未登录 Machine learning suggests polygenic risk for cognitive dysfunction in amyotrophic lateral sclerosis 机器学习提示肌萎缩性侧索硬化症认知功能障碍的多基因风险 Placek, Katerina; Benatar, Michael; Wuu, Joanne; Rampersaud, Evadnie; Hennessy, Laura; Van Deerlin, Vivianna M.; Grossman, Murray; Irwin, David J.; Elman, Lauren; McCluskey, Leo; Quinn, Colin; Granit, Volkan; Statland, Jeffrey M.; Burns, Ted M.; Ravits, John; Swenson, Andrea; Katz, Jon; Pioro, Erik P.; Jackson, Carlayne; Caress, James; So, Yuen; Maiser, Samuel; Walk, David; Lee, Edward B.; Trojanowski, John Q.; Cook, Philip; Gee, James; Sha, Jin; Naj, Adam C.; Rademakers, Rosa; Chen, Wenan; Wu, Gang; Paul Taylor, J.; McMillan, Corey T. 分享 收藏
Validation of serum neurofilaments as prognostic and potential pharmacodynamic biomarkers for ALS Benatar, Michael; Zhang, Lanyu; Wang, Lily; Granit, Volkan; Statland, Jeffrey; Barohn, Richard; Swenson, Andrea; Ravits, John; Jackson, Carlayne; Burns, Ted M.; Trivedi, Jaya; Pioro, Erik P.; Caress, James; Katz, Jonathan; McCauley, Jacob L.; Rademakers, Rosa; Malaspina, Andrea; Ostrow, Lyle W.; Wuu, Joanne 分享 收藏
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Randomized phase 2 study of FcRn antagonist efgartigimod in generalized myasthenia gravis FcRn拮抗剂efgartigimod在全身性重症肌无力中的随机2期研究 Howard, James F., Jr.; Bril, Vera; Burns, Ted M.; Mantegazza, Renato; Bilinska, Malgorzata; Szczudlik, Andrzej; Beydoun, Said; De Rivera Garrido, Francisco Javier Rodriguez; Piehl, Fredrik; Rottoli, Mariarosa; Van Damme, Philip; Tuan Vu; Evoli, Amelia; Freimer, Miriam; Mozaffar, Tahseen; Ward, E. Sally; Dreier, Torsten; Ulrichts, Peter; Verschueren, Katrien; Guglietta, Antonio; de Haard, Hans; Leupin, Nicolas; Verschuuren, Jan J. G. M.; Claeys, Kristl; Diez-Tejedor, Exuperio; Mathew, Veena; Sgarzi, Manlio; Harvey, Brittany Leigh; Farias, Jerrica; Frangiomore, Rita; Heintzman, Sarah; de Meel, Robert; Chopra, Manisha; Alboini, Paolo Emilio; Hietala, Albert; Genge, Angela 分享 收藏
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Validation of a simple disease-specific, quality-of-life measure for diabetic polyneuropathy CAPPRI Gwathmey, Kelly G.; Sadjadi, Reza; Horton, William B.; Conaway, Mark R.; Barnett-Tapia, Carolina; Bril, Vera; Russell, James W.; Shaibani, Aziz; Mauermann, Michelle L.; Hehir, Michael K.; Kolb, Noah; Guptill, Jeffrey; Hobson-Webb, Lisa; Gable, Karissa; Raja, Shruti; Silvestri, Nicholas; Wolfe, Gil I.; Smith, A. Gordon; Malik, Rabia; Traub, Rebecca; Joshi, Amruta; Elliott, Matthew P.; Jones, Sarah; Burns, Ted M. 分享 收藏
Rituximab as treatment for anti-MuSK myasthenia gravis Multicenter blinded prospective review Hehir, Michael K.; Hobson-Webb, Lisa D.; Benatar, Michael; Barnett, Carolina; Silvestri, Nicholas J.; Howard, James F., Jr.; Howard, Diantha; Visser, Amy; Crum, Brian A.; Nowak, Richard; Beekman, Rachel; Kumar, Aditya; Ruzhansky, Katherine; Chen, I-Hweii Amy; Pulley, Michael T.; LaBoy, Shannon M.; Fellman, Melissa A.; Greene, Shane M.; Pasnoor, Mamatha; Burns, Ted M. 分享 收藏
Construction and validation of a novel disease-specific quality-of-life instrument for patients with primary antibody deficiency disease (PADQOL-16) Ballow, Mark; Conaway, Mark R.; Sriaroon, Panida; Rachid, Rima A.; Seeborg, Filiz O.; Duff, Carla M.; Bonilla, Francisco A.; Younger, M. Elizabeth M.; Shapiro, Ralph; Burns, Ted M. 分享 收藏
A randomized controlled trial of methotrexate for patients with generalized myasthenia gravis Pasnoor, Mamatha; He, Jianghua; Herbelin, Laura; Burns, Ted M.; Nations, Sharon; Bril, Vera; Wang, Annabel K.; Elsheikh, Bakri H.; Kissel, John T.; Saperstein, David; Shaibani, J. Aziz; Jackson, Carlayne; Swenson, Andrea; Howard, James F., Jr.; Goyal, Namita; David, William; Wicklund, Matthew; Pulley, Michael; Becker, Mara; Mozaffar, Tahseen; Benatar, Michael; Pazcuzzi, Robert; Simpson, Ericka; Rosenfeld, Jeffrey; Dimachkie, Mazen M.; Statland, Jeffrey M.; Barohn, Richard J. 分享 收藏
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Psychometrics evaluation of Charcot-Marie-Tooth Neuropathy Score (CMTNSv2) second version, using Rasch analysis Sadjadi, Reza; Reilly, Mary M.; Shy, Michael E.; Pareyson, Davide; Laura, Matilde; Murphy, Sinead; Feely, Shawna M. E.; Grider, Tiffany; Bacon, Chelsea; Piscosquito, Giuseppe; Calabrese, Daniela; Burns, Ted M. 分享 收藏
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Multipoint incremental motor unit number estimation as an outcome measure in ALS Shefner, J. M.; Watson, M. L.; Simionescu, L.; Caress, J. B.; Burns, T. M.; Maragakis, N. J.; Benatar, M.; David, W. S.; Sharma, K. R.; Rutkove, S. B. 分享 收藏
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