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收藏BMN 349, a small molecule inhibitor of Z alpha-1 antitrypsin polymerization, increases secretion and reduces intrahepatic inclusions in a mouse model of diseaseBMN 349,一种Z α-1抗胰蛋白酶聚合的小分子抑制剂,可增加分泌并减少疾病小鼠模型中的肝内包涵体
Handyside, Britta; Wenzel, Heather; Mackenzie, Donald; Chang, Catherine; Greenslade, Annie; Van Vleet, Jeremy; Heglar, Brian; Chen, Joseph C.; Zhang, Lening; Larimore, Kevin; Zhou, Huiyu; Trantcheva, Iva; Sims, Lawrence; Evans, Kristin; Fong, Sylvia; Kumar, Gyanendra; Annu, Kavya; Ronzoni, Riccardo; Irving, James A.; Wang, Bing; Bunting, Stuart; Lomas, David A.
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收藏Wearable monitoring for rehabilitation: Deep learning-driven vertical ground reaction force estimation for anterior cruciate ligament reconstruction康复中的可穿戴监测:基于深度学习的垂直地面反作用力估计用于前交叉韧带重建
Chen, Tianxiao; Xu, Datao; Wang, Meizi; Zhou, Zhifeng; Jie, Tianle; Zhou, Huiyu; Yuan, Yi; Baker, Julien S.; Gao, Zixiang; Gu, Yaodong
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收藏Impact of AAVMYBPC3 Gene Transfer on Heart Structure and Function in Human and Mouse Models of Hypertrophic Cardiomyopathy
Vitelli, Catherine; Zhang, Lening; Murphy, Ryan; Blus, Bartlomiej; Christianson, Terri; Giaramita, Alexander; Holtzinger, John; Handyside, Britta; May, Hannah; Ann Pham; Tu Nguyen; Zhou, Huiyu; Ntai, Ioanna; Mearini, Giulia; Ricotti, Valeria; Voit, Thomas; Eschenhagen, Thomas; Carrier, Lucie; Agarwal, Pooja; Bunting, Stuart; Sumandea, Marius
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收藏Achieving efficacy in subjects with sustained pegvaliase-neutralizing antibody responses
Aryal, Madhukar; Lau, Kelly; Boyer, Ryan; Zhou, Huiyu; Abend, Johanna; Gu, Karen; Olbertz, Joy; Gupta, Soumi; Zoog, Stephen; Larimore, Kevin
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收藏Pu-erh tea ameliorates obesity and modulates gut microbiota in high fat diet fed mice
Ye, Jing; Zhao, Yan; Chen, Xiangming; Zhou, Huiyu; Yang, Yucheng; Zhang, Xueqin; Huang, Yayan; Zhang, Na; Lui, Edmund M. K.; Xiao, Meitian
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收藏Pharmacology of BMN 250 administered via intracerebroventricular infusion once every 2 weeks for twenty-six weeks or longer in a canine model of mucopolysaccharidosis type IIIB
Ellinwood, N. Matthew; Valentine, Bethann; Hess, Andrew S.; Jens, Jackie K.; Snella, Elizabeth M.; Ware, Wendy A.; Hostetter, Shannon J.; Ben-Shlomo, Gil; Jeffery, Nicholas; Safayi, Sina; Smith, Jodi D.; Millman, Suzanne T.; Parsons, Rebecca L.; Butt, Mark T.; Cooper, Jonathan D.; Nestrasil, Igor; Prill, Heather; Liu, Xiao; Zhou, Huiyu; Lawrence, Roger; Crawford, Brett; Grover, Anita; Melton, Andrew; Cherukuri, Anu; Wait, Jill C. M.; Pinkstaff, Jason; McCullagh, Emma
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