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Enhancing pediatric access to cell and gene therapies 提高儿科获得细胞和基因疗法的机会 Mackall, Crystal L.; Bollard, Catherine M.; Goodman, Nancy; Carr, Casey; Gardner, Rebecca; Rouce, Rayne; Sotillo, Elena; Stoner, Rich; Urnov, Fyodor D.; Wayne, Alan S.; Park, Julie; Kohn, Donald B. 分享 收藏
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INTRAVENTRICULAR B7-H3 CAR T CELLS FOR DIFFUSE INTRINSIC PONTINE GLIOMA: INTERIM ANALYSIS OF BRAINCHILD-03 ARM C Vitanza, Nicholas; Ronsley, Rebecca; Wilson, Ashley; Huang, Wenjun; Seidel, Kristy; Pinto, Navin; Gust, Juliane; Gardner, Rebecca; Jensen, Michael; Park, Julie 分享 收藏
TUMOR INFLAMMATION-ASSOCIATED NEUROTOXICITY (TIAN): A TOXICITY SYNDROME IN PATIENTS TREATED WITH IMMUNOTHERAPY FOR CENTRAL NERVOUS SYSTEM TUMORS Mahdi, Jasia; Dietrich, Jorg; Straathof, Karin; Roddie, Claire; Scott, Brian; Davidson, Tom Belle; Prolo, Laura; Batchelor, Tracy; Campen, Cynthia; Davis, Kara; Gust, Juliane; Lim, Michael; Majzner, Robbie; Park, Julie; Partap, Sonia; Ramakrishna, Sneha; Richards, Rebecca; Schultz, Liora; Vitanza, Nicholas; Wang, Leo; Mackall, Crystal; Monje, Michelle 分享 收藏
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KIR/KIR-ligand genotypes and clinical outcomes following chemoimmunotherapy in patients with relapsed or refractory neuroblastoma: a report from the Children's Oncology Group 复发或难治性神经母细胞瘤患者化学免疫治疗后的KIR/KIR配体基因型和临床结局: 来自儿童肿瘤学组的报告 Erbe, Amy K.; Diccianni, Mitch B.; Mody, Rajen; Naranjo, Arlene; Zhang, Fan F.; Birstler, Jen; Kim, KyungMann; Feils, Arika S.; Hung, Jung-Tung; London, Wendy B.; Shulkin, Barry L.; Mathew, Varsha; Parisi, Marguerite T.; Servaes, Sabah; Asgharzadeh, Shahab; Maris, John M.; Park, Julie; Yu, Alice L.; Sondel, Paul M.; Bagatell, Rochelle 分享 收藏
Second Paediatric Strategy Forum for anaplastic lymphoma kinase (ALK) inhibition in paediatric malignancies ACCELERATE in collaboration with the European Medicines Agency with the participation of the Food and Drug Administration Pearson, Andrew D. J.; Barry, Elly; Mosse, Yael P.; Ligas, Franca; Bird, Nick; de Rojas, Teresa; Zimmerman, Zachary F.; Wilner, Keith; Woessmann, Willi; Weiner, Susan; Weigel, Brenda; Venkatramani, Rajkumar; Valteau, Dominique; Trahair, Toby; Smith, Malcolm; Singh, Sonia; Selvaggi, Giovanni; Scobie, Nicole; Schleiermacher, Gudrun; Richardson, Nicholas; Park, Julie; Nysom, Karsten; Norga, Koen; Merino, Margret; McDonough, Joe; Matloub, Yousif; V. Marshall, Lynley; Lowe, Eric; Lesa, Giovanni; Irwin, Meredith; Karres, Dominik; Gajjar, Amar; Doz, Francois; Fox, Elizabeth; DuBois, Steven G.; Donoghue, Martha; Casanova, Michela; Caron, Hubert; Buenger, Vickie; Bradford, Diana; Blanc, Patricia; Barone, Amy; Reaman, Gregory; Vassal, Gilles 分享 收藏
