Gupta, Shveta; Arbesu, Mario Guillermo; Davoli, Mauro; Chan, Anthony K. C.; Mancuso, Maria E. 分享 收藏
Plain Language Summary on Safety and Efficacy of Damoctocog Alfa Pegol in Previously Treated Children Aged 7 to < 12 Years With Severe Haemophilia A in the Phase 3, Open Label Alfa-PROTECT Main Study 关于在III期、开放标签的Alfa-PROTECT主要研究中,已接受治疗、年龄在7至<12岁、患有严重A型血友病儿童中使用达莫托斯酶α-聚乙二醇化衍生物的安全性和有效性的简明语言摘要 Ozelo, Margareth C.; Luciani, Matteo; Glosli, Heidi; Kavakli, Kaan; Samji, Nasrin; Makris, Gregory C.; Tueckmantel, Claudia; Enriquez, Monika Maas; Oliveira, Luciana C.; Gupta, Shveta; Arbesu, Mario Guillermo; Davoli, Mauro; Chan, Anthony K. C.; Mancuso, Maria Elisa 分享 收藏
Impact of Fidanacogene Elaparvovec Gene Therapy on Joint Health in Adults With Haemophilia B: Results From a Phase 3 Study Fidanacogene Elaparvovec基因疗法对血友病B成人患者关节健康的影响:一项3期研究的结果 Matino, Davide; Frenzel, Laurent; Antmen, Ali Bulent; Astermark, Jan; Cerqueira, Monica H.; Cuker, Adam; Katsarou-Fasouli, Olga; Kavakli, Kaan; Ozelo, Margareth C.; P'ng, Stephanie; Wang, Jiaan-der; Agathon, Delphine; Biondo, Francesca; Klaus, Pascal; McKay, John; Rupon, Jeremy; Sun, Pengling; Wilcox, Lisa J.; Plonski, Frank 分享 收藏
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Reduced Doses of Factor Concentrates and Bypassing Agents to Treat Breakthrough Bleeds in Patients with Hemophilia A and B on Fitusiran Antithrombin-Based Dosing Regimen: ATLAS-OLE 降低因子浓缩物和旁路剂的剂量以治疗接受Fitusiran抗凝血酶基础剂量方案的患者中血友病A和B的突破性出血:ATLAS-OLE Pipe, Steven W.; Kavakli, Kaan; Matsushita, Tadashi; Tran, Huyen; Zulfikar, Bulent; Menapace, Laurel; Puurunen, Marja; Hu, Wenruo; Shen, Yuqian; Kaddi, Chanchala; Salinas, Vanessa 分享 收藏
Inhibitor development upon switching from plasma-derived to recombinant factor VIII in previously untreated patients with severe hemophilia A: the PUP-SWITCH study 既往未接受治疗的重度A型血友病患者从血浆来源凝血因子VIII转换为重组凝血因子VIII时抑制物的产生:PUP-SWITCH研究 Miri, Syna; Rosendaal, Frits R.; Kavakli, Kaan; Eshghi, Peyman; Moghaddam, Soha Mohammadi; Scardo, Sara; Habibpanah, Behnaz; Elalfy, Mohsen; Halimeh, Susan; Nicolo, Gabriella; Gokcebay, Dilek; Ozbek, Namik; Celkan, Tiraje; Mohammadi, Ahmad; Karimi, Mehran; Shahsavani, Amin; Yilmaz, Baris; Albayrak, Canan; Gunes, Burcak; Kaya, Zuehre; Ay, Yilmaz; Akbayram, Sinan; Sarper, Nazan; Mannucci, Pier Mannuccio; Peyvandi, Flora 分享 收藏
Retrospective analysis of hemophilia B in Turkey: identifying main characteristics and treatment options Zulfikar, Bulent; Koc, Basak; Sahin, Fahri; Sasmaz, Hatice Ilgen; Kavakli, Kaan; Balkan, Can; Antmen, Ali Buelent; Akbayram, Sinan; Guvenc, Birol; Okan, Vahap; Turkkan, Emine; Albayrak, Canan; Albayrak, Davut; Sarper, Nazan; Celkan, Tuelin Tiraje; Ayyildiz, Orhan; Aksu, Salih; Patiroglu, Tuerkan; Salcioglu, Zafer; Gunes, Adalet Meral; Torun, Yasemin Altuner; Caliskan, Umran; Tokgoz, Huseyin; Ay, Yilmaz; Ozdemir, Gul Nihal; Sonmez, Mehmet; Unal, Ekrem; Oner, Ahmet Fayik; Guler, Nil; Kupesiz, Osman Alphan; Oren, Hale; Karaman, Serap; Unuvar, Ayegul; Dagli, Mehmet; Demir, Ahmet Muzaffer; Soker, Murat; Alioglu, Buelent; Kaya, Zuehre; Ayhan, Aylin Canbolat; Bicakci, Zafer; Aral, Yusuf Ziya; Ar, Muhlis Cem 分享 收藏
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Recombinant porcine factor VIII in patients with congenital haemophilia A with inhibitors undergoing surgery: Phase 3, single-arm, open-label study Pfrepper, Christian; Radossi, Paolo; Windyga, Jerzy; Kavakli, Kaan; Schutgens, Roger; Sarper, Nazan; Gu, Joan; Badejo, Kayode; Jain, Nisha 分享 收藏
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