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Type 2N VWD: Conclusions from the Spanish PCM-EVW-ES project Perez-Rodriguez, Almudena; Batlle, Javier; Costa Pinto, Joana; Corrales, Irene; Borras, Nina; Garcia-Martinez, Iris; Rosa Cid, Ana; Bonanad, Santiago; Parra, Rafael; Mingot-Castellano, Maria Eva; Navarro, Nira; Altisent, Carmen; Perez-Montes, Rocio; Moreto, Ana; Herrero, Sonia; Soto, Inmaculada; Fernandez Mosteirin, Nuria; Jimenez-Yuste, Victor; de Andres Jacob, Aurora; Fontanes, Emilia; Mateo, Jose; Castro Quismondo, Nerea; Batlle, Fernando; Vidal, Francisco; Lopez-Fernandez, Maria Fernanda 分享 收藏
Simoctocog Alfa (Nuwiq) in Previously Untreated Patients with Severe Haemophilia A: Final Results of the NuProtect Study Simococog Alfa (Nuwiq) 在先前未经治疗的严重血友病A患者中: NuProtect研究的最终结果 Liesner, Ri J.; Abraham, Aby; Altisent, Carmen; Belletrutti, Mark J.; Carcao, Manuel; Carvalho, Manuela; Chambost, Herve; Chan, Anthony K. C.; Dubey, Leonid; Ducore, Jonathan; Gattens, Michael; Gresele, Paolo; Gruel, Yves; Guillet, Benoit; Jimenez-Yuste, Victor; Kitanovski, Lidija; Klukowska, Anna; Lohade, Sunil; Mancuso, Maria Elisa; Oldenburg, Johannes; Pavlova, Anna; Pollio, Berardino; Sigaud, Marianne; Vdovin, Vladimir; Vilchevska, Kateryna; Wu, John K. M.; Jansen, Martina; Belyanskaya, Larisa; Walter, Olaf; Knaub, Sigurd; Neufeld, Ellis J. 分享 收藏
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Impact of prophylaxis on health-related quality of life of boys with hemophilia: An analysis of pooled data from 9 countries 预防对血友病男孩健康相关生活质量的影响: 来自9个国家的汇总数据分析 Usuba, Koyo; Price, Victoria E.; Blanchette, Victor; Abad, Audrey; Altisent, Carmen; Buchner-Daley, Loretta; Carneiro, Jorge D. A.; Feldman, Brian M.; Fischer, Kathelijn; Grainger, John; Holzhauer, Susanne; Luke, Koon-Hung; Meunier, Sandrine; Ozelo, Margareth; Tang, Ling; Antunes, Sandra V.; Villaca, Paula; Wakefield, Cindy; Wharfe, Gilian; Wu, Runhui; Young, Nancy L. 分享 收藏
Joint status in Spanish haemophilia B patients assessed using the Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US) score Jimenez-Yuste, Victor; Teresa Alvarez-Roman, Maria; Martin-Salces, Monica; De la Corte-Rodriguez, Hortensia; Altisent, Carmen; Parra, Rafael; Nunez, Ramiro; Perez, Rosario; Garcia-Candel, Faustino; Bonanad, Santiago; Querol, Felipe; Alonso, Nieves; Fernandez-Mosteirin, Nuria; Lopez-Ansoar, Elsa; Javier Garcia-Frade, Luis; Bermejo, Nuria; Perez-Gonzalez, Noelia; Jose Gutierrez-Pimentel, Maria; Martinoli, Carlo; Fernandez-Arias, Isabel; Kyung Kim, Hae 分享 收藏
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Recombinant FXIII (rFXIII-A2) Prophylaxis Prevents Bleeding and Allows for Surgery in Patients with Congenital FXIII A-Subunit Deficiency Carcao, Manuel; Altisent, Carmen; Castaman, Giancarlo; Fukutake, Katsuyuki; Kerlin, Bryce A.; Kessler, Craig; Lassila, Riitta; Nugent, Diane; Oldenburg, Johannes; Garly, May-Lill; Rosholm, Anders; Inbal, Aida 分享 收藏
Risk Factors for the Progression from Low to High Titres in 260 Children with Severe Haemophilia A and Newly Developed Inhibitors Mancuso, Maria Elisa; Fischer, Kathelijn; Santagostino, Elena; Oldenburg, Johannes; Platokouki, Helen; Koenigs, Cristoph; Escuriola-Ettingshausen, Carmen; Rivard, George E.; Rosa Cid, Ana; Carcao, Manuel; Ljung, Rolf; Petrini, Pia; Altisent, Carmen; Kenet, Gili; Liesner, Raina; Kurnik, Karin; Auerswald, Guenther; Chambost, Herve; Makipernaa, Anne; ClaudioMolinari, Angelo; Williams, Mike; van den Berg, H. Marijke 分享 收藏
