未登录 Safety, immunogenicity and efficacy of the self-amplifying mRNA ARCT-154 COVID-19 vaccine: pooled phase 1, 2, 3a and 3b randomized, controlled trials Ho, Nhan Thi; Hughes, Steven G.; Ta, Van Thanh; Phan, Lan Trong; Do, Quyet; Nguyen, Thuong Vu; Pham, Anh Thi Van; Dang, Mai Thi Ngoc; Nguyen, Luong Viet; Trinh, Quang Vinh; Pham, Hung Ngoc; Chu, Men Van; Nguyen, Toan Trong; Luong, Quang Chan; Le, Vy Thi Tuong; Nguyen, Thang Van; Tran, Ly-Thi-Le; Luu, Anh Thi Van; Nguyen, Anh Ngoc; Nguyen, Nhung-Thi-Hong; Vu, Hai-Son; Edelman, Jonathan M.; Parker, Suezanne; Sullivan, Brian; Sullivan, Sean; Ruan, Qian; Clemente, Brenda; Luk, Brian; Lindert, Kelly; Berdieva, Dina; Murphy, Kat; Sekulovich, Rose; Greener, Benjamin; Smolenov, Igor; Chivukula, Pad; Nguyen, Van Thu; Nguyen, Xuan-Hung 分享 收藏
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Outcomes in Pregnant Persons Immunized with a Cell-Based Quadrivalent Inactivated Influenza Vaccine: A Prospective Observational Cohort Study Robinson, Christopher; Van Boxmeer, Josephine; Tilson, Hugh; Scialli, Anthony; Vanchiere, John A.; Ides, Ellis; Sawlwin, Daphne; Molrine, Deborah; Hohenboken, Matthew; Edelman, Jonathan; Albano, Jessica D. 分享 收藏
A Prospective Cohort Study on Pregnancy Outcomes of Persons Immunized with a Seasonal Quadrivalent Inactivated Influenza Vaccine during Pregnancy Robinson, Christopher; Oberye, Janine; van Boxmeer, Josephine; Albano, Jessica D.; Tilson, Hugh; Scialli, Anthony; Vanchiere, John A.; Ides, Ellis; Sawlwin, Daphne; Hohenboken, Matthew; Edelman, Jonathan 分享 收藏
Efficacy of a Cell-Culture-Derived Quadrivalent Influenza Vaccine in Children Nolan, Terence; Fortanier, Alexandre C.; Leav, Brett; Poder, Airi; Bravo, Lulu C.; Szymanski, Henryk T.; Heeringa, Marten; Vermeulen, Wim; Matassa, Vince; Smolenov, Igor; Edelman, Jonathan M. 分享 收藏
Prevention of influenza during mismatched seasons in older adults with an MF59-adjuvanted quadrivalent influenza vaccine: a randomised, controlled, multicentre, phase 3 efficacy study Beran, Jiri; Reynales, Humberto; Poder, Airi; Yu, Charles Y.; Pitisuttithum, Punnee; Yuan, Lee Li; Vermeulen, Wim; Verhoeven, Carole; Leav, Brett; Zhang, Bin; Sawlwin, Daphne; Hamers-Heijnen, Esther; Edelman, Jonathan; Smolenov, Igor 分享 收藏
Quantitative disease progression model of α-1 proteinase inhibitor therapy on computed tomography lung density in patients with α-1 antitrypsin deficiency Tortorici, Michael A.; Rogers, James A.; Vit, Oliver; Bexon, Martin; Sandhaus, Robert A.; Burdon, Jonathan; Chorostowska-Wynimko, Joanna; Thompson, Philip; Stocks, James; McElvaney, Noel G.; Chapman, Kenneth R.; Edelman, Jonathan M. 分享 收藏
Safety of C1-inhibitor concentrate use for hereditary angioedema in pediatric patients Busse, Paula; Baker, James; Martinez-Saguer, Inmaculada; Bernstein, Jonathan A.; Craig, Timothy; Magerl, Markus; Riedl, Marc; Shapiro, Ralph; Frank, Michael; Lumry, William; Rosch, Jeffrey; Edelman, Jonathan; Williams-Herman, Debora; Feuersenger, Henrike; Rojavin, Mikhail 分享 收藏
