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Early Access to Tafamidis for Patients With Transthyretin Amyloid Cardiomyopathy 特发性转甲状腺素蛋白淀粉样变性心肌病患者早期使用塔拉姆尼德的途径 Crespo-Leiro, Maria G.; Hanna, Mazen; Damy, Thibaud; Delgado, Diego; Ebede, Ben; Marino, Valentina; Wang, Ronnie; Maurer, Mathew S.; Garcia-Pavia, Pablo; Drachman, Brian M. 分享 收藏
Vutrisiran in Patients with Transthyretin Amyloidosis with Cardiomyopathy Fontana, Marianna; Berk, John L.; Gillmore, Julian D.; Witteles, Ronald M.; Grogan, Martha; Drachman, Brian; Damy, Thibaud; Garcia-Pavia, Pablo; Taubel, Jorg; Solomon, Scott D.; Sheikh, Farooq H.; Tahara, Nobuhiro; Gonzalez-Costello, Jose; Tsujita, Kenichi; Morbach, Caroline; Pozsonyi, Zoltan; Petrie, Mark C.; Delgado, Diego; van der Meer, Peter; Jabbour, Andrew; Bondue, Antoine; Kim, Darae; Azevedo, Olga; Hvitfeldt Poulsen, Steen; Yilmaz, Ali; Jankowska, Ewa A.; Algalarrondo, Vincent; Slugg, Andrew; Garg, Pushkal P.; Boyle, Katherine L.; Yureneva, Elena; Silliman, Nancy; Yang, Lilli; Chen, Jihong; Eraly, Satish A.; Vest, John; Maurer, Mathew S. 分享 收藏
AmyNet: a Novel Deep Learning Imaging Approach to Identify Incidental Myocardial Uptake Indicative of Cardiac Amyloidosis on Whole Body 99Tc-Bone Scintigraphy Imaging AmyNet:一种新型深度学习影像方法,用于识别全身99Tc-骨闪烁成像中提示心脏淀粉样变的偶发心肌摄取 Bhattaru, Abhijit; Rojulpote, Chaitanya; Vidula, Mahesh; Duda, Jeffrey; Thompson, Elizabeth; Swago, Sophia; Gee, James; Pieretti, Janice; Drachman, Brian; Dorbala, Sharmila; Witschey, Walter; Bravo, Paco 分享 收藏
Tafamidis treatment for transthyretin amyloid cardiomyopathy: results from an open-label, early-access, long-term study extension in an all-comers population Crespo-Leiro, M. G.; Hanna, M.; Damy, T.; Delgado, D.; Ebede, B.; Angeli, F. S.; Maurer, M. S.; Garcia-Pavia, P.; Drachman, B. M. 分享 收藏
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The Cardiac Amyloidosis Registry Study (CARS): Rationale, Design and Methodology Stern, Lily K.; Grodin, Justin L.; Maurer, Mathew S.; Ruberg, Frederick L.; Patel, Ayan R.; Khouri, Michel G.; Roth, Lori R.; Aras, Mandar A.; Bhardwaj, Anju; Bhattacharya, Priyanka; Brailovsky, Yevgeniy; Drachman, Brian M.; Ebong, Imo A.; Fine, Nowell M.; Gaggin, Hanna; Gopal, Deepa; Griffin, Jan; Judge, Daniel; Kim, Paul; Mitchell, Joshua; Mitter, Sumeet S.; Mohan, Rajeev C.; Ramos, Hannia; Reyentovich, Alex; Sheikh, Farooq H.; Sperry, Brett; Carter, Spencer; Urey, Marcus; Vaishnav, Joban; Vest, Amanda R.; Kittleson, Michelle M.; Patel, Jignesh K. 分享 收藏
Deep learning approach for automated segmentation of myocardium using bone scintigraphy single-photon emission computed tomography/computed tomography in patients with suspected cardiac amyloidosis Bhattaru, Abhijit; Rojulpote, Chaitanya; Vidula, Mahesh; Duda, Jeffrey; Maclean, Matthew T.; Swago, Sophia; Thompson, Elizabeth; Gee, James; Pieretti, Janice; Drachman, Brian; Cohen, Adam; Dorbala, Sharmila; Bravo, Paco E.; Witschey, Walter R. 分享 收藏
APOLLO-B, a Study of Patisiran in Patients With Transthyretin Cardiac Amyloidosis: Primary LongTerm Results From the Open-Label Extension Period Hung, Rebecca R.; Correia, Edileide D.; Berk, John L.; Drachman, Brian; Fontana, Marianna; Gillmore, Julian D.; Mesquita, Claudio T.; Simoes, Marcus V.; Yureneva, Elena; White, Matthew T.; Sweetser, Marianne T.; Jay, Patrick Y.; Vest, John; Maurer, Mathew S. 分享 收藏
Sex Differences in Wild-Type Transthyretin Amyloidosis: An Analysis from the Transthyretin Amyloidosis Outcomes Survey (THAOS) 野生型转甲状腺素蛋白淀粉样变性的性别差异: 来自转甲状腺素蛋白淀粉样变性结果调查 (THAOS) 的分析 Campbell, Courtney M.; LoRusso, Samantha; Dispenzieri, Angela; Kristen, Arnt V.; Maurer, Mathew S.; Rapezzi, Claudio; Lairez, Olivier; Drachman, Brian; Garcia-Pavia, Pablo; Grogan, Martha; Chapman, Doug; Amass, Leslie 分享 收藏
Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy Elliott, Perry; Drachman, Brian M.; Gottlieb, Stephen S.; Hoffman, James E.; Hummel, Scott L.; Lenihan, Daniel J.; Ebede, Ben; Gundapaneni, Balarama; Li, Benjamin; Sultan, Marla B.; Shah, Sanjiv J. 分享 收藏
