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Perspectives on the current diagnostic and treatment paradigms in secondary hemophagocytic lymphohistiocytosis (HLH) Naymagon, Leonard; Roehrs, Philip; Hermiston, Michelle; Connelly, James; Bednarski, Jeffrey; Boelens, Jaap-Jan; Chandrakasan, Shanmuganathan; Saldana, Blachy Davila; Henry, Michael M.; Satwani, Prakash; Ray, Anish; Walkovich, Kelly; Teachey, David; Behrens, Edward M.; Canna, Scott W.; Kumar, Ashish 分享 收藏
Multidisciplinary approach to treating complex immune dysregulation disorders: an adaptive model for institutional implementation 多学科方法治疗复杂免疫失调障碍:一种适用于机构实施的适应性模型 Henderson, Lauren A.; Abraham, Roshini S.; Ahmed, Aisha; Blount, Lindsey; Canna, Scott W.; Chaimowitz, Natalia S.; Chandrakasan, Shanmuganathan; Coates, Bria; Connelly, James A.; Cooper, Megan A.; Duncan, Christine N.; French, Anthony; Hazen, Melissa; Hermiston, Michelle L.; Nolan, Brian; Ray, Anish; Rose, Melissa J.; Satter, Lisa Forbes; Schulert, Grant; Tejtel, Sara Kristen Sexson; Vogel, Tiphanie; Walkovich, Kelly; Zinter, Matt S. 分享 收藏
Outcomes of Immunosuppressive Therapy in Children Less Than Three Years of Age with Idiopathic Severe Aplastic Anemia: A North American Collaboration 小于3岁特发性严重再生障碍性贫血患儿免疫抑制治疗的结局:一项北美合作研究 Dayagi, Talya Wittmann; Willis, Laura; Corriveau-Bourque, Catherine; Cada, Michaela; Rogers, Zora R.; Nakano, Taizo A.; Olson, Timothy S.; Wang, Winfred C.; Gillio, Alfred; Coates, Thomas D.; Chawla, Anjulika; Castillo, Paul; Kurre, Peter; Gamper, Christopher; Arnold, Staci D.; Joshi, Sarita; Geddis, Amy E.; Boklan, Jessica; Rothman, Jennifer A.; Huang, James N.; Kupfer, Gary M.; Glader, Bertil; Walkovich, Kelly J.; Thompson, Alexis; Hanna, Rabi; Williams, David A.; Shimamura, Akiko; Dror, Yigal 分享 收藏
Real-world treatment patterns and outcomes in patients with primary hemophagocytic lymphohistiocytosis treated with emapalumab Chandrakasan, Shanmuganathan; Jordan, Michael B.; Baker, Ashley; Behrens, Edward M.; Bhatla, Deepika; Chien, May; Eckstein, Olive S.; Henry, Michael M.; Hermiston, Michelle L.; Hinson, Ashley P.; Leiding, Jennifer W.; Oladapo, Abiola; Patel, Sachit A.; Pednekar, Priti; Ray, Anish K.; Saldana, Blachy Davila; Sarangi, Susmita N.; Walkovich, Kelly J.; Yee, John D.; Zoref-Lorenz, Adi; Allen, Carl E. 分享 收藏
Clinical and Treatment History of Patients with Partial DiGeorge Syndrome and Autoimmune Cytopenia at Multiple Centers(vol 44, 72, 2024) Patel, Priya K.; Chinga, Michell Lozano; Yilmaz, Melis; Joychan, Sonia; Ujhazi, Boglarka; Ellison, Maryssa; Gordon, Sumai; Nieves, Daime; Csomos, Krisztian; Eslin, Don; Afify, Zeinab A.; Meznarich, Jessica; Bohnsack, John; Walkovich, Kelly; Seidel, Markus G.; Sharapova, Svetlana; Boyarchuk, Oksana; Latysheva, Elena; Tuzankina, Irina; Shaker, Ahmad B.; Ayala, Irmel; Sriaroon, Panida; Westermann-Clark, Emma; Walter, Jolan E. 分享 收藏