Minimum clinically important difference analysis confirms the efficacy of IgPro10 in CIDP: the PRIMA trial Merkies, Ingemar S. J.; Lawo, John-Philip; Edelman, Jonathan M.; De Bleecker, Jan L.; Sommer, Claudia; Robberecht, Wim; Saarela, Mika; Kamienowski, Jerzy; Stelmasiak, Zbigniew; Mielke, Orell; Tackenberg, Bjoern; Leger, Jean-Marc 分享 收藏
Prevention of Hereditary Angioedema Attacks with a Subcutaneous C1 Inhibitor Longhurst, H.; Cicardi, M.; Craig, T.; Bork, K.; Grattan, C.; Baker, J.; Li, H. H.; Reshef, A.; Bonner, J.; Bernstein, J. A.; Anderson, J.; Lumry, W. R.; Farkas, H.; Katelaris, C. H.; Sussman, G. L.; Jacobs, J.; Riedl, M.; Manning, M. E.; Hebert, J.; Keith, P. K.; Kivity, S.; Neri, S.; Levy, D. S.; Baeza, M. L.; Nathan, R.; Schwartz, L. B.; Caballero, T.; Yang, W.; Crisan, I.; Hernandez, M. D.; Hussain, I.; Tarzi, M.; Ritchie, B.; Kralickova, P.; Guilarte, M.; Rehman, S. M.; Banerji, A.; Gower, R. G.; Bensen-Kennedy, D.; Edelman, J.; Feuersenger, H.; Lawo, J. -P.; Machnig, T.; Pawaskar, D.; Pragst, I.; Zuraw, B. L. 分享 收藏
Long-term efficacy and safety of α1 proteinase inhibitor treatment for emphysema caused by severe α1 antitrypsin deficiency: an open-label extension trial (RAPID-OLE) McElvaney, Noel G.; Burdon, Jonathan; Holmes, Mark; Glanville, Allan; Wark, Peter A. B.; Thompson, Philip J.; Hernandez, Paul; Chlumsky, Jan; Teschler, Helmut; Ficker, Joachim H.; Seersholm, Niels; Altraja, Alan; Makitaro, Riitta; Chorostowska-Wynimko, Joanna; Sanak, Marek; Stoicescu, Paul I.; Piitulainen, Eeva; Vit, Oliver; Wencker, Marion; Tortorici, Michael A.; Fries, Michael; Edelman, Jonathan M.; Chapman, Kenneth R. 分享 收藏
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Safety and Usage of C1-Inhibitor in Hereditary Angioedema: Berinert Registry Data Riedl, Marc A.; Bygum, Anette; Lumry, William; Magerl, Markus; Bernstein, Jonathan A.; Busse, Paula; Craig, Timothy; Frank, Michael M.; Edelman, Jonathan; Williams-Herman, Debora; Feuersenger, Henrike; Rojavin, Mikhail 分享 收藏
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LATE-BREAKING ABSTRACT: Long-term efficacy of A1-PI therapy in RAPID and RAPID extension trials McElvaney, N. Gerard; Chapman, Kenneth R.; Burdon, Jonathan; Piitulainen, Eeva; Seersholm, Niels; Stocks, James; Sandhaus, Robert; Vit, Oliver; Fries, Michael; Edelman, Jonathan M. 分享 收藏
Assessment of A1-PI dose-exposure and exposure-response relationships in patients with Alpha-1 antitrypsin inhibitor deficiency Tortorici, Michael A.; Yao, Zhenling; Rogers, James A.; Vit, Oliver; Bexon, Martin; Sandhaus, Robert; Burdon, Jonathan; Piitulainen, Eeva; Seersholm, Niels; Stocks, James; McElvaney, N. Gerard; Chapman, Kenneth R.; Edelman, Jonathan 分享 收藏
Safety of bi-weekly infusion of A1-PI augmentation therapy in RAPID Seersholm, Niels; Sandhaus, Robert; Chapman, Kenneth R.; Burdon, Jonathan; Piitulainen, Eeva; Stocks, James; Tortorici, Michael; Rosenberg, Tanja; Vit, Oliver; Bexon, Martin; Edelman, Jonathan; McElvaney, N. Gerard 分享 收藏
Population pharmacokinetics of A1-PI in patients with Alpha-1 antitrypsin deficiency Tortorici, Michael A.; Vit, Oliver; Bexon, Martin; Sandhaus, Robert; Burdon, Jonathan; Piitulainen, Eeva; Seersholm, Niels; Stocks, James; McElvaney, N. Gerard; Chapman, Kenneth R.; Edelman, Jonathan 分享 收藏