Efficacy and safety with >3 years of inotersen treatment for the polyneuropathy of hereditary transthyretin amyloidosis Coelho, Teresa; Whelan, Carol; Conceicao, Isabel; Brannagan, Thomas; Wang, Annabel; Polydefkis, Michael; Dyck, Peter; Plante-Bordeneuve, Violaine; Berk, John; Merlini, Giampaolo; Obici, Laura; Drachman, Brian; Gorevic, Peter; Schmidt, Hartmut; Plana, Josep Maria Campistol; Gamez, Josep; Kristen, Arnt; Mazzeo, Anna; Narayana, Arvind; Olugemo, Kemi; Aquino, Peter; Benson, Merrill; Gertz, Morie 分享 收藏
ATTR amyloidosis during the COVID-19 pandemic: insights from a global medical roundtable Brannagan, Thomas H., III; Auer-Grumbach, Michaela; Berk, John L.; Briani, Chiara; Bril, Vera; Coelho, Teresa; Damy, Thibaud; Dispenzieri, Angela; Drachman, Brian M.; Fine, Nowell; Gaggin, Hanna K.; Gertz, Morie; Gillmore, Julian D.; Gonzalez, Esther; Hanna, Mazen; Hurwitz, David R.; Khella, Sami L.; Maurer, Mathew S.; Nativi-Nicolau, Jose; Olugemo, Kemi; Quintana, Luis F.; Rosen, Andrew M.; Schmidt, Hartmut H.; Shehata, Jacqueline; Waddington-Cruz, Marcia; Whelan, Carol; Ruberg, Frederick L. 分享 收藏
Avoiding misdiagnosis: expert consensus recommendations for the suspicion and diagnosis of transthyretin amyloidosis for the general practitioner Gertz, Morie; Adams, David; Ando, Yukio; Beirao, Joao Melo; Bokhari, Sabahat; Coelho, Teresa; Comenzo, Raymond L.; Damy, Thibaud; Dorbala, Sharmila; Drachman, Brian M.; Fontana, Marianna; Gillmore, Julian D.; Grogan, Martha; Hawkins, Philip N.; Lousada, Isabelle; Kristen, Arnt V.; Ruberg, Frederick L.; Suhr, Ole B.; Maurer, Mathew S.; Nativi-Nicolau, Jose; Quarta, Candida Cristina; Rapezzi, Claudio; Witteles, Ronald; Merlini, Giampaolo 分享 收藏
Expert Consensus Recommendations for the Suspicion and Diagnosis of Transthyretin Cardiac Amyloidosis Maurer, Mathew S.; Bokhari, Sabahat; Damy, Thibaud; Dorbala, Sharmila; Drachman, Brian M.; Fontana, Marianna; Grogan, Martha; Kristen, Arnt V.; Lousada, Isabelle; Nativi-Nicolau, Jose; Cristina Quarta, Candida; Rapezzi, Claudio; Ruberg, Frederick L.; Witteles, Ronald; Merlini, Giampaolo 分享 收藏
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Efficacy of Tafamidis in Transthyretin Amyloid Cardiomyopathy in the ATTR-ACT Trial: Sensitivity Analyses Further Support the Primary Results Maurer, Mathew S.; Schwartz, Jeffrey H.; Gundapaneni, Balarama; Elliott, Perry; Merlini, Giampaolo; Cruz, Marcia Waddington; Kristen, Arnt V.; Grogan, Martha; Witteles, Ronald; Damy, Thibaud; Drachman, Brian M.; Shah, Sanjiv J.; Hanna, Mazen; Judge, Daniel P.; Gottlieb, Stephen S.; Berk, John L.; Lenihan, Daniel J.; Hoffman, James E.; Hummel, Scott L.; Velazquez, Eric J.; Patterson, Terrell A.; Sultan, Marla B.; Rapezzi, Claudio 分享 收藏
Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy 转甲状腺素蛋白淀粉样心肌病患者的Tafamidis治疗 Maurer, Mathew S.; Schwartz, Jeffrey H.; Gundapaneni, Balarama; Elliott, Perry M.; Merlini, Giampaolo; Waddington-Cruz, Marcia; Kristen, Arnt V.; Grogan, Martha; Witteles, Ronald; Damy, Thibaud; Drachman, Brian M.; Shah, Sanjiv J.; Hanna, Mazen; Judge, Daniel P.; Barsdorf, Alexandra I.; Huber, Peter; Patterson, Terrell A.; Riley, Steven; Schumacher, Jennifer; Stewart, Michelle; Sultan, Marla B.; Rapezzi, Claudio 分享 收藏
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Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis Benson, M. D.; Waddington-Cruz, M.; Berk, J. L.; Polydefkis, M.; Dyck, P. J.; Wang, A. K.; Plante-Bordeneuve, V.; Barroso, F. A.; Merlini, G.; Obici, L.; Scheinberg, M.; Brannagan, T. H., III; Litchy, W. J.; Whelan, C.; Drachman, B. M.; Adams, D.; Heitner, S. B.; Conceicao, I.; Schmidt, H. H.; Vita, G.; Campistol, J. M.; Gamez, J.; Gorevic, P. D.; Gane, E.; Shah, A. M.; Solomon, S. D.; Monia, B. P.; Hughes, S. G.; Kwoh, T. J.; McEvoy, B. W.; Jung, S. W.; Baker, B. F.; Ackermann, E. J.; Gertz, M. A.; Coelho, T. 分享 收藏