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Luspatercept for myelodysplastic syndromes/myeloproliferative neoplasm with ring sideroblasts and thrombocytosis Komrokji, Rami S.; Platzbecker, Uwe; Fenaux, Pierre; Zeidan, Amer M.; Garcia-Manero, Guillermo; Mufti, Ghulam J.; Santini, Valeria; Diez-Campelo, Maria; Finelli, Carlo; Jurcic, Joseph G.; Greenberg, Peter L.; Sekeres, Mikkael A.; DeZern, Amy E.; Savona, Michael R.; Shetty, Jeevan K.; Ito, Rodrigo; Zhang, George; Ha, Xianwei; Backstrom, Jay T.; Verma, Amit 分享 收藏
Eltrombopag Added to Immunosuppression in Severe Aplastic Anemia de Latour, R. Peffault; Kulasekararaj, A.; Iacobelli, S.; Terwel, S. R.; Cook, R.; Griffin, M.; Halkes, C. J. M.; Recher, C.; Barraco, F.; Forcade, E.; Vallejo, J-C; Drexler, B.; Mear, J-B; Smith, A. E.; Angelucci, E.; Raymakers, R. A. P.; de Groot, M. R.; Daguindau, E.; Nur, E.; Barcellini, W.; Russell, N. H.; Terriou, L.; Iori, A-P; La Rocca, U.; Sureda, A.; Sanchez-Ortega, I; Xicoy, B.; Jarque, I; Cavenagh, J.; de Fontbrune, F. Sicre; Marotta, S.; Munir, T.; Tjon, J. M. L.; Tavitian, S.; Praire, A.; Clement, L.; Rabian, F.; Marano, L.; Hill, A.; Palmisani, E.; Muus, P.; Cacace, F.; Frieri, C.; Van Lint, M-T; Passweg, J. R.; Marsh, J. C. W.; Socie, G.; Mufti, G. J.; Dufour, C.; Risitano, A. M. 分享 收藏
Health-Related Quality of Life Outcomes in Patients with Myelodysplastic Syndromes with Ring Sideroblasts Treated with Luspatercept in the MEDALIST Phase 3 Trial 在MEDALIST 3期试验中,用Luspatercept治疗的环状成纤维细胞的骨髓增生异常综合征患者的健康相关生活质量 Oliva, Esther Natalie; Platzbecker, Uwe; Garcia-Manero, Guillermo; Mufti, Ghulam J.; Santini, Valeria; Sekeres, Mikkael A.; Komrokji, Rami S.; Shetty, Jeevan K.; Tang, Derek; Guo, Shien; Liao, Weiqin; Zhang, George; Ha, Xianwei; Ito, Rodrigo; Lord-Bessen, Jennifer; Backstrom, Jay T.; Fenaux, Pierre 分享 收藏
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Clinical and prognostic significance of small paroxysmal nocturnal hemoglobinuria clones in myelodysplastic syndrome and aplastic anemia Fattizzo, Bruno; Ireland, Robin; Dunlop, Alan; Yallop, Deborah; Kassam, Shireen; Large, Joanna; Gandhi, Shreyans; Muus, Petra; Manogaran, Charles; Sanchez, Katy; Consonni, Dario; Barcellini, Wilma; Mufti, Ghulam J.; Marsh, Judith C. W.; Kulasekararaj, Austin G. 分享 收藏
Functional reconstruction of human AML reveals stem cell origin and vulnerability of treatment-resistant MLL-rearranged leukemia Zeisig, Bernd B.; Fung, Tsz Kan; Zarowiecki, Magdalena; Tsai, Chiou Tsun; Luo, Huacheng; Stanojevic, Boban; Lynn, Claire; Leung, Anskar Y. H.; Zuna, Jan; Zaliova, Marketa; Bornhauser, Martin; von Bonin, Malte; Lenhard, Boris; Huang, Suming; Mufti, Ghulam J.; So, Chi Wai Eric 分享 收藏