Molecular and clinical profile of von Willebrand disease in Spain (PCM-EVW-ES): Proposal for a new diagnostic paradigm Batlle, Javier; Perez-Rodriguez, Almudena; Corrales, Irene; Fernanda Lopez-Fernandez, Maria; Rodriguez-Trillo, Angela; Loures, Esther; Rosa Cid, Ana; Bonanad, Santiago; Cabrera, Noelia; Moret, Andres; Parra, Rafael; Eva Mingot-Castellano, Maria; Balda, Ignacia; Altisent, Carmen; Perez-Montes, Rocio; Maria Fisac, Rosa; Iruin, Gemma; Herrero, Sonia; Soto, Inmaculada; de Rueda, Beatriz; Jimenez-Yuste, Victor; Alonso, Nieves; Vilarino, Dolores; Arija, Olga; Campos, Rosa; Jose Paloma, Maria; Bermejo, Nuria; Toll, Teresa; Mateo, Jose; Arribalzaga, Karmele; Marco, Pascual; Palomo, Angeles; Sarmiento, Lizheidy; Inigo, Belen; del Mar Nieto, Maria; Vidal, Rosa; Paz Martinez, Maria; Aguinaco, Reyes; Maria Cesar, Jesus; Ferreiro, Maria; Garcia-Frade, Javier; Maria Rodriguez-Huerta, Ana; Cuesta, Jorge; Rodriguez-Gonzalez, Ramon; Garcia-Candel, Faustino; Cornudella, Rosa; Aguilar, Carlos; Borras, Nina; Vidal, Francisco 分享 收藏
Advanced cell-based modeling of the royal disease: characterization of the mutated F9 mRNA Martorell, L.; Luce, E.; Vazquez, J. L.; Richaud-Patin, Y.; Jimenez-Delgado, S.; Corrales, I.; Borras, N.; Casacuberta-Serra, S.; Weber, A.; Parra, R.; Altisent, C.; Follenzi, A.; Dubart-Kupperschmitt, A.; Raya, A.; Vidal, F.; Barquinero, J. 分享 收藏
Immunogenicity, efficacy and safety of Nuwiq® (human-cl rhFVIII) in previously untreated patients with severe haemophilia A-Interim results from the NuProtect Study Liesner, R. J.; Abashidze, M.; Aleinikova, O.; Altisent, C.; Belletrutti, M. J.; Borel-Derlon, A.; Carcao, M.; Chambost, H.; Chan, A. K. C.; Dubey, L.; Ducore, J.; Fouzia, N. A.; Gattens, M.; Gruel, Y.; Guillet, B.; Kavardakova, N.; El Khorassani, M.; Klukowska, A.; Lambert, T.; Lohade, S.; Sigaud, M.; Turea, V.; Wu, J. K. M.; Vdovin, V.; Pavlova, A.; Jansen, M.; Belyanskaya, L.; Walter, O.; Knaub, S.; Neufeld, E. J. 分享 收藏
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Adherence to prophylaxis and quality of life in children and adolescents with severe haemophilia A 严重血友病A的儿童和青少年坚持预防和生活质量 Garcia-Dasi, M.; Aznar, J. A.; Jimenez-Yuste, V.; Altisent, C.; Bonanad, S.; Mingot, E.; Lucia, F.; Gimenez, F.; Fernanda Lopez, M.; Marco, P.; Perez, R.; Fernandez, M. A.; Paloma, M. J.; Galmes, B.; Herrero, S.; Garcia-Talavera, J. A. 分享 收藏
Bleeding before prophylaxis in severe hemophilia: paradigm shift over two decades Nijdam, Annelies; Altisent, Carmen; Carcao, Manuel D.; Cid, Ana R.; Claeyssens-Donadel, Segolene; Kurnik, Karin; Ljung, Rolf; Nolan, Beatrice; Petrini, Pia; Platokouki, Helen; Rafowicz, Anne; Thomas, Angela E.; Fischer, Kathelijn 分享 收藏
International cross-cultural validation study of the Canadian Haemophilia Outcomes: Kids' Life Assessment Tool McCusker, P. J.; Fischer, K.; Holzhauer, S.; Meunier, S.; Altisent, C.; Grainger, J. D.; Blanchette, V. S.; Burke, T. A.; Wakefield, C.; Young, N. L. 分享 收藏
Proteomic analysis of platelet N-glycoproteins in PMM2-CDG patients de la Morena-Barrio, M. E.; Di Michele, M.; Lozano, M. L.; Rivera, J.; Perez-Duenas, B.; Altisent, C.; Sevivas, T.; Vicente, V.; Jaeken, J.; Freson, K.; Corral, J. 分享 收藏