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收藏Aberrant lysosomal dynamics disrupt myogenesis via mTORC1 signalling in X-linked myotubular myopathyX连锁肌管型肌营养不良中,异常的溶酶体动力学通过mTORC1信号通路破坏肌生成。
Kora, Kengo; Yoshida, Takeshi; Yokoyama, Atsushi; Fujiwara, Kei; Yano, Naoko; Kayaki, Taisei; Kajimoto, Satoshi; Nishikawa, Kinuko; Sakurai, Hidetoshi; Takita, Junko
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收藏Distinct muscle regenerative capacity of human induced pluripotent stem cell-derived mesenchymal stromal cells in Ullrich congenital muscular dystrophy model mice
Yokomizo-Goto, Megumi; Takenaka-Ninagawa, Nana; Zhao, Chengzhu; Yoshioka, Clemence Kiho Bourgeois; Miki, Mayuho; Motoike, Souta; Inada, Yoshiko; Zujur, Denise; Theoputra, William; Jin, Yonghui; Toguchida, Junya; Ikeya, Makoto; Sakurai, Hidetoshi
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收藏Heparan Sulfate Chain-Conjugated Laminin-E8 Fragments Advance Paraxial Mesodermal Differentiation Followed by High Myogenic Induction from hiPSCs
Zhao, Mingming; Taniguchi, Yukimasa; Shimono, Chisei; Jonouchi, Tatsuya; Cheng, Yushen; Shimizu, Yasuhiro; Nalbandian, Minas; Yamamoto, Takuya; Nakagawa, Masato; Sekiguchi, Kiyotoshi; Sakurai, Hidetoshi
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收藏Possible involvement of zinc transporter ZIP13 in myogenic differentiation锌转运蛋白ZIP13可能参与肌源性分化
Shoji, Masaki; Ohashi, Takuto; Nagase, Saki; Yuri, Haato; Ichihashi, Kenta; Takagishi, Teruhisa; Nagata, Yuji; Nomura, Yuki; Fukunaka, Ayako; Kenjou, Sae; Miyake, Hatsuna; Hara, Takafumi; Yoshigai, Emi; Fujitani, Yoshio; Sakurai, Hidetoshi; dos Santos, Heloisa G.; Fukada, Toshiyuki; Kuzuhara, Takashi
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收藏Dual CRISPR-Cas3 system for inducing multi-exon skipping in DMD patient-derived iPSCs
Kita, Yuto; Okuzaki, Yuya; Naoe, Youichi; Lee, Joseph; Bang, Uikyu; Okawa, Natsumi; Ichiki, Akane; Jonouchi, Tatsuya; Sakurai, Hidetoshi; Kojima, Yusuke; Hotta, Akitsu
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收藏Simple and efficient differentiation of human iPSCs into contractible skeletal muscles for muscular disease modeling
Rashid, Muhammad Irfanur; Ito, Takuji; Miya, Fuyuki; Shimojo, Daisuke; Arimoto, Kanae; Onodera, Kazunari; Okada, Rina; Nagashima, Takunori; Yamamoto, Kazuki; Khatun, Zohora; Shimul, Rayhanul Islam; Niwa, Jun-ichi; Katsuno, Masahisa; Sobue, Gen; Okano, Hideyuki; Sakurai, Hidetoshi; Shimizu, Kazunori; Doyu, Manabu; Okada, Yohei
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收藏Evaluation of Human-Induced Pluripotent Stem Cells Derived from a Patient with Schwartz-Jampel Syndrome Revealed Distinct Hyperexcitability in the Skeletal Muscles来自schwartz-jampel综合征患者的人类诱导多能干细胞的评估显示骨骼肌明显的过度兴奋
Yamashita, Yuri; Nakada, Satoshi; Nakamura, Kyoko; Sakurai, Hidetoshi; Ohno, Kinji; Goto, Tomohide; Mabuchi, Yo; Akazawa, Chihiro; Hattori, Nobutaka; Arikawa-Hirasawa, Eri
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收藏A mutation in DOK7 in congenital myasthenic syndrome forms aggresome in cultured cells, and reduces DOK7 expression and MuSK phosphorylation in patient-derived iPS cells
Zhang, Shaochuan; Ohkawara, Bisei; Ito, Mikako; Huang, Zhizhou; Zhao, Fei; Nakata, Tomohiko; Takeuchi, Tomoya; Sakurai, Hidetoshi; Komaki, Hirofumi; Kamon, Masayoshi; Araki, Toshiyuki; Ohno, Kinji
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