Ectopic Humanized Mesenchymal Niche in Mice Enables Robust Engraftment of Myelodysplastic Stem Cells Mian, Syed A.; Abarrategi, Ander; Kong, Kar Lok; Rouault-Pierre, Kevin; Wood, Henry; Oedekoven, Caroline A.; Smith, Alexander E.; Batsivari, Antoniana; Ariza-McNaughton, Linda; Johnson, Peter; Snoeks, Thomas; Mufti, Ghulam J.; Bonnet, Dominique 分享 收藏
Impact of somatic mutations in myelodysplastic patients with isolated partial or total loss of chromosome 7 体细胞突变对7号染色体部分或全部缺失的骨髓增生异常综合征患者的影响 Crisa, Elena; Kulasekararaj, Austin G.; Adema, Vera; Such, Esperanza; Schanz, Julie; Haase, Detlef; Shirneshan, Katayoon; Best, Steven; Mian, Syed A.; Kizilors, Aytug; Cervera, Jose; Lea, Nicholas; Ferrero, Dario; Germing, Ulrich; Hildebrandt, Barbara; Martinez, Ana Belen Valencia; Santini, Valeria; Sanz, Guillermo F.; Sole, Francesc; Mufti, Ghulam J. 分享 收藏
Luspatercept in Patients with Lower-Risk Myelodysplastic Syndromes Fenaux, Pierre; Platzbecker, Uwe; Mufti, Ghulam J.; Garcia-Manero, Guillermo; Buckstein, Rena; Santini, Valeria; Diez-Campelo, Maria; Finelli, Carlo; Cazzola, Mario; Ilhan, Osman; Sekeres, Mikkael A.; Falantes, Jose F.; Arrizabalaga, Beatriz; Salvi, Flavia; Giai, Valentina; Vyas, Paresh; Bowen, David; Selleslag, Dominik; DeZern, Amy E.; Jurcic, Joseph G.; Germing, Ulrich; Goetze, Katharina S.; Quesnel, Bruno; Beyne-Rauzy, Odile; Cluzeau, Thomas; Voso, Maria-Teresa; Mazure, Dominiek; Vellenga, Edo; Greenberg, Peter L.; Hellstrom-Lindberg, Eva; Zeidan, Amer M.; Ades, Lionel; Verma, Amit; Savona, Michael R.; Laadem, Abderrahmane; Benzohra, Aziz; Zhang, Jennie; Rampersad, Anita; Dunshee, Diana R.; Linde, Peter G.; Sherman, Matthew L.; Komrokji, Rami S.; List, Alan F. 分享 收藏
Non-del(5q) myelodysplastic syndromes-associated loci detected by SNP-array genome-wide association meta-analysis Snp-array全基因组关联meta分析检测非del(5q) 骨髓增生异常综合征相关位点 McGraw, Kathy L.; Cheng, Chia-Ho; Chen, Y. Ann; Hou, Hsin-An; Nilsson, Bjorn; Genovese, Giulio; Cluzeau, Thomas; Pellagatti, Andrea; Przychodzen, Bartlomiej P.; Mallo, Mar; Arenillas, Leonor; Mohamedali, Azim; Ades, Lionel; Sallman, David A.; Padron, Eric; Sokol, Lubomir; Moreilhon, Chimene; Raynaud, Sophie; Tien, Hwei-Fang; Boultwood, Jacqueline; Ebert, Benjamin L.; Sole, Francesc; Fenaux, Pierre; Mufti, Ghulam J.; Maciejewski, Jaroslaw P.; Kanetsky, Peter A.; List, Alan F. 分享 收藏
Similar outcomes of alemtuzumab-based hematopoietic cell transplantation for SAA patients older or younger than 50 years Sheth, Vipul Sharad; Potter, Victoria; Gandhi, Shreyans A.; Kulasekararaj, Austin Gladston; de Lavallade, Hugues; Muus, Petra; Pagliuca, Antonio; Rice, Carmel F. M.; Mehra, Varun; Grimaldi, Francesco; Inam, Shafqat; Barber, Linda D.; Mufti, Ghulam J.; Marsh, Judith C. 分享 收藏