Clinical and Treatment History of Patients with Partial DiGeorge Syndrome and Autoimmune Cytopenia at Multiple Centers Patel, Priya K.; Chinga, Michell Lozano; Yilmaz, Melis; Joychan, Sonia; Ujhazi, Boglarka; Ellison, Maryssa; Gordon, Sumai; Nieves, Daime; Csomos, Krisztian; Eslin, Don; Afify, Zeinab A.; Meznarich, Jessica; Bohnsack, John; Walkovich, Kelly; Seidel, Markus G.; Sharapova, Svetlana; Boyarchyk, Oksana; Latysheva, Elena; Tuzankina, Irina; Shaker, Ahmad B.; Ayala, Irmel; Sriaroon, Panida; Westermann-Clark, Emma; Walter, Jolan E. 分享 收藏
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Monogenic early-onset lymphoproliferation and autoimmunity: Natural history of STAT3 gain-of-function syndrome 单基因早发性淋巴细胞增殖和自身免疫: STAT3功能获得综合征的自然史 Leiding, Jennifer W.; Vogel, Tiphanie P.; Santarlas, Valentine G. J.; Mhaskar, Rahul; Smith, Madison R.; Carisey, Alexandre; Vargas-Hernandez, Alexander; Silva-Carmona, Manuel; Heeg, Maximilian; Rensing-Ehl, Anne; Neven, Benedicte; Hadjadj, Jerome; Hambleton, Sophie; Leahy, Timothy Ronan; Meesilpavikai, Kornvalee; Cunningham-Rundles, Charlotte; Dutmer, Cullen M.; Sharapova, Svetlana O.; Taskinen, Mervi; Chua, Ignatius; Hague, Rosie; Klemann, Christian; Kostyuchenko, Larysa; Morio, Tomohiro; Thatayatikom, Akaluck; Ozen, Ahmet; Scherbina, Anna; Bauer, Cindy S.; Flanagan, Sarah E.; Gambineri, Eleonora; Giovannini-Chami, Lisa; Heimall, Jennifer; Sullivan, Kathleen E.; Allenspach, Eric; Romberg, Nei; Deane, Sean G.; Prince, Benjamin T.; Rose, Melissa J.; Bohnsack, John; Mousallem, Talal; Jesudas, Rohith; Vilela, Maria Marluce Dos Santos; O'Sullivan, Michael; Schmid, Jana Pachlopnik; Pruhova, Stepanka; Klocperk, Adam; Rees, Matthew; Su, Helen; Bahna, Sami; Baris, Saf; Bartnikas, Lisa M.; Berger, Amy Chang; Briggs, Tracy A.; Brothers, Shannon; Bundy, Vanessa; Chan, Alice Y.; Chandrakasan, Shanmuganathan; Christiansen, Mette; Cole, Theresa; Cook, Matthew C.; Desai, Mukesh M.; Fischer, Ute; Fulcher, David A.; Gallo, Silvanna; Gauthier, Amelie; Gennery, Andrew R.; Marques, Jose Goncalo; Gottrand, Frederic; Grimbacher, Bodo; Grunebaum, Eyal; Haapaniemi, Emma; Hamalainen, Sari; Heiskanen, Kaarina; Heiskanen-Kosma, Tarja; Hoffman, Hal M.; Gonzalez-Granado, Luis Ignacio; Guerrerio, Anthony L.; Kainulainen, Leena; Kumar, Ashish; Lawrence, Monica G.; Levin, Carina; Martelius, Timi; Neth, Olaf; Olbrich, Peter; Palma, Alejandro; Patel, Niraj C.; Pozos, Tamara; Preece, Kahn; Lugo Reyes, Saul Oswaldo; Russell, Mark A.; Schejter, Yael; Seroogy, Christine; Sinclair, Jan; Skevofilax, Effie; Suan, Daniel; Suez, Daniel; Szabolcs, Paul; Velasco, Helena; Warnatz, Klaus; Walkovich, Kelly; Worth, Austen; Seppanen, Mikko R. J.; Torgerson, Troy R.; Sogkas, Georgios; Ehl, Stephan; Tangye, Stuart G.; Cooper, Megan A.; Milner, Joshua D.; Satter, Lisa R. Forbes 分享 收藏