IDENTIFICATION OF MOLECULAR RELATIONSHIPS BETWEEN LIVING AND POST-MORTEM BRAIN TISSUE Liharska, Lora; Beckmann, Noam; Park, Julie; Feng, Claudia; Hoffman, Gabriel; Roussos, Panos; Bendl, Jaroslav; Stahl, Eli; Sklar, Pamela; Schadt, Eric; Kopell, Brian; Charney, Alexander 分享 收藏
CLINICAL UPDATES AND CORRELATIVE FINDINGS FROM THE FIRST PATIENT WITH DIPG TREATED WITH INTRACRANIAL CAR T CELLS Vitanza, Nicholas; Wilson, Ashley; Gust, Juliane; Huang, Wenjun; Perez, Francisco; Albert, Catherine; Pinto, Navin; Gardner, Rebecca; Orentas, Rimas; Berens, Michael; Jensen, Michael; Park, Julie 分享 收藏
Unrealistic parental expectations for cure in poor-prognosis childhood cancer Mack, Jennifer W.; Cronin, Angel M.; Uno, Hajime; Shusterman, Suzanne; Twist, Clare J.; Bagatell, Rochelle; Rosenberg, Abby; Marachelian, Araz; Granger, M. Meaghan; Bender, Julia Glade; Baker, Justin N.; Park, Julie; Cohn, Susan L.; Levine, Alyssa; Taddei, Sarah; Diller, Lisa R. 分享 收藏
LOCOREGIONAL HER2CAR T CELLS FOR PEDIATRIC CENTRAL NERVOUS SYSTEM TUMORS: PRECLINICAL EFFICACY TO TOLERABILITY IN FIRST PATIENT Vitanza, Nicholas; Johnson, Adam; Beebe, Adam; Gust, Juliane; Hauptman, Jason; Hoeppner, Corrine; Wilson, Ashley; Perez, Francisco; Pinto, Navin; Orenta, Rimas; Finn, Laura; Gardner, Rebecca; Park, Julie; Jensen, Michael 分享 收藏
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Natural antibodies to non-human glycans Neu5Gc and alpha-gal correlate with outcome of high-risk neuroblastoma patients treated with dinutuximab on COG ANBL0032 and ANBL0931 Diccianni, Mitchell B.; Mielke, Jenna; Williams, Richard; Messer, Karen; Ozkaynak, Fevzi; Gilman, Andrew L.; Naranjo, Arlene; London, Wendy; Sondel, Paul M.; Park, Julie; Yu, Alice L. 分享 收藏
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Novel childhood asthma genes interact with in utero and early-life tobacco smoke exposure Scholtens, Salome; Postma, Dirkje S.; Moffatt, Miriam F.; Panasevich, Sviatlana; Granell, Raquel; Henderson, A. John; Melen, Erik; Nyberg, Fredrik; Pershagen, Goeran; Jarvis, Deborah; Ramasamy, Adaikalavan; Wjst, Matthias; Svanes, Cecilie; Bouzigon, Emmanuelle; Demenais, Florence; Kauffmann, Francine; Siroux, Valerie; von Mutius, Erika; Ege, Markus Johannes; Braun-Fahrlaender, Charlotte; Genuneit, Jon; Brunekreef, Bert; Smit, Henriette A.; Wijga, Alet H.; Kerkhof, Marjan; Curjuric, Ivan; Imboden, Medea; Thun, Gian A.; Probst-Hensch, Nicole; Freidin, Maxim B.; Bragina, Elena Iu.; Deev, I. A.; Puzyrev, V. P.; Daley, Denise; Park, Julie; Becker, Allan; Chan-Yeung, Moira; Kozyrskyj, Anita L.; Pare, Peter; Marenholz, Ingo; Lau, Susanne; Keil, Thomas; Lee, Young-Ae; Kabesch, Michael; Wijmenga, Cisca; Franke, Lude; Nolte, Ilja M.; Vonk, Judith; Kumar, Ashish; Farrall, Martin; Cookson, William O. C. M.; Strachan, David P.; Koppelman, Gerard H.; Boezen, H. Marike 分享 收藏
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