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United Global Advocacy Drives Updates to World Health Organization Essential Medicines List 联合国全球倡导推动世界卫生组织基本药物目录更新 Pierce, Glenn F.; Kaczmarek, Radek; Page, David; Baumann, Alain; Farrugia, Albert; Garrido, Cesar; Mancuso, Maria Elisa; O'Mahony, Brian; Skinner, Mark W.; Mekhuzla, Salome 分享 收藏
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Development of a novel gene editing lexicon for hemophilia: methodology and results 开发用于血友病的新型基因编辑词典: 方法和结果 Kessler, Craig M.; Valentino, Leonard A.; Thornburg, Courtney D.; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Mckeown, William; Pierce, Glenn F.; Khair, Kate; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Sindhurakar, Anil; Whyte, Lauren; Delwart, Virginie; Chiao, Megan; Gutstein, David E.; Antonino, Ilia; Hermans, Cedric; Pipe, Steven W. 分享 收藏
Operationalising a Haemophilia Gene Editing Lexicon for Practical Use 操作血友病基因编辑词典以供实际使用 Mckeown, William; Hermans, Cedric; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Pierce, Glenn F.; Khair, Kate; Valentino, Leonard A.; Pipe, Steven W.; Pillai, Monisha; Jones, Micheala; Delwart, Virginie; Sindhurakar, Anil; Gutstein, David E.; Kessler, Craig M. 分享 收藏
Adeno-associated virus-based gene therapy for hemophilia- addressing the gaps 基于腺相关病毒的血友病基因治疗-解决差距 Miesbach, Wolfgang; Batty, Paul; Chowdary, Pratima; Fong, Sylvia; Kaczmarek, Radoslaw; Leebeek, Frank W. G.; Long, Brian; Mahlangu, Johnny; Makris, Mike; Pierce, Glenn F.; Pipe, Steven W.; Srivastava, Alok; Voorberg, Jan; Peyvandi, Flora 分享 收藏
Contrasting Approaches in the Implementation of GRADE Methodology in Guidelines for Haemophilia and Von Willebrand Disease Skinner, Mark W.; Albisetti, Manuela; Ardila, Jesus; Astermark, Jan; Blatny, Jan; Carcao, Manuel; Chowdary, Pratima; Connell, Nathan T.; Crato, Miguel; Dargaud, Yesim; d'Oiron, Roseline; Dunn, Amy L.; Escobar, Miguel A.; Escuriola-Ettingshausen, Carmen; Gouider, Emna; Harroche, Annie; Hermans, Cedric; Jimenez-Yuste, Victor; Kaczmarek, Radoslaw; Kenet, Gili; Khoo, Liane; Klamroth, Robert; Langer, Florian; Lillicrap, David; Mahlangu, Johnny; Male, Christoph; Matsushita, Tadashi; Meunier, Sandrine; Miesbach, Wolfgang; Nolan, Beatrice; Oldenburg, Johannes; O'Mahony, Brian; Ozelo, Margareth; Pierce, Glenn F.; Ramos, Gloria; Recht, Michael; Romero-Lux, Olivia; Rotellini, Dawn; Santoro, Rita C.; Singleton, Tammuella C.; Srivastava, Alok; Susen, Sophie; Talks, Kate; Tran, Huyen; Valentino, Leonard A.; Windyga, Jerzy; Yang, Renchi; Mancuso, Maria Elisa 分享 收藏
International Society on Thrombosis and Haemostasis Clinical Practice Guideline for Treatment of Congenital Haemophilia-A Critical Appraisal Albisetti, Manuela; Ardila, Jesus; Astermark, Jan; Blatny, Jan; Carcao, Manuel; Chowdary, Pratima; Connell, Nathan T.; Crato, Miguel; Dargaud, Yesim; d'Oiron, Roseline; Dunn, Amy L.; Escobar, Miguel A.; Ettingshausen, Carmen Escuriola; Fischer, Kathelijn; Gouider, Emna; Harroche, Annie; Hermans, Cedric; Jimenez-Yuste, Victor; Kaczmarek, Radoslaw; Kenet, Gili; Khoo, Liane; Klamroth, Robert; Langer, Florian; Lillicrap, David; Mahlangu, Johnny; Male, Christoph; Mancuso, Maria Elisa; Matsushita, Tadashi; Meunier, Sandrine; Miesbach, Wolfgang; Nolan, Beatrice; Oldenburg, Johannes; O'Mahony, Brian; Ozelo, Margareth; Pierce, Glenn F.; Ramos, Gloria; Recht, Michael; Romero-Lux, Olivia; Rotellini, Dawn; Santoro, Rita C.; Singleton, Tammuella C.; Skinner, Mark W.; Srivastava, Alok; Susen, Sophie; Talks, Kate; Tran, Huyen; Valentino, Leonard A.; Windyga, Jerzy; Yang, Renchi 分享 收藏
The management of liver disease in people with congenital bleeding disorders: guidance from European Association for Haemophilia and Allied Disorders, European Haemophilia Consortium, ISTH, and World Federation of Hemophilia La Mura, Vincenzo; Colombo, Massimo; Foster, Graham R.; Angeli, Paolo; Miesbach, Wolfgang; Klamroth, Robert; Pierce, Glenn F.; O'Mahony, Brian; Lim, Ming Y.; Hernandez-Gea, Virginia; Makris, Michael; Peyvandi, Flora 分享 收藏
A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results 血友病社区的新型基因编辑词典策略: 开发和初步结果的研究计划 Hermans, Cedric; Valentino, Leonard A.; Thornburg, Courtney D.; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Mckeown, William; Pierce, Glenn F.; Khair, Kate; Pipe, Steven W.; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Chiao, Megan; Antonino, Ilia; Kessler, Craig 分享 收藏
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