SOCS1 Haploinsufficiency Presenting as Severe Enthesitis, Bone Marrow Hypocellularity, and Refractory Thrombocytopenia in a Pediatric Patient with Subsequent Response to JAK Inhibition Michniacki, Thomas F.; Walkovich, Kelly; DeMeyer, Lauren; Saad, Nadine; Hannibal, Mark; Basiaga, Matthew L.; Horst, Kelly K.; Mohan, Smriti; Chen, Liang; Brodeur, Kailey; Du, Yan; Frame, David; Ngo, Sandra; Simoneau, Jillian; Brown, Noah; Lee, Pui Y. 分享 收藏
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Histiocytic Neoplasms, Version 2.2021 Go, Ronald S.; Jacobsen, Eric; Baiocchi, Robert; Buhtoiarov, Ilia; Butler, Erin B.; Campbell, Patrick K.; Coulter, Don W.; Diamond, Eli; Flagg, Aron; Goodman, Aaron M.; Goyal, Gaurav; Gratzinger, Dita; Hendrie, Paul C.; Higman, Meghan; Hogarty, Michael D.; Janku, Filip; Karmali, Reem; Morgan, David; Raldow, Anne C.; Stefanovic, Alexandra; Tantravahi, Srinivas K.; Walkovich, Kelly; Zhang, Ling; Bergman, Mary Anne; Darlow, Susan D. 分享 收藏
Distinct genetic pathways define pre-malignant versus compensatory clonal hematopoiesis in Shwachman-Diamond syndrome 不同的遗传途径定义了shwachman-diamond综合征的恶性前造血与代偿性克隆造血 Kennedy, Alyssa L.; Myers, Kasiani C.; Bowman, James; Gibson, Christopher J.; Camarda, Nicholas D.; Furutani, Elissa; Muscato, Gwen M.; Klein, Robert H.; Ballotti, Kaitlyn; Liu, Shanshan; Harris, Chad E.; Galvin, Ashley; Malsch, Maggie; Dale, David; Gansner, John M.; Nakano, Taizo A.; Bertuch, Alison; Vlachos, Adrianna; Lipton, Jeffrey M.; Castillo, Paul; Connelly, James; Churpek, Jane; Edwards, John R.; Hijiya, Nobuko; Ho, Richard H.; Hofmann, Inga; Huang, James N.; Keel, Sioban; Lamble, Adam; Lau, Bonnie W.; Norkin, Maxim; Stieglitz, Elliot; Stock, Wendy; Walkovich, Kelly; Boettcher, Steffen; Brendel, Christian; Fleming, Mark D.; Davies, Stella M.; Weller, Edie A.; Bahl, Christopher; Carter, Scott L.; Shimamura, Akiko; Lindsley, R. Coleman 分享 收藏
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Clinical features and outcomes of patients with Shwachman-Diamond syndrome and myelodysplastic syndrome or acute myeloid leukaemia: a multicentre, retrospective, cohort study Myers, Kasiani C.; Furutani, Elissa; Weller, Edie; Siegele, Bradford; Galvin, Ashley; Arsenault, Valerie; Alter, Blanche P.; Boulad, Farid; Bueso-Ramos, Carlos; Burroughs, Lauri; Castillo, Paul; Connelly, James; Davies, Stella M.; DiNardo, Courtney D.; Hanif, Iftikhar; Ho, Richard H.; Karras, Nicole; Manalang, Michelle; McReynolds, Lisa J.; Nakano, Taizo A.; Nalepa, Grzegorz; Norkin, Maxim; Oberley, Matthew J.; Orgel, Etan; Pastore, Yves D.; Rosenthal, Joseph; Walkovich, Kelly; Larson, Jordan; Malsch, Maggie; Elghetany, M. Tarek; Fleming, Mark D.; Shimamura, Akiko 分享 收藏
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