Effect of low-level BCR-ABL1 kinase domain mutations identified by next-generation sequencing in patients with chronic myeloid leukaemia: a population-based study Kizilors, Aytug; Crisa, Elena; Lea, Nicholas; Passera, Roberto; Mian, Syed; Anwar, Jamal; Best, Steve; Nicolini, Franck E.; Ireland, Robin; Aldouri, Maadh; Pocock, Christopher; Corbett, Tim; Gale, Richard; Bart-Smith, Emily; Weston-Smith, Simon; Wykes, Clare; Kulasekararaj, Austin; Jackson, Sophie; Harrington, Patrick; McLornan, Donal; Raj, Kavita; Pagliuca, Antonio; Mufti, Ghulam J.; de Lavallade, Hugues 分享 收藏
Clinical, histopathological and molecular characterization of hypoplastic myelodysplastic syndrome Bono, Elisa; McLornan, Donal; Travaglino, Erica; Gandhi, Shreyans; Galli, Anna; Khan, Alesia Abigael; Kulasekararaj, Austin G.; Boveri, Emanuela; Raj, Kavita; Elena, Chiara; Ireland, Robin M.; Bianchessi, Antonio; Jiang, Jie; Todisco, Gabriele; Ferretti, Virginia Valeria; Cazzola, Mario; Marsh, Judith C. W.; Malcovati, Luca; Mufti, Ghulam J. 分享 收藏
Clinical and morphological predictors of outcome in older aplastic anemia patients treated with eltrombopag Fattizzo, Bruno; Kulasekararaj, Austin G.; Hill, Anita; Benson-Quarm, Nana; Griffin, Morag; Munir, Talha; Arnold, Louise; Riley, Kathryn; Ireland, Robin; De Lavallade, Hugues; Potter, Victoria; Consonni, Dario; Hillmen, Peter; Mufti, Ghulam J.; Barcellini, Wilma; Marsh, Judith C. W. 分享 收藏
Epstein-Barr Virus and Monoclonal Gammopathy of Clinical Significance in Autologous Stem Cell Transplantation for Multiple Sclerosis Epstein-barr病毒和单克隆丙球蛋白病在自体干细胞移植治疗多发性硬化中的临床意义 Mehra, Varun; Rhone, Elijah; Widya, Stefani; Zuckerman, Mark; Potter, Victoria; Raj, Kavita; Kulasekararaj, Austin; McLornan, Donal; de Lavallade, Hugues; Benson-Quarm, Nana; Lim, Christina; Ware, Sarah; Sudhanva, Malur; Malik, Omar; Nicholas, Richard; Muraro, Paolo A.; Marsh, Judith; Mufti, Ghulam J.; Silber, Eli; Pagliuca, Antonio; Kazmi, Majid A. 分享 收藏
Impact of T-cell depletion strategies on outcomes following hematopoietic stem cell transplantation for idiopathic aplastic anemia: A study on behalf of the European blood and marrow transplant severe aplastic anemia working party Samarasinghe, Sujith; Clesham, Katherine; Iacobelli, Simona; Sbianchi, Giulia; Knol, Cora; Hamladji, Rose-Marie; Socie, Gerard; Aljurf, Mahmoud; Koh, Mickey; Sengeloev, Henrik; Dalle, Jean-Hugues; Robinson, Stephen; Van Lint, Maria Teresa; Halkes, Constantijn J. M.; Beelen, Dietrich; Mufti, Ghulam J.; Snowden, John; Blaise, Didier; de Latour, Regis Peffault; Marsh, Judith; Dufour, Carlo; Risitano, Antonio M. 分享 收藏
Clonal hematopoiesis in patients with multiple myeloma undergoing autologous stem cell transplantation Chitre, Sneha; Stoelzel, Friedrich; Cuthill, Kirsty; Streetly, Mathew; Graham, Charlotte; Dill, Claudia; Mohamedali, Azim; Smith, Alexander; Schetelig, Johannes; Altmann, Heidi; Bornhaeuser, Martin; Mufti, Ghulam J. 分享 收藏